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cemsidomide

Phase 2

Multiple Myeloma | Small molecule | Oncology |C4 Therapeutics, Inc.|Last Updated: Aug 12, 2026

Development status

Highest phase Phase 2
Registered trials 3 across 1 sponsor since Feb 2021

Target and mechanism

Molecular targetIKZF1/3
Target class-Domide (Cereblon)
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials3
Total Enrollment384

FDA Designations

No designations recorded

Clinical trial landscape

cemsidomide · 3 trials · 4 indications

Phase 2 1Phase 1 2
NCT07284758A Study to Evaluate the Efficacy of Cemsidomide + Dexamethasone in Participants With Relapsed/Refractory Multiple MyelomaMultiple Myeloma
RECRUITING100 Analytics
PHASE2RECRUITING
A Study to Evaluate the Efficacy of Cemsidomide + Dexamethasone in Participants With Relapsed/Refractory Multiple Myeloma
Multiple MyelomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Overall response rate (ORR) per International Myeloma Working Group (IMWG) Response Criteria by an Independent Review Committee (IRC)
up to approximately 43 months
Safety and tolerability of cemsidomide in combination with elranatamab
Cycle 1 approximately 28 days

Dose limiting toxicity rate

Phase 1: Safety and tolerability of cemsidomide
Baseline through 30 days after the last dose of study treatment

Percent of subjects with adverse events (AEs) with cemsidomide as a single agent

Phase 1: Safety and tolerability of cemsidomide in combination with dexamethasone
Baseline through 30 days after the last dose of study treatment

Percent of subjects with AEs with cemsidomide in combination with dexamethasone

Phase 1: Maximum tolerated dose (MTD) or recommended Phase 2 dose (RP2D) for cemsidomide
Days 1-28

Percent of subjects with dose-limiting toxicities (DLTs) with cemsidomide as a single agent

Phase 1: MTD or recommended RP2D for cemsidomide in combination with dexamethasone
Days 1-28

Percent of subjects with DLTs with cemsidomide in combination with dexamethasone

Phase 2: Antitumor activity of cemsidomide as a single agent
Baseline through 6 months after the last dose of study treatment, or until disease progression, whichever occurs first

Overall Response Rate (ORR) based on Best Overall Response (BOR), Duration of Response (DOR), and Progression Free Survival (PFS) of cemsidomide

Phase 2: Antitumor activity of cemsidomide in combination with dexamethasone
Baseline through 6 months after the last dose of study treatment, or until disease progression, whichever occurs first

ORR based on BOR, DOR, and PFS of cemsidomide in combination with dexamethasone in subjects with MM based on International Myeloma Working Group (IMWG) criteria

Secondary Endpoints

Duration of response (DoR; IRC assessed)
up to approximately 43 months
Complete response (CR) rate (IRC assessed)
up to approximately 43 months
Time to response (IRC assessed)
up to approximately 43 months
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cemsidomide + Dexamethasone:EXPERIMENTALParticipants receive cemsidomide plus dexamethasone during a 28-day treatment cycle, and will continue to receive treatment until the participant meets one of the discontinuation criteria.
Non-randomized cemsidomide (tablet) plus elranatamab (subcutaneous injection)EXPERIMENTAL -
Phase 1: Arm A - cemsidomideEXPERIMENTALParticipants with r/r NHL or r/r MM will be treated with oral cemsidomide as a single agent administered at different dosages and dosing schedules.
Phase 1: Arm B1 - cemsidomideEXPERIMENTALParticipants with r/r MM will be treated with escalating doses of oral cemsidomide as a single agent administered at different dosages and dosing schedules in each cohort, until the determination of maximum tolerated dose (MTD)/recommended Phase 2 dose (RP2D) or Sponsor discretion.
Phase 1: Arm B2 - cemsidomide in combination with dexamethasoneEXPERIMENTALParticipants with r/r MM will be treated with escalating doses of oral cemsidomide in combination with a fixed dose of oral dexamethasone in each cohort
Phase 1: Arm C - cemsidomideEXPERIMENTALParticipants with r/r NHL will be treated with escalating doses of oral cemsidomide single agent administered according to different dosing schedules in each cohort
Phase 2: Arm 1 - cemsidomideEXPERIMENTALParticipants with r/r MM will be treated with oral cemsidomide single agent
Phase 2: Arm 2 - cemsidomide in combination with dexamethasoneEXPERIMENTALParticipants with r/r MM treated with oral cemsidomide in combination with oral dexamethasone
Phase 2: Arm 3 - CFT7455EXPERIMENTALParticipants with r/r peripheral T-cell lymphoma (PTCL) treated with oral cemsidomide single agent

Interventions

NameTypeDescription
CemsidomideDRUGdosed orally (PO) once a day (QD) 14 days on/14 days off for each 28-day cycle
DexamethasoneDRUGdosed PO once a week (QW) on Days 1, 8, 15, and 22 for each 28-day cycle
ElranatamabBIOLOGICAL• BCMA-CD3 bispecific antibody
Dexamethasone OralDRUGoral dexamethasone \[ ≤75 years old: 40 mg once per week (QW) on days 1, 8, 15, and 22; \>75 Years old: 20 mg QW on days 1, 8, 15, and 22\]
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites21

Inclusion Criteria: 1. Be willing and able to provide signed informed consent for the study. 2. Age ≥ 18 years at the time of signed consent. 3. Subjects must have a documented diagnosis of MM and measurable disease at enrollment. 4. Received at least 3 prior anti-myeloma regimens (for a minimum of...

Countries:United StatesUnited Kingdom
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Recent Changes (Last 90 Days)

LOWAug 12, 2026NCT07280013lastUpdatePostDate: changed
LOWAug 12, 2026NCT07280013lastUpdatePostDate: changed
LOWAug 6, 2026NCT07284758lastUpdatePostDate: changed
LOWAug 6, 2026NCT07284758lastUpdatePostDate: changed
LOWJul 14, 2026NCT07280013lastUpdatePostDate: changed
LOWJul 14, 2026NCT07280013lastUpdatePostDate: changed
LOWJul 2, 2026NCT07284758lastUpdatePostDate: changed
LOWJul 2, 2026NCT07284758lastUpdatePostDate: changed
LOWJul 2, 2026NCT07284758lastUpdatePostDate: changed
LOWJul 2, 2026NCT07284758lastUpdatePostDate: changed

Frequently asked questions about cemsidomide

What is cemsidomide used for?

Cemsidomide is an investigational small molecule being studied for the treatment of multiple myeloma, a cancer of plasma cells in the bone marrow. It is being evaluated in relapsed or refractory multiple myeloma, meaning disease that has returned or stopped responding to prior therapy. It is also being studied in non-Hodgkin's lymphoma.

What does cemsidomide target?

Cemsidomide targets IKZF1 and IKZF3, two transcription factors also known as Ikaros and Aiolos. It belongs to the -domide class of cereblon-binding agents, meaning it works through the cereblon E3 ligase pathway to promote degradation of these targets. This mechanism is designed to disrupt myeloma cell survival and growth.

Who is developing cemsidomide?

Cemsidomide is being developed by C4 Therapeutics, Inc., a biopharmaceutical company traded on the Nasdaq under the ticker CCCC. The company is advancing the asset in oncology, with multiple myeloma as its lead indication.

What phase is cemsidomide in?

Cemsidomide is in Phase 2 clinical development. It is an investigational agent and has not been approved by the FDA. The Phase 2 study is evaluating cemsidomide in combination with dexamethasone, while earlier-stage studies are testing it in additional combination regimens.

What clinical trials is cemsidomide in?

Cemsidomide is being studied in three clinical trials. NCT07284758 is a Phase 2 study of cemsidomide plus dexamethasone in relapsed or refractory multiple myeloma, recruiting in the United States and United Kingdom. NCT07280013 is a Phase 1 study combining cemsidomide with elranatamab. NCT04756726 is a Phase 1 study in non-Hodgkin's lymphoma and multiple myeloma.

How many patients are enrolled in cemsidomide trials?

Across the three cemsidomide clinical trials, total planned enrollment is 384 participants. The Phase 2 study NCT07284758 plans to enroll 100 participants, the Phase 1 elranatamab combination study NCT07280013 plans 60, and the Phase 1 study NCT04756726 plans 224. All three trials are active, and none have been completed.