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Farnesyl Protein Transferase Inhibitor

Phase 1

Leukemia | Small molecule | Oncology |Merck & Company, Inc.|Last Updated: Jun 17, 2015

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment132

FDA Designations

No designations recorded

Clinical trial landscape

Farnesyl Protein Transferase Inhibitor · 2 trials · 6 indications

Phase 1 2
NCT00034684Study of Farnesyl Protein Transferase Inhibitor (FPTI) in Patients With Leukemia (Study P00701)Leukemia
COMPLETED132 Analytics
NCT00040547Farnesyl Protein Transferase Inhibitor (FPTI) in Combination With Docetaxel in Advanced Solid Tumors (Study P01964)(COMPLETED)Neoplasms
COMPLETED29 Analytics
PHASE1COMPLETED
Study of Farnesyl Protein Transferase Inhibitor (FPTI) in Patients With Leukemia (Study P00701)
LeukemiaUnlock trial analytics
PHASE1COMPLETED
Farnesyl Protein Transferase Inhibitor (FPTI) in Combination With Docetaxel in Advanced Solid Tumors (Study P01964)(COMPLETED)
NeoplasmsUnlock trial analytics

Study Endpoints

Primary Endpoints

Adverse Events
Laboratory Tests
ECG

Secondary Endpoints

Physical Exam
Pharmacokinetics
Tumor Response
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Interventions

NameTypeDescription
Farnesyl Protein Transferase InhibitorDRUG -
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo

Inclusion Criteria: * Pathologically documented chronic myelogenous leukemia in blast crisis, myelodysplasia, acute myelogenous leukemia, or acute lymphocytic leukemia. * Life expectancy of 12 weeks or greater. * ECOG Performance Status less than or equal to 2. * Meets protocol requirements for spe...

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Competitive Landscape -Leukemia 327 trials

Top 20 of 63 competitors

CompanyTickerTrialsLead PhaseDrugs
Amgen Inc.AMGN8PHASE3Blinatumomab, Low-intensity chemotherapy regimen
Eli Lilly and CompanyLLY9PHASE3Pirtobrutinib, Idelalisib, Bendamustine, Rituximab
BeOne Medicines Ltd. Sponsored ADRONC13PHASE3Sonrotoclax, Zanubrutinib, Venetoclax, Obinutuzumab
AbbVie, Inc.ABBV24PHASE3Venetoclax
AstraZeneca PLCAZN18PHASE3Acalabrutinib, Rituximab, Chlorambucil
Merck & Co., Inc.MRK7PHASE3Nemtabrutinib, Fludarabine, Cyclophosphamide, Bendamustine, Rituximab
Johnson & JohnsonJNJ12PHASE3Ibrutinib, Venetoclax, Chlorambucil, Obinutuzumab
Novartis AG Sponsored ADRNVS21PHASE3Imatinib, Nilotinib, Bosutinib, Dasatinib, Asciminib
Kura Oncology, Inc.KURA5PHASE3Ziftomenib, Venetoclax, Azacitidine, Daunorubicin, Cytarabine
Nurix Therapeutics, Inc.NRIX5PHASE3NX-5948, Pirtobrutinib
Syndax Pharmaceuticals IncSNDX4PHASE3Revumenib, Intensive Chemotherapy Regimen
Takeda Pharmaceutical Co. Ltd. Sponsored ADRTAK1PHASE3Ponatinib, Imatinib, Vincristine, Dexamethasone, Cytarabine
SELLAS Life Sciences Group, Inc.SLS1PHASE3Galinpepimut-S, Azacitidine, Venetoclax, Decitabine, Cytarabine
Grifols, S.A. Sponsored ADR Class BGRFS1PHASE3Xembify
Bristol-Myers Squibb CompanyBMY7PHASE2Azacitidine
Pfizer Inc.PFE6PHASE2Gemtuzumab ozogamicine- Cytarabine- Gilteritinib
Ascentage Pharma Group International Unsponsored ADRAAPG11PHASE3Olverembatinib
Tango Therapeutics, Inc.TNGX7PHASE3AG-120, Azacitidine
Incyte CorporationINCY6PHASE2Ruxolitinib
Actinium Pharmaceuticals, Inc. (Delaware)ATNM2PHASE3Iomab-B, Conventional Care
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Frequently asked questions about Farnesyl Protein Transferase Inhibitor

What is Farnesyl Protein Transferase Inhibitor used for?

Farnesyl Protein Transferase Inhibitor is an investigational small molecule being studied for the treatment of leukemia and neoplasms. It has been evaluated in patients with leukemia, myelodysplastic syndromes, chronic myeloid leukemia in blast crisis, lymphocytic leukemia, and advanced solid tumors. The drug is still in clinical development and is not approved.

Who makes Farnesyl Protein Transferase Inhibitor?

Farnesyl Protein Transferase Inhibitor is being developed by Merck & Company, Inc., which trades under the ticker symbol MRK. The company has sponsored clinical trials of this investigational oncology drug.

What phase is Farnesyl Protein Transferase Inhibitor in?

Farnesyl Protein Transferase Inhibitor is in Phase 1 clinical development. Two Phase 1 trials have been completed, one in leukemia and related conditions and another in advanced solid tumors. The drug remains investigational and has not been approved.

What clinical trials is Farnesyl Protein Transferase Inhibitor in?

Farnesyl Protein Transferase Inhibitor has been studied in two completed Phase 1 trials. NCT00034684 enrolled 132 patients with leukemia, myelodysplastic syndromes, chronic myeloid leukemia in blast crisis, and lymphocytic leukemia. NCT00040547 enrolled 29 patients with advanced solid tumors and combined the drug with docetaxel.

How does Farnesyl Protein Transferase Inhibitor work?

Farnesyl Protein Transferase Inhibitor works by inhibiting farnesyl protein transferase, an enzyme involved in the farnesylation of proteins. This process is important for the function of certain proteins that can drive cancer cell growth. By blocking this enzyme, the drug aims to disrupt cancer cell signaling.