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REGN10597

Phase 1

Melanoma | Small molecule | Oncology |Regeneron Pharmaceuticals, Inc.|Last Updated: Apr 28, 2026

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment240

FDA Designations

No designations recorded

Clinical trial landscape

REGN10597 · 1 trial · 3 indications

Phase 1 1
NCT06413680A First-In Human (FIH) Study to Find Out How Well REGN10597 Medicine Given Alone or in Combination With Cemiplimab Works in Adult Participants Who Have Cancer With Tumors That Have Spread in Their BodyMelanoma
RECRUITING240 Analytics
PHASE1RECRUITING
A First-In Human (FIH) Study to Find Out How Well REGN10597 Medicine Given Alone or in Combination With Cemiplimab Works in Adult Participants Who Have Cancer With Tumors That Have Spread in Their Body
MelanomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence of Dose-Limiting Toxicities (DLTs)
Up to Day 29

Dose escalation

Incidence of Treatment-Emergent Adverse Event (TEAEs)
Approximately 6 Years

Dose escalation

Incidence of Serious Adverse Events (SAEs)
Approximately 6 Years

Dose escalation

Incidence of TEAEs leading to treatment discontinuation
Approximately 6 Years

Dose escalation

Incidence of TEAEs leading to death
Approximately 6 Years

Dose escalation

Number of participants with Grade 3 laboratory abnormalities
Approximately 6 Years

Dose escalation Grade 3 or higher per Common Terminology Criteria for Adverse Events (CTCAE) version 5.0

Objective Response Rate (ORR) per Response Evaluation Criteria In Solid Tumors (RECIST 1.1) criteria by investigator assessment
Approximately 6 Years

Dose expansion

Secondary Endpoints

ORR based on RECIST 1.1 criteria by investigator assessment
Approximately 6 Years
Best Overall Response (BOR) based on RECIST 1.1 criteria
Approximately 6 Years
Duration Of Response (DOR) based on RECIST 1.1 criteria
Approximately 6 Years
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Phase 1: Monotherapy Dose EscalationEXPERIMENTALMultiple Dose Level (DL) Cohorts to identify the Recommended Phase 2 Dose (RP2D)
Phase 2: Monotherapy Dose ExpansionEXPERIMENTALCohort 1: Melanoma participants Cohort 2: Clear-cell Renal-Cell Carcinoma (ccRCC) participants
Phase 1: Combination Dose EscalationEXPERIMENTALMultiple DL Cohorts to identify the RP2D
Phase 2: Combination Dose ExpansionEXPERIMENTALCohort 1: Melanoma participants

Interventions

NameTypeDescription
REGN10597DRUGAdministered per the protocol
CemiplimabDRUGAdministered per the protocol
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites11

Key Inclusion Criteria: Dose escalation cohorts: 1\. Histologically or cytologically confirmed diagnosis of solid malignancy (locally advanced or metastatic) with confirmed progression on standard-of-care therapy. Participants are required to submit archival tissue if it is available Dose expansi...

Countries:United States
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Frequently asked questions about REGN10597

What is REGN10597 used for?

REGN10597 is an investigational small molecule being developed for the treatment of melanoma. It is also being studied in clear-cell renal-cell carcinoma (ccRCC) and advanced solid tumors. The drug is intended for adult participants whose tumors have spread in their body.

Who makes REGN10597?

REGN10597 is being developed by Regeneron Pharmaceuticals, Inc., a biopharmaceutical company traded on the Nasdaq under the ticker symbol REGN. The company is currently conducting a first-in-human study of the drug in the United States.

What phase is REGN10597 in?

REGN10597 is in Phase 1 clinical development. It is an investigational drug and has not been approved by the FDA. The ongoing Phase 1 trial is recruiting participants to evaluate the drug alone or in combination with cemiplimab.

What clinical trials is REGN10597 in?

REGN10597 is being studied in a single Phase 1 clinical trial with the identifier NCT06413680. This first-in-human study is recruiting 240 adult participants in the United States with melanoma, clear-cell renal-cell carcinoma, or advanced solid tumors. The trial is not randomized or double-blinded.

How does REGN10597 work?

REGN10597 is a small molecule therapeutic being investigated for its anti-cancer activity. The specific molecular target of REGN10597 has not been disclosed in the available clinical trial information. The drug is being studied alone and in combination with cemiplimab, an immunotherapy agent.