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SAR113244

Phase 1

Systemic Lupus Erythematosus | Small molecule | Immunology |Sanofi|Last Updated: May 2, 2016

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindCONTROLLEDDMC
Total Trials1
Total Enrollment21
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02321709Multiple Ascending Dose Study To Assess The Safety Profile Of SAR113244 Versus Placebo In Lupus Male And Female PatientsPHASE1 COMPLETED 21Nov 1, 2014Mar 1, 2016May 2, 20161 Germany
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Study Endpoints
Primary Endpoints
Number of participants with adverse events and treatment-emergent adverse events
Up to 16 weeks after inclusion
Change in physical examination, body weight, vital signs and laboratory parameters
Up to 16 weeks after inclusion
Safety and tolerability (erythema, swelling, degree of itching, and present pain intensity at injection site by measuring diameter and qualitative assessment)
Up to 16 weeks after inclusion
Secondary Endpoints
Assessment of pharmacokinetic parameter - maximum concentration (Cmax)
Up to D113 after inclusion
Assessment of pharmacokinetic parameter - time of maximum concentration (Tmax)
Up to D113 after inclusion
Assessment of pharmacokinetic parameter - area under curve 0-4 weeks (AUC0-4w)
Up to D113 after inclusion
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeBASIC_SCIENCE
Treatment Arms
ArmTypeDescription
SAR113244 cohort 1EXPERIMENTALTwo administrations of dosage 1 SAR113244 or placebo subcutaneous dose (Q4 weeks)
SAR113244 cohort 2EXPERIMENTALTwo administrations of dosage 2 SAR113244 or placebo subcutaneous dose (Q4 weeks)
SAR113244 cohort 3EXPERIMENTALTwo administrations of dosage 3 SAR113244 or placebo subcutaneous dose (Q4 weeks)
Interventions
NameTypeDescription
SAR113244DRUGPharmaceutical form:solution for injection Route of administration: subcutaneous
placeboDRUGPharmaceutical form:solution for injection Route of administration: subcutaneous
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion criteria: * Male or female patients, between 18 and 75 years of age, inclusive. * Clinical diagnosis of systemic lupus erythematosus (SLE) by American College Rheumatology criteria. * Autoantibody-posititve. * On active and stable SLE disease. Exclusion criteria: * Pregnant and nursing....

Countries:Germany
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