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Autogene Cevumeran

Phase 2

Muscle-invasive Urothelial Carcinoma | Small molecule | Oncology |BioNTech SE|Last Updated: Sep 2, 2026

Success Probability

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLED
Total Trials1
Total Enrollment62

FDA Designations

No designations recorded

Clinical trial landscape

Autogene Cevumeran · 4 trials · 11 indications

Phase 2 3Phase 1 1
NCT06534983A Study to Evaluate the Efficacy and Safety of Autogene Cevumeran With Nivolumab Versus Nivolumab Alone in Participants With High-risk Muscle-invasive Urothelial Carcinoma (MIUC)Muscle-invasive Urothelial Carcinoma
ACTIVE NOT_RECRUITING62 Analytics
NCT05968326A Study of the Efficacy and Safety of Adjuvant Autogene Cevumeran Plus Atezolizumab and mFOLFIRINOX Versus mFOLFIRINOX Alone in Participants With Resected PDACAdenocarcinoma, Pancreatic Ductal
RECRUITING260 Analytics
NCT03815058A Study to Evaluate the Efficacy and Safety of Autogene Cevumeran (RO7198457) in Combination With Pembrolizumab Versus Pembrolizumab Alone in Participants With Previously Untreated Advanced Melanoma.Advanced Melanoma
COMPLETED131 Analytics
PHASE2ACTIVE NOT_RECRUITING
A Study to Evaluate the Efficacy and Safety of Autogene Cevumeran With Nivolumab Versus Nivolumab Alone in Participants With High-risk Muscle-invasive Urothelial Carcinoma (MIUC)
Muscle-invasive Urothelial CarcinomaUnlock trial analytics
PHASE2RECRUITING
A Study of the Efficacy and Safety of Adjuvant Autogene Cevumeran Plus Atezolizumab and mFOLFIRINOX Versus mFOLFIRINOX Alone in Participants With Resected PDAC
Adenocarcinoma, Pancreatic DuctalUnlock trial analytics
PHASE2COMPLETED
A Study to Evaluate the Efficacy and Safety of Autogene Cevumeran (RO7198457) in Combination With Pembrolizumab Versus Pembrolizumab Alone in Participants With Previously Untreated Advanced Melanoma.
Advanced MelanomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants With Adverse Events (AEs)
Up to approximately 15 months
Disease Free Survival (DFS)
From randomization to first recurrence of PDAC or first occurrence of new cancer, as determined by the investigator, or death from any cause (whichever occurs first), up to approximately 6 years
Progression-free Survival (PFS) According to Response Evaluation Criteria in Solid Tumors, Version 1.1 (RECIST v.1.1) After Randomization
From randomization to PD or death (up to approximately 60 months)

PFS was defined as the time from randomization to the first documented PD as determined by the investigator according to RECIST v1.1 or death from any cause, whichever occurred first. PD was defined as at least a 20% increase in the sum of diameters (SOD) of target lesions, taking as reference the smallest sum on study (nadir), including baseline. In addition to the relative increase of 20%, the sum must also demonstrate an absolute increase of at least 5 millimeters (mm). Kaplan-Meier (KM) method was used to estimate median PFS.

Percentage of Participants with Dose-Limiting Toxicities (DLTs)
Phase 1a: Days 1 to 14 / Phase 1b: Days 1 to 21
MTD/Recommended Phase 2 Dose (RP2D) of Autogene Cevumeran
Phase 1a: Days 1 to 14 / Phase 1b: Days 1 to 21
Percentage of Participants with Adverse Events (AEs)
Baseline up to end of the study (up to approximately 3 years)
Percentage of Participants with Immune-Mediated Adverse Events (imAEs)
Baseline up to end of the study (up to approximately 3 years)
Percentage of Participants by Number of Treatment Cycles Received
Baseline up to end of the study (up to approximately 3 years)
Dose Intensity of Autogene Cevumeran
Baseline up to end of the study (up to approximately 3 years)
Change from Baseline in Targeted Vital Signs
Baseline up to end of study (up to approximately 3 years)
Change from Baseline in Targeted Clinical Laboratory Test Results
Baseline up to end of study (up to approximately 3 years)
Change from Baseline in ECGs
Baseline up to end of study (up to approximately 3 years)

Secondary Endpoints

DFS Rates at 12, 24, and 36 Months
Months 12, 24, 36
Overall Survival (OS)
From randomization to death from any cause (up to approximately 6 years)
OS Rates at 3 and 5 Years
Years 3 and 5
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Autogene Cevumeran + NivolumabEXPERIMENTALParticipants will receive autogene cevumeran along with nivolumab intravenously (IV) at a recommended dose at specified timepoints.
NivolumabACTIVE_COMPARATORParticipants will receive 480 milligrams (mg) of nivolumab, IV, once every 4 weeks (Q4W) for 1 year.
Arm 1: Autogene Cevumeran + Atezolizumab + mFOLFIRINOXEXPERIMENTALParticipants will receive autogene cevumeran, atezolizumab and mFOLFIRINOX.
Arm 2: mFOLFIRINOXACTIVE_COMPARATORParticipants will receive mFOLFIRINOX.
Safety Run-in Period: Autogene Cevumeran + PembrolizumabEXPERIMENTALParticipants will receive at least one cycle of 200 mg pembrolizumab monotherapy by intravenous (IV) infusion followed by 200 mg pembrolizumab IV infusion every 3 weeks (Q3W) plus a recommended dose of autogene cevumeran.
Randomized Period: Arm A: PembrolizumabACTIVE_COMPARATORParticipants will receive 200 mg pembrolizumab administered by IV infusion Q3W. Participants in Arm A have the option to cross over to combination treatment with autogene cevumeran plus pembrolizumab (Arm B) after confirmed disease progression.
Randomized Period: Arm B: Autogene Cevumeran + PembrolizumabEXPERIMENTALParticipants will receive at least one cycle of 200 mg pembrolizumab monotherapy by IV infusion followed by 200 mg pembrolizumab IV infusion Q3W plus a recommended dose of autogene cevumeran.
Phase 1a Flat Dose Escalation: Autogene CevumeranEXPERIMENTALParticipants will receive autogene cevumeran at escalated dosages.
Phase 1b Flat Dose Escalation: Autogene Cevumeran + AtezolizumabEXPERIMENTALParticipants will receive autogene cevumeran at escalated dosages along with atezolizumab at a fixed dose of 1200 milligrams (mg)
Phase Ib: Dose Exploration: Autogene Cevumeran + AtezolizumabEXPERIMENTALNon-small cell lung cancer (NSCLC) or melanoma cancer immunotherapy (CIT)-treated participants will receive autogene cevumeran (at dosage lower than maximum tolerated dose \[MTD\] based on available safety data) along with atezolizumab at a fixed dose of 1200 mg.
Phase 1b Expansion: Autogene Cevumeran + AtezolizumabEXPERIMENTALParticipants with different indications as per inclusion criteria will receive autogene cevumeran (at multiple dose levels below MTD based on available safety data) along with atezolizumab at a fixed dose of 1200 mg.
Phase 1b Expansion: Autogene Cevumeran + Atezolizumab (Serial Biopsy)EXPERIMENTALCIT-naive patients with selected tumor types who consent to optional serial biopsies will receive autogene cevumeran (at multiple dose levels below MTD based on available safety data) along with atezolizumab at a dixed dose of 1200 mg.

Interventions

NameTypeDescription
Autogene CevumeranDRUGAutogene cevumeran will be administered as an IV infusion per the schedule specified in the arm.
NivolumabDRUGNivolumab will be administered as an IV infusion per the schedule specified in the arm.
AtezolizumabDRUGAtezolizumab will be administered IV at a dose of 1680 milligrams (mg) at specified timepoints.
mFOLFIRINOXDRUGmFOLFIRINOX (oxaliplatin, leucovorin, irinotecan, 5-FU) will be administered IV at specified timepoints.
PembrolizumabDRUGParticipants will receive 200 mg pembrolizumab administered by IV infusion Q3W.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites43

Inclusion Criteria: * Participants must have the capacity to participate/enroll in the study and to provide informed consent * Histologically confirmed muscle-invasive UC (also termed transitional cell carcinoma \[TCC\]) of the bladder or upper urinary tract * Tumor-node-metastasis (TNM ) classific...

Countries:United StatesArgentinaAustraliaCanadaDenmarkGermanyGreeceItalyNorwayPolandSouth KoreaSpainSwedenTaiwanUnited KingdomBelgiumFranceNetherlands
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Recent Changes (Last 90 Days)

LOWSep 2, 2026NCT05968326lastUpdatePostDate: changed
LOWSep 2, 2026NCT05968326lastUpdatePostDate: changed
LOWSep 2, 2026NCT05968326lastUpdatePostDate: changed
MEDIUMAug 6, 2026NCT06534983Status: RECRUITING → ACTIVE_NOT_RECRUITING
MEDIUMAug 6, 2026NCT06534983Status: RECRUITING → ACTIVE_NOT_RECRUITING
LOWAug 4, 2026NCT05968326lastUpdatePostDate: changed
LOWAug 4, 2026NCT06534983lastUpdatePostDate: changed
LOWAug 4, 2026NCT05968326lastUpdatePostDate: changed
LOWAug 4, 2026NCT06534983lastUpdatePostDate: changed
MEDIUMJul 9, 2026NCT03289962TRIAL_REMOVED: changed
MEDIUMJul 9, 2026NCT03289962TRIAL_REMOVED: changed
MEDIUMJul 9, 2026NCT03289962TRIAL_REMOVED: changed
LOWJul 7, 2026NCT05968326lastUpdatePostDate: changed
LOWJul 7, 2026NCT06534983lastUpdatePostDate: changed
LOWJul 7, 2026NCT05968326lastUpdatePostDate: changed
LOWJul 7, 2026NCT06534983lastUpdatePostDate: changed
LOWJun 9, 2026NCT05968326lastUpdatePostDate: changed

Frequently asked questions about Autogene Cevumeran

What is Autogene Cevumeran used for?

Autogene Cevumeran is an investigational cancer therapy being studied for the treatment of advanced melanoma, muscle-invasive urothelial carcinoma, and resected pancreatic ductal adenocarcinoma. It is also being evaluated in combination with checkpoint inhibitors such as atezolizumab, pembrolizumab, and nivolumab in clinical trials.

What does Autogene Cevumeran target?

Autogene Cevumeran is a gene therapy that targets tumor-specific mutations by encoding personalized neoantigens. It is designed to stimulate the immune system to recognize and attack cancer cells bearing these mutations. The therapy is being tested across multiple solid tumor types.

Who is developing Autogene Cevumeran?

Autogene Cevumeran is being developed by BioNTech SE, a biotechnology company traded on the NASDAQ under the ticker symbol BNTX. The company is conducting clinical trials of the therapy in various cancer indications.

What phase is Autogene Cevumeran in?

Autogene Cevumeran is currently in Phase 2 clinical development. It is an investigational drug and has not been approved by regulatory authorities. Clinical trials are ongoing to evaluate its safety and efficacy in several cancer types.

What clinical trials is Autogene Cevumeran in?

Autogene Cevumeran is being studied in multiple trials, including NCT03289962 (Phase 1, completed), NCT03815058 (Phase 2, completed), NCT05968326 (Phase 2, recruiting), and NCT06534983 (Phase 2, active). These trials evaluate the drug alone or in combination with other therapies.

Is Autogene Cevumeran the same as RO7198457?

Yes, Autogene Cevumeran is also known as RO7198457. This alternative name appears in clinical trial records and is used interchangeably with Autogene Cevumeran in research and regulatory documents.