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CP-675,206

Phase 3

Melanoma | Small molecule | Oncology |AstraZeneca PLC|Last Updated: Jul 2, 2012

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment740
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00257205CP-675,206 Versus Either Dacarbazine Or Temozolomide In Patients Without Prior TherapyPHASE3 COMPLETED 655Mar 1, 2006Aug 1, 2010Jul 2, 2012143 United States, Argentina +19
NCT00431275Study to Compare Two Formulations of CP-675,206 Monoclonal AntibodyPHASE1 COMPLETED 85Jun 1, 2006Feb 1, 2008Jun 6, 20128 United States
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Study Endpoints
Primary Endpoints
overall survival
August 2010
Pharmacokinetics: maximum plasma concentration of CP-675,206
1 hour
Pharmacokinetics: AUC, defined as the area under the concentration -time curve
Time 0 to Day 85
Secondary Endpoints
adverse events
1 year
PFS at 6 months
6 months
objective tumor response
1 year
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
BACTIVE_COMPARATORChoice of one or the other Dacarbazine or Temozolomide(CP-675,206) (choice)
AEXPERIMENTAL -
Commercial FormulationEXPERIMENTALCommercial Formulation
Current FormulationEXPERIMENTALCurrent Formulation
Interventions
NameTypeDescription
dacarbazineDRUGdecarbazine 1000 mg/m2 IV Q 21 days x 12
CP-675,206DRUGCP-675,206 15 mg/kg IV Q 90 days x 4
temozolomideDRUGtemozolomide 200 mg/m2 orally on Days 1-5 every 28 days x 12
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites143

Inclusion Criteria: * Surgically incurable melanoma, either Stage IV or IIIC with N3 status for regional lymph nodes and in-transit or satellite lesions. * Serum lactic acid dehydrogenase (LDH) \<= 2 x ULN * ECOG performance status of 0 or 1 Exclusion Criteria: * Received any systemic therapy for...

Countries:United StatesArgentinaAustraliaAustriaBelgiumCanadaFranceGermanyGreeceIsraelItalyMexicoNetherlandsPolandRussiaSlovakiaSouth AfricaSpainSwedenSwitzerlandUnited Kingdom
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Competitive Landscape -Melanoma 127 trials
CompanyTickerTrialsLead PhaseDrugs
Merck & Co., Inc.MRK6PHASE3Intismeran autogene, Pembrolizumab, pembrolizumab, Pembrolizumab Berahyaluronidase alfa
Bristol-Myers Squibb CompanyBMY7PHASE3Nivolumab, Nivolumab + Relatlimab, rHuPH20, Relatlimab, relatlimab+nivolumab
Regeneron Pharmaceuticals, Inc.REGN8PHASE3Fianlimab, Cemiplimab, Pembrolizumab, fianlimab, cemiplimab
Pfizer Inc.PFE4PHASE3Encorafenib, Binimetinib, Pembrolizumab, PF-08046049, PF-07799933
IDEAYA Biosciences, Inc.IDYA4PHASE3Darovasertib, IDE196, Crizotinib, Pembrolizumab, Ipilimumab
Iovance Biotherapeutics IncIOVA6PHASE3Lifileucel plus Pembrolizumab, Pembrolizumab with Optional Crossover Period, Lifileucel, LN-145/LN-144, Cyclophosphamide
Replimune Group, Inc.REPL5PHASE3Vusolimogene Oderparepvec, Nivolumab, Pembrolizumab, Single-agent chemotherapy, RP1
Amgen Inc.AMGN1PHASE3ABP 206, Nivolumab
Immunocore Holdings Plc Shs Sponsored American Depositary Shares Repr 1 ShIMCR3PHASE3Tebentafusp, Brenetafusp, Nivolumab
Immatics N.V.IMTX2PHASE3IMA203, nivolumab plus relatlimab, lifileucel, pembrolizumab, ipilimumab
Aura Biosciences IncAURA4PHASE3Bel-sar
Novartis AG Sponsored ADRNVS6PHASE2LXH254, LTT462, Trametinib, Ribociclib, DYP688
IO Biotech, Inc.IOBT2PHASE3IO102-IO103, Pembrolizumab, Pembrolizumab KEYTRUDA
Erasca, Inc.ERAS1PHASE3Naporafenib, Dacarbazine, Temozolomide, Trametinib
AstraZeneca PLCAZN3PHASE2Ceralasertib, Durvalumab, AZD6750, rilvegostomig, Trastuzumab deruxtecan
Eikon Therapeutics, Inc.EIKN2PHASE2EIK1001, Pembrolizumab, Association atezolizumab + BDB001 + RT
Moderna, Inc.MRNA1PHASE2mRNA-4157, Pembrolizumab
Genmab A/S Sponsored ADRGMAB2PHASE2Acasunlimab, Pembrolizumab, GEN1042, Cisplatin, Carboplatin
Agenus Inc.AGEN1PHASE2Botensilimab, Balstilimab
ImmunityBio IncIBRX1PHASE2N-803 + Pembrolizumab
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