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padeliporfin VTP

Phase 3

Transitional Cell Cancer of Renal Pelvis and Ureter | Small molecule | Oncology |Icon Plc|Last Updated: Jul 30, 2026

Success Probability

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Trial Design

UNCONTROLLEDDMC
Total Trials1
Total Enrollment89

FDA Designations

No designations recorded

Clinical trial landscape

padeliporfin VTP · 1 trial · 1 indication

Phase 3 1
NCT04620239ENdoluminal LIGHT ActivatED Treatment of Upper Tract Urothelial Cancer (ENLIGHTED) StudyTransitional Cell Cancer of Renal Pelvis and Ureter
ACTIVE NOT_RECRUITING89 Analytics
PHASE3ACTIVE NOT_RECRUITING
ENdoluminal LIGHT ActivatED Treatment of Upper Tract Urothelial Cancer (ENLIGHTED) Study
Transitional Cell Cancer of Renal Pelvis and UreterUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of patients with absence of UTUC tumors in the entire ipsilateral calyces, renal pelvis and ureter
28 +/- 3 days post last treatment

Primary efficacy outcome is the absence of UTUC tumors in the entire ipsilateral calyces renal pelvis and ureter on endoscopic evaluation at the time of Primary Response Evaluation (PRE) (28 +/- 3 days post last treatment) during padeliporfin VTP induction treatment phase. This outcome will be determined dichotomously as either failure or success in achieving complete response. · Complete Response will be defined as absence of disease based on: * absence of visual tumor on endoscopy * no evidence of tumor on biopsy (if feasible) * negative urinary cytology by instrumented collection

Secondary Endpoints

Duration of response at the entire ipsilateral kidney
12 months post PRE
Duration of response at the Treatment Area of the ipsilateral kidney
3, 6, 9, and 12 months post PRE
Overall renal function
6 and 12 months post PRE
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
padeliporfin VTPEXPERIMENTALInduction Treatment phase:1-3 padeliporfin VTP treatments provided 4 weeks (28 +/-3 days) apart. Maintenance Treatment Phase: Repeated maintenance VTP treatments during this period will be provided for patients who show evidence of tumor recurrence that is deemed treatable.

Interventions

NameTypeDescription
padeliporfin VTPDRUGDuring treatment, placement at the target area of an optical light fiber, through the working channel of the ureteroscope. Intravenous administration of padeliporfin at the dose of 3.66 mg/kg infused over 10 minutes. Each target area will be illuminated for 10 minutes.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites18

Inclusion Criteria: * Male and female patients 18 years or older * Able to understand and provide written informed consent and willing to comply with all tests and procedures associated with the study * New or recurrent low-grade, non-invasive UTUC disease * Biopsy-proven disease . A concurrence of...

Countries:United StatesFranceGermanyIsraelSpain
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Recent Changes (Last 90 Days)

MEDIUMJul 30, 2026NCT04620239Status: RECRUITING → ACTIVE_NOT_RECRUITING
MEDIUMJul 30, 2026NCT04620239Status: RECRUITING → ACTIVE_NOT_RECRUITING
LOWMay 26, 2026NCT04620239primaryCompletionDate: changed
LOWMay 24, 2026NCT04620239studyFirstPostDate: changed

Frequently asked questions about padeliporfin VTP

What is padeliporfin VTP used for?

Padeliporfin VTP is an investigational small molecule being studied for the treatment of transitional cell cancer of the renal pelvis and ureter, a type of upper tract urothelial cancer. It is currently in Phase 3 clinical development and has not been approved by regulatory authorities.

What does padeliporfin VTP target?

Padeliporfin VTP is a small molecule that is activated by light in a procedure called vascular targeted photodynamic therapy. The drug is designed to be activated within the tumor to destroy cancer cells, though its specific molecular target has not been disclosed.

Who is developing padeliporfin VTP?

Padeliporfin VTP is being developed by Icon Plc, a company listed on the stock exchange under the ticker ICLR. The drug is currently in Phase 3 clinical trials for the treatment of transitional cell cancer of the renal pelvis and ureter.

What phase is padeliporfin VTP in?

Padeliporfin VTP is in Phase 3 clinical development. It is an investigational drug and has not yet received regulatory approval. The ongoing Phase 3 trial is active but not recruiting participants, with an enrollment target of 89 patients.

What clinical trials is padeliporfin VTP in?

Padeliporfin VTP is being evaluated in a Phase 3 clinical trial with the identifier NCT04620239, known as the ENLIGHTED study. This trial is active but not recruiting and is being conducted in the United States, France, Germany, Israel, and Spain.

Is padeliporfin VTP the same as other treatments for upper tract urothelial cancer?

Padeliporfin VTP is a distinct investigational therapy being studied specifically for transitional cell cancer of the renal pelvis and ureter. It is not known to be the same as any other approved treatment, and its unique mechanism involves light-activated destruction of tumor tissue.