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LY3410738

Phase 1

Acute Myeloid Leukemia (AML) | Small molecule | Oncology |Eli Lilly and Company|Last Updated: Jul 22, 2026

Target and mechanism

Molecular targetIDH
Target classGene
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment260

FDA Designations

No designations recorded

Clinical trial landscape

LY3410738 · 4 trials · 9 indications

Phase 1 4
NCT06181084A Study Comparing Different Formulations of LY3410738 in Healthy Adult ParticipantsHealthy
COMPLETED60 Analytics
NCT06181045A Study of LY3410738 in Healthy Adult ParticipantsHealthy
COMPLETED42 Analytics
NCT04603001Study of Oral LY3410738 in Patients With Advanced Hematologic Malignancies With IDH1 or IDH2 MutationsAcute Myeloid Leukemia (AML)
ACTIVE NOT_RECRUITING260 Analytics
NCT04521686Study of LY3410738 Administered to Patients With Advanced Solid Tumors With IDH1 or IDH2 MutationsCholangiocarcinoma
ACTIVE NOT_RECRUITING200 Analytics
PHASE1COMPLETED
A Study Comparing Different Formulations of LY3410738 in Healthy Adult Participants
HealthyUnlock trial analytics
PHASE1COMPLETED
A Study of LY3410738 in Healthy Adult Participants
HealthyUnlock trial analytics
PHASE1ACTIVE NOT_RECRUITING
Study of Oral LY3410738 in Patients With Advanced Hematologic Malignancies With IDH1 or IDH2 Mutations
Acute Myeloid Leukemia (AML)Unlock trial analytics
PHASE1ACTIVE NOT_RECRUITING
Study of LY3410738 Administered to Patients With Advanced Solid Tumors With IDH1 or IDH2 Mutations
CholangiocarcinomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Pharmacokinetics (PK): Area Under the Concentration-Time Curve from Hour 0 to the Last Measurable Concentration (AUC0-tlast) of LY3410738 Tablets Versus Capsules
Predose up to 48 hours postdose

PK: AUC0-tlast of LY3410738 Tablets Versus Capsules

PK: Area Under the Concentration from Hour 0 Extrapolated to Infinity (AUC0-∞) of LY3410738 Tablets Versus Capsules
Predose up to 48 hours postdose

PK: AUC0-∞ of LY3410738 Tablets Versus Capsules

PK: Maximum Observed Plasma Concentration (Cmax) of LY3410738 Tablets Versus Capsules
Predose up to 48 hours postdose

PK: Cmax of LY3410738 Tablets Versus Capsules

PK: AUC0-tlast of LY3410738 After Standard Low-Fat Meal
Predose up to 48 hours postdose
PK: AUC0-∞ of LY3410738 After Standard Low-Fat Meal
Predose up to 48 hours postdose
PK: Cmax of LY3410738 After Standard Low-Fat Meal
Predose up to 48 hours postdose
PK: AUC0-tlast of LY3410738 after Esomeprazole oral dose in the Fasted State
Predose up to 48 hours postdose
PK: AUC0-∞ of LY3410738 after Esomeprazole oral dose in the Fasted State
Predose up to 48 hours postdose
PK: Cmax of LY3410738 after Esomeprazole oral dose in the Fasted State
Predose up to 48 hours postdose
PK: AUC0-tlast of LY3410738 after Esomeprazole oral dose in the Fed State
Predose up to 48 hours postdose
PK: AUC0-∞ of LY3410738 after Esomeprazole oral dose in the Fed State
Predose up to 48 hours postdose
PK: Cmax of LY3410738 after Esomeprazole oral dose in the Fed State
Predose up to 48 hours postdose
Number of Participants with One or More Treatment Emergent Adverse Events (TEAEs) and Serious Adverse Event(s) (SAEs) Considered by the Investigator to be Related to Study Drug Administration
Baseline through 53 days

A summary of TEAEs, SAEs and other non-serious adverse events (AEs), regardless of causality, will be reported in the Reported Adverse Events module

To determine the maximum tolerated dose (MTD)/recommended Phase 2 dose (RP2D)
Up to 30 months

For Dose Escalation

To assess the activity of LY3410738 as measured by the overall response rate (ORR) per the Investigator assessment
Up to 30 months

For Dose Expansion

Recommended Phase 2 Dose (RP2D)
Up to 24 months

Secondary Endpoints

Pharmacokinetics (PK): Area Under the Concentration-time Curve, From Time 0 to 24 Hours Post-dose (AUC0-24) of LY3410738
Pre-dose up to 24 hours post-dose
PK: Area Under the Concentration-time Curve, From Time 0 to the Last Measurable Concentration (AUC0-t) of LY3410738
Pre-dose up to 48 hours post-dose
PK: Maximum Observed Plasma Concentration (Cmax) of LY3410738
Pre-dose up to 48 hours post-dose
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelCROSSOVER
PurposeBASIC_SCIENCE

Treatment Arms

ArmTypeDescription
Group 1: Tablet versus CapsuleEXPERIMENTALTreatment A: LY3410738 capsule on Day 1 as a single oral dose in the morning following a fast of at least 10 hours prior to and 4 hours after dosing. Treatment B: LY3410738 tablet on Day 4 as a single oral dose in the morning 10 hours prior to and 4 hours after dosing.
Group 2: Food Effect Comparison GroupEXPERIMENTALTreatment B: LY3410738 table on Day 1 as a single oral dose in the morning following a fast of at least 10 hours prior to and 4 hours after dosing. Treatment C: LY3410738 table on Day 4 as a single oral dose in the morning 30 minutes after starting a standard low-fat meal.
Group 3: Potential of Hydrogen (pH) Effect Fasted GroupEXPERIMENTALTreatment B: LY3410738 table on Day 1 as a single oral dose in the morning following a fast of at least 10 hours prior to and 4 hours after dosing. Treatment D: Esomeprazole single oral dose once daily (QD) in the morning on Days 4 through 8 in fasted state followed by a standard low-fat meal. On Day 9, Esomeprazole a single oral dose followed by LY3410738 tablet as a single oral dose in the morning, following a fast of at least 10 hours prior to and 4 hours after esomeprazole and LY3410738 coadministration.
Group 4: pH Effect Fed GroupEXPERIMENTALTreatment C: LY3410738 table on Day 1 as a single oral dose in the morning 30 minutes after starting a standard low-fat meal. Treatment E: Esomeprazole as a single oral dose QD in the morning on Days 4 through 8, in fasted state followed by a standard low-fat meal. On Day 9, Esomeprazole as a single oral dose followed by a LY3410738 tablet in the morning in fed state standard low-fat meal.
Cohort 1 (Treatment A): LY3410738EXPERIMENTALSingle oral dose of LY3410738 or placebo administered as over-encapsulated capsule formulation.
Cohort 2 (Treatment B): LY3410738PLACEBO_COMPARATORSingle oral dose of LY3410738 or placebo administered as over-encapsulated capsule formulation.
Cohort 3 (Treatment C): LY3410738EXPERIMENTALSingle oral dose of LY3410738 or placebo administered as over-encapsulated capsule or tablet formulation.
Cohort 4 (Treatment D): LY3410738EXPERIMENTALSingle oral dose of LY3410738 or placebo administered as over-encapsulated capsule or tablet formulation.
Cohort 5 (Treatment E): LY3410738EXPERIMENTALSingle oral dose of LY3410738 or placebo administered as over-encapsulated capsule or tablet formulation.
Cohort 6 (Treatment F): LY3410738EXPERIMENTALSingle oral dose of LY3410738 or placebo administered as over-encapsulated capsule or tablet formulation.
Cohort 7 (Treatment G): LY3410738EXPERIMENTALSingle oral dose of LY3410738 or placebo administered as over-encapsulated capsule or tablet formulation.
Dose Escalation Arm A (Monotherapy)EXPERIMENTALPatients not requiring a strong cytochrome P450 3A4 (CYP3A4) inhibitor.
Dose Escalation Arm B (Monotherapy)EXPERIMENTALPatients requiring a strong CYP3A4 inhibitor for active management or prevention of a lifethreatening condition, such as an azole administered to prevent invasive fungal infection.
Dose Escalation Arm C (LY3410738, Venetoclax, and Azacitidine)EXPERIMENTALPatients with no prior venetoclax therapy and not requiring a strong CYP3A4 inhibitor for active treatment within 7 days of starting LY3410738.
Cohort 1EXPERIMENTALPatients with relapsed/refractory (R/R) AML harboring an IDH1 R132 mutation who have received a prior IDH inhibitor.
Cohort 2EXPERIMENTALPatients with R/R AML harboring an IDH1 R132 mutation who have not received a prior IDH inhibitor.
Cohort 3EXPERIMENTALPatients with R/R MDS, chronic myelomonocytic leukemia (CMML) or other advanced hematologic malignancy harboring an IDH1 R132 mutation.
Cohort 4EXPERIMENTALPatients with R/R AML, MDS, CMML or other advanced hematologic malignancy harboring IDH2 mutations.
Cohort 5EXPERIMENTALPatients with newly diagnosed AML, R/R AML, or other advanced hematologic malignancy harboring IDH1 and/or IDH2 mutations with no prior venetoclax therapy. Strong CYP3A4 inhibitor allowed but not required.
LY3410738EXPERIMENTALPhase 1 dose escalation - Multiple doses of LY3410738
LY3410738 alone or in combination with gemcitabine and cisplatin or in combination with durvalumabEXPERIMENTALPhase 1 dose expansion - The maximum tolerated dose (MTD)/recommended Phase 2 dose (RP2D) of LY3410738 alone or in combination with gemcitabine plus cisplatin or in combination with durvalumab

Interventions

NameTypeDescription
LY3410738DRUGAdministered orally.
EsomeprazoleDRUGAdministered orally.
PlaceboDRUGAdministered orally.
VenetoclaxDRUGOral venetoclax
AzacitidineDRUGSubcutaneous or intravenous azacitidine
GemcitabineDRUGIntravenous gemcitabine
CisplatinDRUGIntravenous cisplatin
DurvalumabDRUGIntravenous durvalumab
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Eligibility Criteria

Age Range18 Years to 55 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria: * Must have Body mass index (BMI) within the range of 18.0 to 32.0 kilograms per square meter (kg/m\^2), inclusive. * Male and female participants in good health, determined by no clinically significant findings from medical history, 12-lead Electrocardiogram (ECG), vital sign m...

Countries:United StatesAustraliaBelgiumCanadaFinlandFranceGermanyIsraelSingaporeSouth KoreaSpainTaiwanHong KongJapan
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Recent Changes (Last 90 Days)

MEDIUMJul 22, 2026NCT04521686Completion: 2026-11 → 2027-05
MEDIUMJul 22, 2026NCT04603001Completion: 2026-11 → 2027-05
MEDIUMJul 22, 2026NCT04521686Completion: 2026-11 → 2027-05
MEDIUMJul 22, 2026NCT04603001Completion: 2026-11 → 2027-05
MEDIUMJul 8, 2026NCT04521686Completion: 2026-05 → 2026-11
MEDIUMJul 8, 2026NCT04521686Completion: 2026-05 → 2026-11
MEDIUMJul 2, 2026NCT04603001Completion: 2026-05 → 2026-11
MEDIUMJul 2, 2026NCT04603001Completion: 2026-05 → 2026-11
MEDIUMJul 2, 2026NCT04603001Completion: 2026-05 → 2026-11

Frequently asked questions about LY3410738

What is LY3410738 used for?

LY3410738 is an investigational small molecule being studied for the treatment of cancers with IDH1 or IDH2 mutations, including acute myeloid leukemia (AML), cholangiocarcinoma, and other advanced solid tumors and hematologic malignancies. It is currently in Phase 1 clinical trials and is not yet approved by the FDA.

What does LY3410738 target?

LY3410738 targets IDH, which stands for isocitrate dehydrogenase, a gene that can be mutated in certain cancers. By targeting IDH1 and IDH2 mutations, the drug aims to interfere with cancer cell growth. It is being studied in patients whose tumors carry these specific genetic alterations.

Who makes LY3410738?

LY3410738 is being developed by Eli Lilly and Company, a pharmaceutical company listed on the stock exchange under the ticker symbol LLY. The drug is currently in Phase 1 clinical development for oncology indications.

What phase is LY3410738 in?

LY3410738 is in Phase 1 clinical trials. It is an investigational drug, meaning it has not been approved by regulatory authorities such as the FDA. All of its clinical studies are early-stage, focusing on safety, tolerability, and dosing in patients with IDH-mutated cancers.

What clinical trials is LY3410738 in?

LY3410738 has been studied in several Phase 1 trials. NCT04521686 is an active trial in advanced solid tumors with IDH1 or IDH2 mutations. NCT04603001 is an active trial in hematologic malignancies like AML. NCT06181045 and NCT06181084, both completed, evaluated the drug in healthy participants.

Is LY3410738 the same as other IDH inhibitors?

LY3410738 is a distinct investigational drug developed by Eli Lilly. It targets IDH1 and IDH2 mutations, similar to other IDH inhibitors, but it is a unique chemical entity. No alternative names for LY3410738 have been disclosed in clinical trial registrations.