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N-Plate/ romiplostim

Phase 2

Myelodysplastic Syndromes | Small molecule | Oncology |Amgen Inc.|Last Updated: Aug 16, 2023

Success Probability

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Trial Design

CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment77

FDA Designations

No designations recorded

Clinical trial landscape

N-Plate/ romiplostim · 1 trial · 1 indication

Phase 2 1
NCT02335268Validation of a Predictive Model of Response to Romiplostim in Patients With IPSS Low or Intermediate-1 Risk MDS and ThrombocytopeniaMyelodysplastic Syndromes
COMPLETED77 Analytics
PHASE2COMPLETED
Validation of a Predictive Model of Response to Romiplostim in Patients With IPSS Low or Intermediate-1 Risk MDS and Thrombocytopenia
Myelodysplastic SyndromesUnlock trial analytics

Study Endpoints

Primary Endpoints

Hematologic Improvement of Platelets (HI-P) After 4 Months on Therapy
after 4 months on therapy (week 16)

The primary efficacy endpoint was the rate of HI-P defined as an absolute increase of platelet count to ≥ 30/nL for patients starting at \> 20/nL or an increase of platelets from \< 20/nL to \> 20/nL and by at least 100%, according to IWG 2006 criteria lasting for ≥ 8 weeks after at least 16 Weeks of romiplostim treatment.

Secondary Endpoints

Cumulative Hematologic Improvement
week 16
The Incidence of Disease Progression to Higher Stage MDS or AML
week 16
Increase of Peripheral Blasts During Therapy
week 16
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Group 1EXPERIMENTALStratification into group 1 if Score (Baseline-TPO Level and previous thrombocyte transfusions) are +3 TPO based model to predict subsequent response to romiplostim in MDS patients with IPSS Low/Int-1 according to a model developed by Sekeres et. al./ BJH 2014
Group 2EXPERIMENTALStratification into group 2 if Score (Baseline-TPO Level and previous thrombocyte transfusions) are -1 or -2 TPO based model to predict subsequent response to romiplostim in MDS patients with IPSS Low/Int-1 according to a model developed by Sekeres et. al./ BJH 2014
Group 3EXPERIMENTALStratification into group 3 if Score (Baseline-TPO Level and previous thrombocyte transfusions) are -6 TPO based model to predict subsequent response to romiplostim in MDS patients with IPSS Low/Int-1 according to a model developed by Sekeres et. al./ BJH 2014

Interventions

NameTypeDescription
N-Plate / romiplostimDRUGmedical intervention in 3 patient groups (MDS patients with IPSS Low/Int-1) that are stratified according to their baseline TPO-Level and previous transfusions
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites36

Inclusion Criteria: * Subjects must meet the following inclusion/exclusion criteria to be eligible for the study. * Must understand and voluntarily sign the informed consent form * Age older 18 years at the time of signing the informed consent form * Must be able to adhere to the study visit schedu...

Countries:FranceGermany
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Frequently asked questions about N-Plate/ romiplostim

What is N-Plate (romiplostim) used for?

N-Plate (romiplostim) is used for Myelodysplastic Syndromes (MDS), specifically in patients with IPSS low or intermediate-1 risk MDS and thrombocytopenia. It is being developed by Amgen Inc. (AMGN) and is currently in Phase 2 clinical development as an investigational therapy.

What does N-Plate (romiplostim) target?

N-Plate (romiplostim) is a small molecule developed by Amgen Inc. (AMGN) for the treatment of Myelodysplastic Syndromes. The specific molecular target has not been disclosed in the available information, so its mechanism of action is not detailed here.

Who makes N-Plate (romiplostim)?

N-Plate (romiplostim) is developed by Amgen Inc., a biopharmaceutical company traded on NASDAQ under the ticker AMGN. The drug is being investigated for use in Myelodysplastic Syndromes and is currently in Phase 2 clinical trials.

What phase is N-Plate (romiplostim) in?

N-Plate (romiplostim) is in Phase 2 clinical development. It is an investigational drug, not yet approved by regulatory authorities. The ongoing development focuses on Myelodysplastic Syndromes, with a completed Phase 2 trial that enrolled 77 participants.

What clinical trials is N-Plate (romiplostim) in?

N-Plate (romiplostim) has one completed Phase 2 trial, NCT02335268, titled "Validation of a Predictive Model of Response to Romiplostim in Patients With IPSS Low or Intermediate-1 Risk MDS and Thrombocytopenia." The trial enrolled 77 participants in France and Germany and was a controlled, biomarker-selected study.

Is N-Plate (romiplostim) the same as romiplostim?

Yes, N-Plate (romiplostim) is the same as romiplostim. The drug is known by both names, with romiplostim being the generic name and N-Plate a brand name. It is being developed by Amgen Inc. (AMGN) for Myelodysplastic Syndromes.