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Pertuzumab

Phase 3

Breast Neoplasms | Small molecule | Oncology |AstraZeneca PLC|Last Updated: Feb 23, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedACTIVE_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment927
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05113251Trastuzumab Deruxtecan (T-DXd) Alone or in Sequence With THP, Versus Standard Treatment (ddAC-THP), in HER2-positive Early Breast CancerPHASE3 ACTIVE NOT_RECRUITING 927Oct 25, 2021Apr 30, 2027Feb 23, 2026145 United States, Brazil +16
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Study Endpoints
Primary Endpoints
rate of pathologic complete response (pCR)
Up to 39 months after study start

Proportion of participants who have no evidence by H\&E staining of residual invasive disease

Secondary Endpoints
Event-Free Survival
Up to 72 months after study start
Invasive Disease-Free Survival (IDFS)
Up to 72 months after study start
Overall Survival
Up to 72 months after study start
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Arm AEXPERIMENTALTrastuzumab deruxtecan
Arm BEXPERIMENTALT-DXd, followed by THP
Arm CACTIVE_COMPARATORdoxorubicin and cyclophosphamide, followed by THP
Interventions
NameTypeDescription
Trastuzumab DeruxtecanDRUGadministered by intravenous infusion
PaclitaxelDRUGadministered by intravenous infusion
TrastuzumabDRUGadministered by intravenous infusion
PertuzumabDRUGadministered by intravenous infusion
DoxorubicinDRUGadministered by intravenous infusion
cyclophosphamideDRUGadministered by intravenous infusion
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites145

Key Inclusion Criteria: * Patients must be at least 18 years of age. * Histologically documented HER2-positive early breast cancer (EBC) participants, including clinical stage at presentation (based on mammogram or breast MRI assessment): T0-4 (inclusive of inflammatory breast cancer), N1-3, M0 or ...

Countries:United StatesBrazilBulgariaCanadaChinaGermanyIndiaItalyJapanPeruPhilippinesPolandRussiaSaudi ArabiaSouth KoreaSpainTaiwanThailand
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT05113251primaryCompletionDate: changed
LOWMay 24, 2026NCT05113251studyFirstPostDate: changed