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GCS-100

Phase 2

Chronic Kidney Disease | Small molecule | Nephrology |Innoviva, Inc.|Last Updated: Dec 26, 2016

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDBiomarker
Total Trials3
Total Enrollment241
FDA Designations
No designations recorded
Clinical Trials (3)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02155673A Phase 2 Extension Study of Study GCS-100-CS-4002PHASE2 COMPLETED 92Jan 1, 2014Jun 1, 2016Dec 26, 20165 United States
NCT01843790A Phase 2a Study of Weekly Doses of GCS-100 in Patients With Chronic Kidney DiseasePHASE2 COMPLETED 120Jun 1, 2013Sep 1, 2014Sep 1, 20154 United States
NCT01717248Safety Study of GCS-100 to Treat Chronic Kidney DiseasePHASE1 COMPLETED 29Jan 1, 2013Jun 1, 2013Jun 20, 20134 United States
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Study Endpoints
Primary Endpoints
Evaluation of Safety
Participants will be followed for the duration of the study, up to 1 year with a four week additional follow-up period.

Evaluation of safety measures for long-term dosing including collection of adverse events in clinically significant changes in lab values

Change in estimated glomerular filtration rate (eGFR) from baseline relative to placebo after administration of GCS-100 for 8 weeks in patients with chronic kidney disease (CKD) and baseline eGFR of 15 - 44 mL/min/1.73m2
12 weeks
Secondary Endpoints
Number of adverse events as a measure of safety and tolerability of GCS-100 administered for 8 weeks relative to placebo in patients with CKD
12 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingSINGLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Low Dose GCS-100EXPERIMENTALLow dose of GCS-100
High Dose GCS-100EXPERIMENTALGCS-100 High dose
Placebo, salinePLACEBO_COMPARATORSaline, dosed weekly for 8 weeks
GCS-100 low doseEXPERIMENTALLow dose of GCS-100 given IV once per week for 8 weeks
GCS-100 high doseEXPERIMENTALHigh dose of GCS-100 given IV once per week for 8 weeks
GCS-100EXPERIMENTALGCS-100 will be administered once weekly by a ten minutes injection.
Interventions
NameTypeDescription
GCS-100DRUG1.5 mg/m2 or 30 mg/m2 GCS-100. GCS-100 will be administered as IV infusions once weekly for 8 weeks with a 1 week and 4 week follow-up period and then at least every 30 days for up to a total of 1 year.
Placebo, SalineDRUGThe amount (in mg) of drug to be administered will be determined based on body surface area, which will be calculated based on body weight and height. The drug dose should be calculated on Day 1. Drug should be added to an infusion bag or syringe containing 0.9% Sodium Chloride Injection, USP. Drug be infused into a large vein via a large bore catheter to avoid local irritation and administered at no more than 2 mg/mL in no less than 60 mL.
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Eligibility Criteria
Age Range18 Years — 80 Years
SexALL
Healthy VolunteersNo
Study Sites5

Inclusion Criteria: 1. Subject is capable of understanding the purpose and risks of the study and is able to provide written informed consent 2. Subject was enrolled in and completed the End of Study (Day 85) of GCS-100-CS-4002 Exclusion Criteria: 1. Subject experienced a Grade 3 or worse adverse...

Countries:United States
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