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DKN-01

Phase 2

Colorectal Cancer | Small molecule | Oncology |Cypherpunk Technologies Inc.|Last Updated: Aug 3, 2025

Success Probability
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Market & Valuation
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Trial Design
RandomizedACTIVE_CONTROLLEDBiomarker
Total Trials1
Total Enrollment188
FDA Designations
No designations recorded
Clinical trial landscape

DKN-01 · 6 trials · 20 indications

Phase 2 2Phase 1 4
NCT05480306Phase 2 Study of DKN-01 in Colorectal CancerColorectal Cancer
COMPLETED188 Analytics
NCT03395080A Study of DKN-01 as a Monotherapy or in Combination With Paclitaxel in Patients With Recurrent Epithelial Endometrial or Epithelial Ovarian Cancer or CarcinosarcomaEndometrial Cancer
COMPLETED111 Analytics
PHASE2COMPLETED
Phase 2 Study of DKN-01 in Colorectal Cancer
Colorectal CancerUnlock trial analytics
PHASE2COMPLETED
A Study of DKN-01 as a Monotherapy or in Combination With Paclitaxel in Patients With Recurrent Epithelial Endometrial or Epithelial Ovarian Cancer or Carcinosarcoma
Endometrial CancerUnlock trial analytics
Study Endpoints
Primary Endpoints
Progression Free Survival (PFS)
approximately 6 months

PFS, as determined by the Investigator per RECIST v1.1 of DKN-01 plus SOC versus SOC.

Number of Subjects With Objective Response Rate (ORR) in EEC or EOC Patients
Baseline to study completion (approximately 6 months)

Best overall response of Complete Response (CR; disappearance of all target lesions, any pathological lymph nodes whether target or non-target must have reduction in short axis to \<10mm) or Partial Response (PR; at least a 30% decrease in the sum of the diameters of target lesions, taking as reference the baseline sum of diameters) as assessed by the Investigator per Response Evaluation Criteria in Solid Tumors Criteria (RECIST v1.1)

Number of Subjects With Objective Response Rate (ORR) in Carcinosarcoma (MMMT) Patients
Baseline to study completion (approximately 6 months)

Best overall response of Complete Response (CR; disappearance of all target lesions, any pathological lymph nodes whether target or non-target must have reduction in short axis to \<10mm) or Partial Response (PR; at least a 30% decrease in the sum of the diameters of target lesions, taking as reference the baseline sum of diameters) as assessed by the Investigator per Response Evaluation Criteria in Solid Tumors Criteria (RECIST v1.1)

Maximum tolerated dose and dose-limiting toxicities as determined in Part A.
End of Cycle 1 (Day 21)

Toxicities will be graded according to the National Cancer Institute Common Terminology Criteria for Adverse Events (NCI-CTCAE v 4.03).

Composite Safety parameters as assessed by new or changing physical examinations, vital signs, electrocardiograms (ECGs), clinical laboratories, concomitant medication reviews, and assessment of adverse events.
Parts A and B: at a minimum Days 1, 8, 15 of each treatment cycle.
Number of subjects with dose limiting toxicities in each treatment arm
Baseline to End of Cycle 1 (each cycle is 28 days, except each cycle is 21 days when DKN-01 is administered with pembrolizumab)
Number of subjects with treatment emergent adverse events related to study treatment (DKN-01 as monotherapy or in combination with paclitaxel or pembrolizumab)
Baseline until 30 days after last dose of study drug
Fluorine F18 sodium fluoride positron emission tomography (NaF-PET/CT) standard uptake value (SUV)
Pre-study to after 6 months of therapy

SUV as measured by NaF-PET/CT in both myeloma bone lesions and normal bone

Fluorine F18 sodium fluoride positron emission tomography (NaF-PET/CT) influx constant (Ki)
Pre-study to after 6 months of therapy

Ki as measured by NaF-PET/CT in both myeloma bone lesions and normal bone

F18 fluorodeoxyglucose positron emission tomography (FDG-PET/CT) standard uptake value (SUV)
Pre-study to after 6 months of therapy

SUV as measured by FDG-PET/CT in both myeloma bone lesions and normal bone

Number of patients with treatment emergent adverse events
Baseline to study completion (approximately 7 months)
Summary of Total Adverse Events (AE)
Baseline to study completion (approximately 3 months)

Total Adverse Events (AE), total treatment emergent adverse events (TEAE), total Serious Adverse Events (SAE), and total dose-limiting toxicity (DLT) for both Parts A and B.

Summary of Patients With Adverse Events (AE)
Baseline to study completion (approximately 3 months)

Number of patients who had Adverse Events (AE) including treatment related treatment emergent adverse events (TEAE), Common Toxicity Criteria for Adverse Effects (CTCAE), and Serious Adverse Events (SAE) for both Parts A and B. Severity was coded to NCI CTCAE version 4.02. For maximum severity and relationship, patients were counted only once in the most severe or most related category.

Progression Free Survival (PFS) in Patients With Relapsed or Refractory Non-small Cell Lung Cancer (NSCLC)
Time from the date of signed informed consent to the first date of objectively determined progressive disease or death from any cause

For Part B only. The distribution of PFS was estimated using the Kaplan-Meier (KM) method. PFS was defined as the time from the date of signed informed consent to the first date of objectively determined progressive disease (Progression is defined by Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.1) and International Multiple Myeloma Working Group (IMWG)) or death from any cause. For patients who were still alive at the time of analysis (ie, data cut-off date) and without evidence of tumor progression, PFS was censored at the date of the most recent objective progression-free observation.

Secondary Endpoints
Objective Response Rate (ORR)
approximately 6 months
Duration of Response (DoR)
approximately 6 months
Overall Survival (OS)
approximately 6 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
TreatmentEXPERIMENTALDKN-01 + FOLFIRI or FOLFOX + bevacizumab
ControlACTIVE_COMPARATORFOLFIRI or FOLFOX + bevacizumab
DKN-01 monotherapy in recurrent EECEXPERIMENTAL300mg DKN-01 monotherapy in recurrent EEC
DKN-01+paclitaxel in recurrent EECEXPERIMENTAL300mg DKN-01+paclitaxel in recurrent EEC
DKN-01 monotherapy in recurrent EOCEXPERIMENTAL300mg DKN-01 monotherapy in recurrent EOC
DKN-01+paclitaxel in recurrent EOCEXPERIMENTAL300mg DKN-01+paclitaxel in recurrent EOC
DKN-01 monotherapy in carcinosarcomaEXPERIMENTAL600mg DKN-01 monotherapy in carcinosarcoma
DKN-01 +paclitaxel in carcinosarcomaEXPERIMENTAL600mg DKN-01 +paclitaxel in carcinosarcoma
150 mg DKN-01 Part AEXPERIMENTALPatients will receive 150 mg of DKN-01 followed by gemcitabine 1000 mg/m2 and cisplatin 25 mg/m2 on Days 1 and 8 of each 21-day cycle.
300 mg DKN-01 Part AEXPERIMENTALPatients will receive 300 mg of DKN-01 followed by gemcitabine 1000 mg/m2 and cisplatin 25 mg/m2 on Days 1 and 8 of each 21-day cycle.
MTD mg DKN-01 Part BEXPERIMENTALPatients are treated at the maximum tolerated dose (MTD) of DKN-01 (or highest dose tested in Part A if the MTD is not defined) followed by gemcitabine 1000 mg/m2 and cisplatin 25 mg/m2 on Days 1 and 8 of each 21-day cycle.
DKN-01 150 mg plus paclitaxelEXPERIMENTALDKN-01 150 mg administered on Days 1 and 15 and paclitaxel 80 mg per meter squared of body surface area (mg/m2) administered on Days 1, 8, 15, and 22
DKN-01 300 mg plus paclitaxelEXPERIMENTALDKN-01 300 mg administered on Days 1 and 15 and paclitaxel 80 mg per meter squared of body surface area (mg/m2) administered on Days 1, 8, 15, and 22
DKN-01 150 mg plus pembrolizumabEXPERIMENTALDKN-01 150 mg administered on Days 1 and 15 and pembrolizumab 200 mg administered on Day 1
DKN-01 300 mg plus pembrolizumabEXPERIMENTALDKN-01 300 mg administered on Days 1 and 15 and pembrolizumab 200 mg administered on Day 1
DKN-01 300 mg monotherapyEXPERIMENTALDKN-01 300 mg administered on Days 1 and 15
DKN-01 300mgEXPERIMENTALDKN-01 plus lenalidomide (Revlimid)/dexamethasone
DKN-01 600mgEXPERIMENTALDKN-01 plus lenalidomide (Revlimid)/dexamethasone
Standard of CareACTIVE_COMPARATORLenalidomide (Revlimid)/dexamethasone
75 milligram (mg) DKN-01 Part AEXPERIMENTALDKN-01: DKN-01 was administered intravenously (IV) once a week over a minimum of 30 minutes and up to a maximum of 2 hours for dose levels of 75 mg, 150 mg and 300 mg. At the 600 mg dose level, DKN-01 was administered by IV on days 1 and 15 of each cycle. PART A - Dose Escalation: Study group of 3 participants were treated with a 28 day cycle of DKN-01 at an assigned dose level until disease progression. Dose escalation occurred sequentially over the doses of 75, 150, 300, and 600 mg until the criteria for reaching the maximum tolerated dose (MTD) were met or the highest planned dose study group was completed. Cycle 1 defined the dose limiting toxicity (DLT) period that governs dose escalation. The dose escalation method was guided by the incidence of DLTs during the first cycle.
600 mg DKN-01 Part AEXPERIMENTALDKN-01: DKN-01 was administered intravenously (IV) once a week over a minimum of 30 minutes and up to a maximum of 2 hours for dose levels of 75 mg, 150 mg and 300 mg. At the 600 mg dose level, DKN-01 was administered by IV on days 1 and 15 of each cycle. PART A - Dose Escalation: Study group of 3 participants were treated with a 28 day cycle of DKN-01 at an assigned dose level until disease progression. Dose escalation occurred sequentially over the doses of 75, 150, 300, and 600 mg until the criteria for reaching the maximum tolerated dose (MTD) were met or the highest planned dose study group was completed. Cycle 1 defined the dose limiting toxicity (DLT) period that governs dose escalation. The dose escalation method was guided by the incidence of DLTs during the first cycle.
300 mg DKN-01 Part BEXPERIMENTALDose Confirmation: Once the MTD had been established or the highest planned dose level completed, 300 mg of DKN-01 was administered as IV on days 1 and 15 of every 28 day cycle.
Interventions
NameTypeDescription
DKN-01DRUG30 minute IV infusion (400mg) every two weeks with an additional loading dose in the first cycle of treatment
FOLFIRIDRUG90-min IV infusion of irinotecan, leucovorin, and fluorouracil followed by a continuous 46-hour infusion of fluorouracil every two weeks
BevacizumabDRUG90-min IV infusion (5mg)
FOLFOXDRUG2 hour IV infusion of oxaliplatin, folinic acid, and fluorouracil followed by a continuous 46-hour infusion of fluorouracil every two weeks
PaclitaxelDRUGAdministered by IV infusion
300mg DKN-01DRUGAdministered by IV infusion
600mg DKN-01DRUGAdministered by IV infusion
gemcitabineDRUGAdministered by IV infusion.
cisplatinDRUGAdministered by IV infusion
DKN-01 150 mgDRUGAdministered by IV infusion
PembrolizumabDRUGAdministered by IV infusion
DKN-01 300 mgDRUGAdministered by IV infusion
DKN-01 600 mgDRUG600 mg IV infusion of DKN-01 administered twice per 28 day cycle on Days 1 and 15, plus lenalidomide/dexamethasone
Standard of CareDRUGCurrent approved standard of care
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Eligibility Criteria
Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites40

Adult patients with advanced CRC with measurable disease (RECIST v1.1) who have radiographically progressed during or following one line of systemic treatment will be enrolled in the study. Inclusion Criteria: Patients meeting all of the following criteria will be considered eligible for study ent...

Countries:United StatesGermanySouth Korea
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