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REM-422

Phase 1

Myelodysplastic Syndromes | Small molecule | Oncology |cbdMD, Inc.|Last Updated: Apr 23, 2025

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment100

FDA Designations

No designations recorded

Clinical trial landscape

REM-422 · 1 trial · 4 indications

Phase 1 1
NCT06297941Study of REM-422 in Patients With AML or Higher Risk MDSMyelodysplastic Syndromes
RECRUITING100 Analytics
PHASE1RECRUITING
Study of REM-422 in Patients With AML or Higher Risk MDS
Myelodysplastic SyndromesUnlock trial analytics

Study Endpoints

Primary Endpoints

Frequency and severity of Treatment Emergent Adverse Events (TEAEs)
24 months

Frequency and severity of Treatment Emergent Adverse Events (TEAEs) will be evaluated according to the NCI-CTCAE version 5.0 and number of participants with Dose Limiting Toxicities will be assessed to determine Safety and Tolerability of REM-422 from the date of randomization until the date of first documented progression or date of death from any cause, whichever came first, assessed up to approximately 24 months.

Maximum Tolerated Dose (MTD) and/or Recommended Phase 2 Dose (RP2D)
Assessed at the end of Cycle 1 (each cycle is 28 days) for each participant for approximately 24 months

Frequency and severity of Treatment Emergent Adverse Events (TEAEs) will be evaluated according to the NCI-CTCAE version 5.0 and the number of participants with Dose Limiting Toxicities will be assessed from the date of first dose of REM-422 until the date of first documented progression or date of death from any cause, whichever came first, assessed up to approximately 24 months

Secondary Endpoints

AML: Rate of Complete Response (remission) (CR)
24 months
AML: Rate of CR with partial hematologic recovery (CRh)
24 months
AML: Duration of CR
24 months
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
REM-422EXPERIMENTALDose Escalation: Participants will receive escalating doses of REM-422 to determine Maximum Tolerated Dose (MTD) and/or Recommended Phase 2 Dose (RP2D)-422, oral capsule administered once daily Dose Expansion: Participants will receive REM-422 at the identified RP2D Treatment will continue until disease progression, therapy intolerance, or participant withdrawal Safety evaluation will continue until 30 days of last administration of REM-422

Interventions

NameTypeDescription
REM-422DRUGREM-422 is a first in class, small molecule mRNA inhibitor that reduces expression of the MYB transcription factor REM-422 will be administered orally once daily
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites9

Inclusion Criteria: 1. Be able to provide informed consent. 2. Be 18 or older at the time of informed consent. 3. Disease criteria: Histologically confirmed diagnosis of either: 1. R/R AML, defined as relapse after transplantation, second or later relapse, refractory to initial induction or ...

Countries:United StatesFrance
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Frequently asked questions about REM-422

What is REM-422 used for?

REM-422 is an investigational small molecule being developed for the treatment of Myelodysplastic Syndromes (MDS), specifically higher risk MDS, as well as Acute Myeloid Leukemia (AML) and refractory AML. It is currently in Phase 1 clinical development for these oncology indications.

Who is developing REM-422?

REM-422 is being developed by cbdMD, Inc., a company traded on the NYSE American under the ticker symbol YCBD. The drug is currently in Phase 1 clinical trials for the treatment of Myelodysplastic Syndromes and Acute Myeloid Leukemia.

What phase is REM-422 in?

REM-422 is currently in Phase 1 clinical development. It is an investigational drug and has not been approved by the FDA. The ongoing Phase 1 trial is actively recruiting participants to evaluate the drug in patients with AML or higher risk MDS.

What clinical trials is REM-422 in?

REM-422 is being studied in a Phase 1 clinical trial with the identifier NCT06297941, titled "Study of REM-422 in Patients With AML or Higher Risk MDS." This trial is currently recruiting and aims to enroll approximately 100 participants in the United States and France.

Is REM-422 a targeted therapy?

REM-422 is a small molecule being developed for the treatment of Myelodysplastic Syndromes and Acute Myeloid Leukemia. The clinical trial for REM-422 uses biomarker-selected patient populations, indicating that the drug may target specific molecular characteristics, though the specific molecular target has not been disclosed.