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UGN-103

Phase 3

Bladder Cancer | Small molecule | Oncology |UroGen Pharma Ltd.|Last Updated: Jan 15, 2026

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment99

FDA Designations

No designations recorded

Clinical trial landscape

UGN-103 · 1 trial · 3 indications

Phase 3 1
NCT06331299A Phase 3 Study of UGN-103 for Treatment of Patients With Low-grade Intermediate-risk Non-muscle Invasive Bladder CancerBladder Cancer
ACTIVE NOT_RECRUITING99 Analytics
PHASE3ACTIVE NOT_RECRUITING
A Phase 3 Study of UGN-103 for Treatment of Patients With Low-grade Intermediate-risk Non-muscle Invasive Bladder Cancer
Bladder CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Complete response rate (CRR)
3 months

CRR is defined as the proportion of patients who achieved CR at the 3-month Visit.

Secondary Endpoints

Duration of response (DOR)
Up to 21 months
Durable complete response (DCR) rate
Up to 21 months
Incidence of treatment-emergent adverse events (TEAEs), serious TEAEs, TEAEs of special interest, and abnormal clinical laboratory test results (hematology and serum chemistry)
Up to 21 months
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
UGN-103EXPERIMENTALPatients will receive UGN-103 (75 mg mitomycin) once weekly for 6 weeks (a total of 6 doses).

Interventions

NameTypeDescription
UGN-103DRUGUGN-103 consists of mitomycin and sterile hydrogel (a proprietary thermally responsive gel) that is used to reconstitute mitomycin before instillation. The reverse thermal properties of UGN-103 allow for local administration of mitomycin as a liquid under chilled conditions, with subsequent conversion to a semi-solid gel depot following instillation into the bladder.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites48

Inclusion Criteria: 1. Provide written informed consent, which includes compliance with the requirements and restrictions listed in the informed consent form (ICF) and the protocol. 2. Patient who has LG-NMIBC (Ta) histologically confirmed by cold cup biopsy at Screening or within 8 weeks before Sc...

Countries:United StatesBulgariaEstoniaGeorgiaLatviaRomaniaSpain
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Recent Changes (Last 90 Days)

LOWMay 26, 2026NCT06331299primaryCompletionDate: changed
LOWMay 24, 2026NCT06331299studyFirstPostDate: changed

Frequently asked questions about UGN-103

What is UGN-103 used for?

UGN-103 is an investigational small molecule being developed for the treatment of low-grade intermediate-risk non-muscle invasive bladder cancer, a form of bladder cancer and urothelial carcinoma. It is currently in Phase 3 clinical development and has not been approved by regulatory authorities.

What does UGN-103 target?

UGN-103 is a small molecule therapeutic, but its specific molecular target has not been disclosed. The drug is being studied for its potential to treat low-grade intermediate-risk non-muscle invasive bladder cancer, though the exact mechanism of action is not publicly detailed.

Who makes UGN-103?

UGN-103 is being developed by UroGen Pharma Ltd., a biopharmaceutical company traded on NASDAQ under the ticker symbol URGN. The company is conducting a Phase 3 clinical trial to evaluate the drug in patients with low-grade intermediate-risk non-muscle invasive bladder cancer.

What phase is UGN-103 in?

UGN-103 is currently in Phase 3 clinical development. It is an investigational drug, meaning it has not yet been approved by regulatory agencies. The ongoing Phase 3 study is active but not recruiting participants, and it is designed to assess the treatment of low-grade intermediate-risk non-muscle invasive bladder cancer.

What clinical trials is UGN-103 in?

UGN-103 is being evaluated in a single Phase 3 clinical trial registered as NCT06331299. This active, non-recruiting study has an enrollment target of 99 participants and is being conducted in the United States, Bulgaria, Estonia, Georgia, Latvia, Romania, and Spain. The trial is not randomized, double-blind, or controlled.