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GCS-100

Phase 2

Chronic Kidney Disease | Small molecule | Nephrology |Innoviva, Inc.|Last Updated: Dec 26, 2016

Success Probability

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Market & Valuation

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Trial Design

RandomizedCONTROLLEDBiomarker
Total Trials3
Total Enrollment241

FDA Designations

No designations recorded

Clinical trial landscape

GCS-100 · 4 trials · 2 indications

Phase 2 3Phase 1 1
NCT02155673A Phase 2 Extension Study of Study GCS-100-CS-4002Chronic Kidney Disease
COMPLETED92 Analytics
NCT01843790A Phase 2a Study of Weekly Doses of GCS-100 in Patients With Chronic Kidney DiseaseChronic Kidney Disease
COMPLETED120 Analytics
NCT00514696Study of the Safety of GCS-100 in Subjects With Chronic Lymphocytic LeukemiaChronic Lymphocytic Leukemia
COMPLETED12 Analytics
PHASE2COMPLETED
A Phase 2 Extension Study of Study GCS-100-CS-4002
Chronic Kidney DiseaseUnlock trial analytics
PHASE2COMPLETED
A Phase 2a Study of Weekly Doses of GCS-100 in Patients With Chronic Kidney Disease
Chronic Kidney DiseaseUnlock trial analytics
PHASE2COMPLETED
Study of the Safety of GCS-100 in Subjects With Chronic Lymphocytic Leukemia
Chronic Lymphocytic LeukemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Evaluation of Safety
Participants will be followed for the duration of the study, up to 1 year with a four week additional follow-up period.

Evaluation of safety measures for long-term dosing including collection of adverse events in clinically significant changes in lab values

Change in estimated glomerular filtration rate (eGFR) from baseline relative to placebo after administration of GCS-100 for 8 weeks in patients with chronic kidney disease (CKD) and baseline eGFR of 15 - 44 mL/min/1.73m2
12 weeks
To Evaluate the effect of GCS-100 on markers of apoptosis in subjects with chronic lymphocytic leukemia using physical examinations, vital signs, lab assessments, and adverse event reporting
Up to 15 cycles X 21 days

Secondary Endpoints

Number of adverse events as a measure of safety and tolerability of GCS-100 administered for 8 weeks relative to placebo in patients with CKD
12 weeks
To evaluate the effect of GCS-100 on peripheral blood leukocyte count in subjects with chronic lymphocytic leukemia using complete blood count, leukocyte count and circulating cells for apoptosis
Hour 6 after Day 1 dosing, and Days 4 and 8
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Study Design & Arms

AllocationRANDOMIZED
MaskingSINGLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Low Dose GCS-100EXPERIMENTALLow dose of GCS-100
High Dose GCS-100EXPERIMENTALGCS-100 High dose
Placebo, salinePLACEBO_COMPARATORSaline, dosed weekly for 8 weeks
GCS-100 low doseEXPERIMENTALLow dose of GCS-100 given IV once per week for 8 weeks
GCS-100 high doseEXPERIMENTALHigh dose of GCS-100 given IV once per week for 8 weeks
GCS-100EXPERIMENTALGCS-100: 160 mg/m2 IV (in the vein) Study Days 1-5 of each 21-day cycle

Interventions

NameTypeDescription
GCS-100DRUG1.5 mg/m2 or 30 mg/m2 GCS-100. GCS-100 will be administered as IV infusions once weekly for 8 weeks with a 1 week and 4 week follow-up period and then at least every 30 days for up to a total of 1 year.
Placebo, SalineDRUGThe amount (in mg) of drug to be administered will be determined based on body surface area, which will be calculated based on body weight and height. The drug dose should be calculated on Day 1. Drug should be added to an infusion bag or syringe containing 0.9% Sodium Chloride Injection, USP. Drug be infused into a large vein via a large bore catheter to avoid local irritation and administered at no more than 2 mg/mL in no less than 60 mL.
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Eligibility Criteria

Age Range18 Years to 80 Years
SexALL
Healthy VolunteersNo
Study Sites5

Inclusion Criteria: 1. Subject is capable of understanding the purpose and risks of the study and is able to provide written informed consent 2. Subject was enrolled in and completed the End of Study (Day 85) of GCS-100-CS-4002 Exclusion Criteria: 1. Subject experienced a Grade 3 or worse adverse...

Countries:United States
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Frequently asked questions about GCS-100

What is GCS-100 used for?

GCS-100 is an investigational small molecule being studied for chronic lymphocytic leukemia and chronic kidney disease. It is developed by Innoviva, Inc. (NASDAQ: INVA). The drug is currently in Phase 2 clinical development for these conditions, with completed trials in both indications.

What does GCS-100 target?

GCS-100 is a small molecule that targets galectin-3, a protein involved in fibrosis and inflammation. By inhibiting galectin-3, GCS-100 aims to reduce tissue scarring and inflammatory processes associated with chronic kidney disease and chronic lymphocytic leukemia.

Who makes GCS-100?

GCS-100 is being developed by Innoviva, Inc., a biopharmaceutical company traded on NASDAQ under the ticker INVA. The company is conducting clinical trials to evaluate the drug's safety and efficacy in chronic kidney disease and chronic lymphocytic leukemia.

What phase is GCS-100 in?

GCS-100 is in Phase 2 clinical development. It has completed three clinical trials, including two Phase 2 studies and one Phase 1 study. No trials are currently active, and the drug remains investigational, not yet approved by regulatory authorities.

What clinical trials has GCS-100 been in?

GCS-100 has been studied in three completed clinical trials. NCT00514696 was a Phase 2 safety study in chronic lymphocytic leukemia with 12 participants. NCT01717248 was a Phase 1 safety study in chronic kidney disease with 29 participants. NCT01843790 was a Phase 2a study with 120 participants, and NCT02155673 was a Phase 2 extension study with 92 participants, both in chronic kidney disease.

Is GCS-100 the same as any other drug?

GCS-100 is also known by its chemical name, modified citrus pectin. It is a small molecule that has been studied under the name GCS-100 in clinical trials for chronic kidney disease and chronic lymphocytic leukemia. No other alternative names have been reported.