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BYL-719

Phase 1

Breast Cancer | Small molecule | Oncology |Novartis AG|Last Updated: Jun 7, 2022

Target and mechanism

Molecular targetPIK3CA
ModalitySmall molecule

Also known as BYL719

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment43

FDA Designations

No designations recorded

Clinical trial landscape

BYL-719 · 1 trial · 1 indication

Phase 1 1
NCT02379247BYL719 and Nab-Paclitaxel in Locally Recurrent or Metastatic HER-2 Negative Breast CancerBreast Cancer
COMPLETED43 Analytics
PHASE1COMPLETED
BYL719 and Nab-Paclitaxel in Locally Recurrent or Metastatic HER-2 Negative Breast Cancer
Breast CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Phase I: Recommended Phase II Dose (RP2D) of BYL-719 (Alpelisib) + Nab-paclitaxel to be Used in Combination to Treat Advanced HER2-negative Breast Cancer
12 months

Phase I was a 3+3 dose escalation design (three dose levels of alpelisib: 250mg, 300mg, and 350mg orally once daily, continuous dosing) with dose-limiting toxicities (DLT) assessed during the first treatment cycle. If two or more of the six patients experienced a dose-limiting toxicity, dosing escalation would cease and maximum tolerated dose (MTD) would be reached. RP2D was the next lower dose at which \<1/6 subjects experienced a DLT.

Phase II: Overall Response Rate (ORR) of Subjects Treated at the Recommended Phase II Dose (RP2D)
24 months

ORR includes complete response (CR) plus partial response (PR). As evaluated per RECIST version 1.1.

Secondary Endpoints

Clinical Benefit Rate (CBR) at 16 Weeks of Study Treatment
16 weeks
Pharmacokinetics of BYL-719 (Alpelisib) When Administered With Nab-paclitaxel
In cycle 1 day 1, from prior to alpelisib dosing through 8 hours after alpelisib dosing
Pharmacokinetics of (Total) Nab-paclitaxel When Administered With BYL-719 (Alpelisib)
In cycle 1 day 1, from prior to alpelisib dosing through 8 hours after alpelisib dosing
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Dose level 1 BYL-719/alpelisib (250mg)+Nab-paclitaxelEXPERIMENTALBYL-719 (alpelisib): 250mg daily on day 1-28 Nab-paclitaxel: 100mg/m2 IV days 1, 8, 15 of each 28 day cycle (Window for Nab-paclitaxel is +/- 1 day)
Dose level 2 BYL-719 (alpelisib) (300mg)+Nab-paclitaxelEXPERIMENTALBYL-719 (alpelisib): 300mg by mouth daily on day 1-28 of each 28 day cycle Nab-paclitaxel: 100mg/m2 given IV on days 1, 8, 15 of each 28 day cycle (Window for Nab-paclitaxel is +/- 1 day)
Dose level 3 BYL-719 (alpelisib) (350mg)+Nab-paclitaxelEXPERIMENTALBYL-719 (alpelisib): 350mg by mouth daily on day 1-28 of each 28 day cycle Nab-paclitaxel: 100mg/m2 given IV on days 1, 8, 15 of each 28 day cycle (Window for Nab-paclitaxel is +/- 1 day)
BYL-719 (alpelisib) Dose ExpansionEXPERIMENTALBYL-719 (alpelisib): RP2D from Phase I by mouth daily on day 1-28 of each 28 day cycle Nab-paclitaxel: 100mg/m2 given IV on days 1, 8, 15 of each 28 day cycle (Window for Nab-paclitaxel is +/- 1 day)

Interventions

NameTypeDescription
BYL-719 (alpelisib)DRUGOral PI3K inhibitor
Nab-paclitaxelDRUGIV taxane
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites4

Inclusion Criteria: 1. Ability to understand and the willingness to sign a written Informed Consent Form. 2. Age ≥ 18 years 3. Histologically proven HER-2 negative breast cancer (HER-2 negative defined as HER IHC 0 or 1+ and/or HER-2 FISH negative); HER-2 negative breast cancer includes hormone pos...

Countries:United States
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Competitive Landscape -Breast Cancer 402 trials

Top 20 of 92 competitors

CompanyTickerTrialsLead PhaseDrugs
AstraZeneca PLCAZN47PHASE3Fulvestrant, Capivasertib
Merck & Co., Inc.MRK12PHASE3Pembrolizumab, Paclitaxel, Doxorubicin, Epirubicin, Cyclophosphamide
Eli Lilly and CompanyLLY27PHASE3Abemaciclib, Standard Adjuvant Endocrine Therapy
BioNTech SE Sponsored ADRBNTX7PHASE3DB-1303/BNT323, T-DM1
Gilead Sciences, Inc.GILD13PHASE3Sacituzumab Govitecan-hziy, Eribulin, Capecitabine Product, Gemcitabine, Vinorelbine
Novartis AG Sponsored ADRNVS30PHASE3Ribociclib
Pfizer Inc.PFE34PHASE3ARV-471, Fulvestrant
BeOne Medicines Ltd. Sponsored ADRONC5PHASE3BGB-43395, Letrozole, Abemaciclib, Palbociclib, Ribociclib
Olema Pharmaceuticals, Inc.OLMA5PHASE3Palazestrant, Fulvestrant, Anastrozole, Letrozole, Exemestane
Jazz Pharmaceuticals Public Limited CompanyJAZZ3PHASE3Zanidatamab, Trastuzumab, Eribulin, Vinorelbine, Gemcitabine
Celcuity Inc.CELC3PHASE3Gedatolisib, Palbociclib, Fulvestrant, Alpelisib
Relay Therapeutics, Inc.RLAY2PHASE3Zovegalisib, Capivasertib, Fulvestrant
GSK plc Sponsored ADRGSK2PHASE3Niraparib
Greenwich LifeSciences, Inc.GLSI1PHASE3GLSI-100
Bristol-Myers Squibb CompanyBMY5PHASE2Iza-bren, Nab-paclitaxel, Paclitaxel, Capecitabine, Carboplatin
BriaCell Therapeutics CorpBCTX2PHASE3SV-BR-1-GM, Cyclophosphamide, Interferon infiltration of the inoculation site, Retifanlimab, Treatment of Physician's Choice
Incyte CorporationINCY4PHASE2Ruxolitinib, Capecitabine, Regorafenib
Natera, Inc.NTRA3PHASE2Discontinuation of the anti-HER2 maintenance therapy
Puma Biotechnology, Inc.PBYI3PHASE2Neratinib, Loperamide, Colesevelam
Atossa Therapeutics, Inc.ATOS1PHASE2endoxifen, goserelin
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Frequently asked questions about BYL-719

What is BYL-719 used for?

BYL-719 is an investigational small molecule being studied for use in oncology, including advanced solid tumors with an alteration of the PIK3CA gene, estrogen receptor positive breast cancer, adenocarcinoma lung cancer, squamous cell lung carcinoma, breast cancer, and head and neck neoplasms. It is being developed by Novartis AG.

What does BYL-719 target?

BYL-719 targets PIK3CA, a gene that encodes the p110 alpha catalytic subunit of phosphatidylinositol 3-kinase. It is being studied in patients whose tumors have an alteration of the PIK3CA gene, as well as in other advanced solid malignancies.

Who makes BYL-719?

BYL-719 is being developed by Novartis AG, a multinational pharmaceutical company traded on the New York Stock Exchange under the ticker symbol NVS. The drug is an investigational small molecule in clinical development for oncology indications.

What phase is BYL-719 in?

BYL-719 is in clinical development, with trials conducted at Phase 1 and Phase 2 stages. The drug is investigational and has not been approved by regulatory authorities. Clinical trials have been completed across multiple studies, including Phase 1 and Phase 2 trials.

What clinical trials is BYL-719 in?

BYL-719 has been studied in several completed clinical trials, including NCT01219699, a Phase 1 study in patients with advanced solid malignancies whose tumors have a PIK3CA gene alteration; NCT01387321, a Phase 1 study in Japanese patients with advanced solid tumors; NCT02051751, a Phase 1 study combining BYL719 with paclitaxel in breast and head-and-neck cancer; and NCT02276027, a Phase 2 study in Chinese patients with non-small cell lung cancer.

Is BYL-719 the same as BYL719?

Yes, BYL-719 and BYL719 refer to the same investigational drug. Both names are used interchangeably in clinical trial documentation and research literature to describe the small molecule being developed by Novartis AG for oncology indications.