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GM-CSF

Phase 1

Colorectal Cancer | Monoclonal antibody | Oncology |Pulse Biosciences, Inc|Last Updated: Aug 19, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment16
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01064375Safety Study of DNA Vaccine Delivered by Intradermal Electroporation to Treat Colorectal CancerPHASE1 COMPLETED 16Dec 1, 2009Aug 1, 2016Aug 19, 20221 Sweden
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Study Endpoints
Primary Endpoints
To evaluate the safety and immunogenicity of a DNA immunisation approach where tetwtCEA DNA will be administered in combination with electroporation.
Within 72 weeks after immunisation
Secondary Endpoints
To assess the efficiency of boosting immunological responses to CEA by intradermal administration of tetwtCEA DNA in combination with electroporation in subjects already vaccinated with CEA DNA
Within 72 weeks after immunisation
To compare effects (safety and immunogenicity) of additional adjuvance with GM-CSF
Within 72 weeks after immunsation
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
CEA DNA prime (cohort I)EXPERIMENTAL5 patients, tetwtCEA DNA intradermal delivery with electroporation, not previously vaccinated with CEA66 DNA. Electrical pulses applied to vaccination sites in skin using Derma Vax immediately after DNA administration. One dose of Cyclophosphamide (300 mg/m2) will be given i.v. three days before each vaccination with tetwtCEA DNA.
CEA DNA boost (cohort II)EXPERIMENTAL10 patients, tetwtCEA DNA intradermal delivery with electroporation, previously vaccinated with CEA66 DNA.Electrical pulses applied to vaccination sites in skin using Derma Vax immediately after DNA administration.One dose of Cyclophosphamide (300 mg/m2) will be given i.v. three days before each vaccination with tetwtCEA DNA.
CEA DNA prime + GM-CSF (cohort III)EXPERIMENTAL5 patients, tetwtCEA DNA intradermal delivery with electroporation + GM-CSF, not previously vaccinated with CEA66 DNA.Electrical pulses applied to vaccination sites in skin using Derma Vax immediately after DNA administration.One dose of Cyclophosphamide (300 mg/m2) will be given i.v. three days before each vaccination with tetwtCEA DNA.
Interventions
NameTypeDescription
tetwtCEA DNA (wt CEA with tetanus toxoid Th epitope)BIOLOGICALTwo vaccinations at week 0 and 12. Intradermal administration of 400ug DNA/dose with electroporation
Derma Vax (electroporation device)DEVICEElectrical pulses applied to vaccination sites in skin using Derma Vax immediately after DNA administration
GM-CSFBIOLOGICALGM-CSF will be given for 4 consecutive days starting the day before the vaccination as an intradermal/subcutaneous administration of 150 ug of GM-CSF
CyclophosphamideDRUGOne intravenous dose of 300 mg/m2 will be given three days before each vaccination with tetwtCEA DNA
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Histological confirmed AJCC stage II or III colorectal cancer * Resection of the primary tumour without evidence of remaining macroscopic disease * Allowable standard chemotherapy or radiotherapy in AJCC stage III completed minimum 2 months prior study entry * Patients recruit...

Countries:Sweden
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Competitive Landscape -Colorectal Cancer 263 trials
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