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Gedatolisib

Phase 3

Breast Cancer | Small molecule | Oncology |Celcuity Inc.|Last Updated: Apr 13, 2026

Target and mechanism

Molecular targetPIK3R1, PIK3CB, PIK3CG, PIK3CA, PIK3R2, PIK3CD
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

RandomizedACTIVE_CONTROLLEDDMC
Total Trials2
Total Enrollment842

FDA Designations

PRIORITY_REVIEW

Clinical trial landscape

Gedatolisib · 4 trials · 8 indications

Phase 3 1Phase 1 3
NCT05501886Gedatolisib Plus Fulvestrant With or Without Palbociclib vs Standard-of-Care for the Treatment of Patients With Advanced or Metastatic HR+/HER2- Breast Cancer (VIKTORIA-1)Breast Cancer
ACTIVE NOT_RECRUITING701 Analytics
PHASE3ACTIVE NOT_RECRUITING
Gedatolisib Plus Fulvestrant With or Without Palbociclib vs Standard-of-Care for the Treatment of Patients With Advanced or Metastatic HR+/HER2- Breast Cancer (VIKTORIA-1)
Breast CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Progression Free Survival (PFS) in Patients with PIK3CA WT and PIK3CA MT Breast Cancer
Approximately 48 months

PFS is defined as the time from randomization to death or the first documented progression, whichever occurs first, confirmed by Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 criteria, as determined based on blinded independent central review (BICR)

Phase 1: Assessment of the safety and tolerability of gedatolisib in combination with darolutamide in metastatic castration-resistant prostate cancer (mCRPC)
Cycle 1, Day 1 to end of safety follow up (each cycle is 28 days and safety follow up will continue until 30 days after last dose of study medication)

Type, incidence, severity (as graded by National Cancer Institute \[NCI\] Common Terminology Criteria for Adverse Events \[CTCAE\] v5.0), seriousness, and relationship to study medications of adverse events (AEs) and any laboratory abnormalities

Phase 1: Identification of the recommended Phase 2 dose (RP2D) of gedatolisib in combination with darolutamide in mCRPC
Through Phase I completion, an average of 1 year.

Incidence of dose-limiting toxicities (DLTs) and AEs graded according to NCI CTCAE v5.0

Phase 2: Assessment of the antitumor activity of gedatolisib in combination with darolutamide in each arm as demonstrated by radiographic progression-free survival (rPFS) by arm
6 months

Radiographic progression-free survival rate at 6 months as measured by the Kaplan-Meier (K-M) method and assessed based on Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 with modifications as specified in Prostate Cancer Working Group 3 (PCWG3) criteria

Maximum Tolerated Dose (MTD) of talazoparib in combination with gedatolisib (Phase I)
28 days

Determine the recommended Phase 2 dose (RP2D) of talazoparib in combination with gedatolisib in patients with advanced human epidermal growth factor receptor 2 (HER2) negative (triple negative or BRCA1/2 deficient) breast cancer.

Objective Response Rate (ORR) (Phase II)
24 Months

Calculate ORR, which will include confirmed complete response (CR) + confirmed partial response (PR) determined as per RECIST1.1 on treatment with talazoparib in combination with gedatolisib in patients with BRCA1/2 deficient advanced HER2 negative breast cancer.

Number of participants with dose limiting toxicities
up to 28 days
Objective response rate observed in patients in the dose expansion portion
16 weeks

Number of patients for each response category, objective response rate (number of patients with a complete response (CR)) relative to the number of response evaluable patients

Secondary Endpoints

Overall Survival (OS) in Patients with PIK3CA WT and PIK3CA MT Breast Cancer
From date of randomization to the date of death due to any cause, up to approximately 48 months
Overall Response Rate (ORR) in Patients with PIK3CA WT and PIK3CA MT Breast Cancer
Up to approximately 48 months
Duration of Response (DOR) in Patients with PIK3CA WT and PIK3CA MT Breast Cancer
Up to approximately 48 months
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Arm A - Patients Lacking PIK3CA Mutations (WT)EXPERIMENTALGedatolisib + Palbociclib + Fulvestrant
Arm B - Patients Lacking PIK3CA Mutations (WT)EXPERIMENTALGedatolisib + Fulvestrant
Arm C - Patients Lacking PIK3CA Mutations (WT)ACTIVE_COMPARATORFulvestrant
Arm D - Patients with PIK3CA Mutation (MT)EXPERIMENTALGedatolisib + Palbociclib + Fulvestrant
Arm E - Patients with PIK3CA Mutation (MT)ACTIVE_COMPARATORAlpelisib + Fulvestrant
Arm F - Patients with PIK3CA Mutation (MT)EXPERIMENTALGedatolisib + Fulvestrant
Phase 1 Arm 1EXPERIMENTALArm 1 - 120 mg of gedatolisib (administered once weekly for 3 weeks on/1 week off) in combination with darolutamide 600 mg (two 300 mg tablets) orally administered twice daily (equivalent to a total daily dose of 1200 mg on Days 1-28 of each cycle)
Phase 1 Arm 2EXPERIMENTALArm 2 - 180 mg of gedatolisib (administered once weekly for 3 weeks on/1 week off) in combination with darolutamide 600 mg (two 300 mg tablets) orally administered twice daily (equivalent to a total daily dose of 1200 mg on Days 1-28 of each cycle)
Phase 2EXPERIMENTALThe recommended Phase 2 dose (RP2D) of gedatolisib (administered once weekly for 3 weeks on/1 week off) in combination with darolutamide 600 mg (two 300 mg tablets) orally administered twice daily (equivalent to a total daily dose of 1200 mg on Days 1-28 of each cycle)
Talazoparib + GedatolisibEXPERIMENTALTalazoparib + Gedatolisib Phase 1: Dose Level -1: Gedatolisib 150mg IV, Days 1,8,15,22; Talazoparib 0.75 mg/orally qd, Days 1-28 Dose Level 1: Gedatolisib 180mg IV, Days 1,8,15,22; Talazoparib 0.75 mg/orally qd, Days 1-28 Dose Level 2: Gedatolisib 180mg IV, Days 1,8,15,22; Talazoparib 1.00 mg/orally qd, Days 1-28 Phase 2: Gedatolisib 180 mg IV on days 1, 8, 15 and 22; Talazoparib 1.00 mg once daily, Days 1-28. Subjects receiving weekly gedatolisib may continue current regimen or may switch to gedatolisib 180 mg IV on days 1, 8, and 15; Talazoparib 1.00 mg once daily, Days 1-28 (3 weeks on/ 1 week off). All changes will be permanent.
Letrozole CohortEXPERIMENTALLetrozole combination cohort in dose escalation
Fulvestrant cohortEXPERIMENTALFulvestrant combination cohort in dose escalation
ARM AEXPERIMENTALGedatolisib + palbociclib + letrozole in dose expansion
ARM BEXPERIMENTALGedatolisib + palbociclib + fulvestrant in dose expansion
ARM CEXPERIMENTALGedatolisib + palbociclib + fulvestrant in dose expansion
Arm DEXPERIMENTALGedatolisib (3:1) + palbociclib + fulvestrant in dose expansion

Interventions

NameTypeDescription
GedatolisibDRUGGedatolisib 180 mg IV given weekly for 3 weeks (Days 1, 8, 15) followed by 1 week off
PalbociclibDRUGPalbociclib 125 mg PO given daily for 3 weeks (21 days), followed by 1 week off
FulvestrantDRUGFulvestrant 500 mg IM (2 × 5 mL injections) given every 2 weeks during Cycle 1 (Days 1 and 15), then every 4 weeks beginning with Cycle 2 Day 1
AlpelisibDRUGAlpelisib 300 mg PO (2 × 150 mg tablets) given daily for 4 weeks (28 days)
DarolutamideDRUGDarolutamide is a novel androgen receptor inhibitor that has been studied and received approval for treatment of patients with nonmetastatic CRPC and in metastatic hormone-sensitive prostate cancer.
TalazoparibDRUG.75-1.00mg
LetrozoleDRUGLetrozole at 2.5 mg daily
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites235

Inclusion Criteria: 1. Histologically or cytologically confirmed diagnosis of metastatic or locally advanced breast cancer Adult females, pre- and/or post-menopausal, and adult males. Pre-menopausal (and peri-menopausal) women can be enrolled if amenable to treatment with an LHRH agonist. Patients ...

Countries:United StatesArgentinaAustraliaAustriaBelgiumBrazilBulgariaCanadaCzechiaFranceGermanyGreeceHungaryIndiaItalyMexicoPolandRomaniaSingaporeSouth KoreaSpainTaiwanUnited Kingdom
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Competitive Landscape -Breast Cancer 399 trials

Top 20 of 91 competitors

CompanyTickerTrialsLead PhaseDrugs
AstraZeneca PLCAZN46PHASE3Fulvestrant, Capivasertib
Merck & Co., Inc.MRK12PHASE3Pembrolizumab, Paclitaxel, Doxorubicin, Epirubicin, Cyclophosphamide
Eli Lilly and CompanyLLY27PHASE3Abemaciclib, Standard Adjuvant Endocrine Therapy
BioNTech SE Sponsored ADRBNTX7PHASE3DB-1303/BNT323, T-DM1
Gilead Sciences, Inc.GILD13PHASE3Sacituzumab Govitecan-hziy, Eribulin, Capecitabine Product, Gemcitabine, Vinorelbine
Novartis AG Sponsored ADRNVS30PHASE3Ribociclib
Pfizer Inc.PFE34PHASE3ARV-471, Fulvestrant
BeOne Medicines Ltd. Sponsored ADRONC5PHASE3BGB-43395, Letrozole, Abemaciclib, Palbociclib, Ribociclib
Olema Pharmaceuticals, Inc.OLMA5PHASE3Palazestrant, Fulvestrant, Anastrozole, Letrozole, Exemestane
Jazz Pharmaceuticals Public Limited CompanyJAZZ3PHASE3Zanidatamab, Trastuzumab, Eribulin, Vinorelbine, Gemcitabine
Celcuity Inc.CELC3PHASE3Gedatolisib, Palbociclib, Fulvestrant, Alpelisib
Relay Therapeutics, Inc.RLAY2PHASE3Zovegalisib, Capivasertib, Fulvestrant
GSK plc Sponsored ADRGSK2PHASE3Niraparib
Greenwich LifeSciences, Inc.GLSI1PHASE3GLSI-100
Bristol-Myers Squibb CompanyBMY5PHASE2Iza-bren, Nab-paclitaxel, Paclitaxel, Capecitabine, Carboplatin
BriaCell Therapeutics CorpBCTX1PHASE3SV-BR-1-GM, Cyclophosphamide, Interferon infiltration of the inoculation site, Retifanlimab, Treatment of Physician's Choice
Incyte CorporationINCY4PHASE2Ruxolitinib, Capecitabine, Regorafenib
Natera, Inc.NTRA3PHASE2Discontinuation of the anti-HER2 maintenance therapy
Puma Biotechnology, Inc.PBYI3PHASE2Neratinib, Loperamide, Colesevelam
Atossa Therapeutics, Inc.ATOS1PHASE2endoxifen, goserelin
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Frequently asked questions about Gedatolisib

What is Gedatolisib used for?

Gedatolisib is an investigational small molecule being studied for the treatment of breast cancer, including HR+/HER2- advanced or metastatic breast cancer, and triple-negative breast cancer (TNBC). It is also being evaluated in metastatic castration-resistant prostate cancer (mCRPC). It is not yet approved and remains in clinical development.

What does Gedatolisib target?

Gedatolisib is a pan-PI3K/mTOR inhibitor that targets the class I PI3K isoforms PIK3CA, PIK3CB, PIK3CD, PIK3CG, and the regulatory subunits PIK3R1 and PIK3R2. By inhibiting these targets, it is designed to block the PI3K signaling pathway involved in tumor growth.

Who is developing Gedatolisib?

Gedatolisib is being developed by Celcuity Inc. (NASDAQ: CELC). The company is conducting clinical trials to evaluate the drug in combination with other agents for the treatment of breast cancer and prostate cancer.

What phase is Gedatolisib in?

Gedatolisib is in Phase 3 clinical development. The Phase 3 VIKTORIA-1 trial (NCT05501886) is evaluating gedatolisib plus fulvestrant with or without palbociclib versus standard-of-care in patients with advanced or metastatic HR+/HER2- breast cancer.

What clinical trials is Gedatolisib in?

Gedatolisib is being studied in multiple trials, including the Phase 3 VIKTORIA-1 trial (NCT05501886) in HR+/HER2- breast cancer, a Phase 1 trial (NCT03911973) in TNBC, a Phase 1 trial (NCT06190899) in mCRPC, and a completed Phase 1 trial (NCT02684032) in metastatic breast cancer.

Is Gedatolisib the same as Arm A or Arm C?

Gedatolisib is the investigational drug being tested in combination regimens referred to as Arm A (gedatolisib plus palbociclib plus fulvestrant) and Arm C (gedatolisib plus palbociclib plus letrozole) in clinical trials. These are treatment arms within studies, not alternative names for the drug itself.