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GSK4771261

Phase 1

Kidney Disease | Small molecule | Nephrology |GSK plc|Last Updated: Jul 30, 2026

Success Probability

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials2
Total Enrollment116

FDA Designations

No designations recorded

Clinical trial landscape

GSK4771261 · 2 trials · 1 indication

Phase 1 2
NCT07600450A Study of GSK4771261 in Healthy Participants Aged 25 to 55 Years of Age InclusiveKidney Disease
NOT YET_RECRUITING30 Analytics
NCT06734234A Study to Evaluate the Safety, Tolerability, and Effects on Blood and Urine Markers of Single Ascending Dose of GSK4771261 in Healthy Participants and Participants With Autosomal Dominant Polycystic Kidney DiseaseKidney Disease
ACTIVE NOT_RECRUITING86 Analytics
PHASE1NOT YET_RECRUITING
A Study of GSK4771261 in Healthy Participants Aged 25 to 55 Years of Age Inclusive
Kidney DiseaseUnlock trial analytics
PHASE1ACTIVE NOT_RECRUITING
A Study to Evaluate the Safety, Tolerability, and Effects on Blood and Urine Markers of Single Ascending Dose of GSK4771261 in Healthy Participants and Participants With Autosomal Dominant Polycystic Kidney Disease
Kidney DiseaseUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants with Adverse Events (AEs), Injection Site Reactions, and Serious AEs (SAEs)
Up to Week 13 (End of Study)
Number of Participants with Clinically Significant Changes from Baseline in Vital Signs
Up to Week 13 (End of Study)
Number of Participants with Clinically Significant Changes from Baseline in Clinical Laboratory Values
Up to Week 13 (End of Study)
Number of Participants with Clinically Significant Changes from Baseline in 12-Lead Electrocardiogram (ECG)
Up to Week 13 (End of Study)
Area under the concentration-time curve from time zero to the time of the last quantifiable concentration (AUC[0-t])
Up to Week 13
Area under the serum concentration-time curve extrapolated to infinite time (AUC[0-inf])
Up to Week 13
Maximum observed serum concentration (Cmax)
Up to Week 13
Part A: Number of Participants with Adverse events (AEs)
From Baseline (Day 1) up to Day 182 (End of study [EoS])

An AE is any untoward medical occurrence in a clinical study participant, temporally associated with the use of a study intervention, whether or not considered related to the study intervention.

Part B: Number of Participants with AEs
From Baseline (Day 1) up to Day 182 (EoS)

An AE is any untoward medical occurrence in a clinical study participant, temporally associated with the use of a study intervention, whether or not considered related to the study intervention.

Part A: Number of Participants with Serious Adverse Events (SAEs)
From Baseline (Day 1) up to Day 182 (EoS)

An SAE is defined as any untoward medical occurrence that, at any dose, meets one or more of the criteria: results in death; is life threatening, requires inpatient hospitalization or prolongation of existing hospitalization; results in persistent or significant disability/incapacity, is a congenital anomaly/birth defect in the offspring of a study participant; abnormal pregnancy outcome (for example, spontaneous abortion, fetal death, stillbirth, congenital anomalies, ectopic pregnancy); is a suspected transmission of any infectious agent via an authorized medicinal product; or other situations.

Part B: Number of Participants with SAEs
From Baseline (Day 1) up to Day 182 (EoS)

An SAE is defined as any untoward medical occurrence that, at any dose, meets one or more of the criteria: results in death; is life threatening, requires inpatient hospitalization or prolongation of existing hospitalization; results in persistent or significant disability/incapacity, is a congenital anomaly/birth defect in the offspring of a study participant; abnormal pregnancy outcome (for example, spontaneous abortion, fetal death, stillbirth, congenital anomalies, ectopic pregnancy); is a suspected transmission of any infectious agent via an authorized medicinal product; or other situations

Part A: Number of Participants with Clinically Significant Changes in Blood Laboratory Values
From Baseline (Day 1) up to Day 182 (EoS)

Number of participants with clinically significant changes in blood laboratory values will be evaluated.

Part B: Number of Participants with Clinically Significant Changes in Blood Laboratory Values
From Baseline (Day 1) up to Day 182 (EoS)

Number of participants with clinically significant changes in blood laboratory values will be evaluated.

Part A: Number of Participants with Clinically Significant Changes in Urine Laboratory Values
From Baseline (Day 1) up to Day 182 (EoS)

Number of participants with clinically significant changes in Urine laboratory values will be evaluated.

Part B: Number of Participants with Clinically Significant Changes in Urine Laboratory Values
From Baseline (Day 1) up to Day 182 (EoS)

Number of participants with clinically significant changes in Urine laboratory values will be evaluated.

Part A: Number of Participants with Clinically Significant Changes in Vital Signs
From Baseline (Day 1) up to Day 182 (EoS)

Number of participants with clinically significant changes in vital signs (will be evaluated.

Part B: Number of Participants with Clinically Significant Changes in Vital Signs
From Baseline (Day 1) up to Day 182 (EoS)

Number of participants with clinically significant changes in vital signs will be evaluated.

Part A: Number of Participants with Clinically Significant Changes in 12-lead Electrocardiogram (ECG)
From Baseline (Day 1) up to Day 182 (EoS)

Number of participants with clinically significant changes in 12-lead ECG parameters will be evaluated.

Part B: Number of Participants with Clinically Significant Changes in 12-lead ECG
From Baseline (Day 1) up to Day 182 (EoS)

Number of participants with clinically significant changes in 12-lead ECG parameters will be evaluated.

Secondary Endpoints

Number of Participants with pre-existing Anti-Drug Antibodies (ADAs)
Up to Week 13 (End of Study)
Number of Participants with treatment-emergent ADAs
Up to Week 13 (End of Study)
Part A: Number of Participants with Anti-drug Antibodies for GSK4771261
From Baseline (Day 1) up to Day 182 (EoS)
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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
GSK4771261EXPERIMENTALHealthy participants of Chinese, Japanese, or White/European ancestry will receive GSK4771261.
PlaceboEXPERIMENTALHealthy participants of Chinese, Japanese, or White/European ancestry will receive Placebo.
Part A: Cohort 1: Participants receiving GSK4771261 Dose level 1EXPERIMENTALHealthy participants will be randomized to receive GSK4771261 Dose level 1.
Part A: Cohort 2 : Participants receiving GSK4771261 Dose level 2EXPERIMENTALHealthy participants will be randomized to receive GSK4771261 Dose level 2.
Part A: Cohort 3: Participants receiving GSK4771261 Dose level 3EXPERIMENTALHealthy participants will be randomized to receive GSK4771261 Dose level 3.
Part A: Cohort 4: Participants receiving GSK4771261 Dose level 4EXPERIMENTALHealthy participants will be randomized to receive GSK4771261 Dose level 4.
Part A: Cohort 5: Participants receiving GSK4771261 Dose level 5EXPERIMENTALHealthy participants will be randomized to receive GSK4771261 Dose level 5.
Part A: Cohort 6: Participants receiving GSK4771261 Dose level 6EXPERIMENTALHealthy participants will be randomized to receive GSK4771261 Dose level 6.
Part A: Cohort 7 (optional): Participants receiving GSK4771261 Dose level 7EXPERIMENTALHealthy participants will be randomized to receive GSK4771261 Dose level 7 as the recommendation of Dose escalation committee (DEC).
Part A: Cohort 8 (optional): Participants receiving GSK4771261 Dose level 8EXPERIMENTALHealthy participants will be randomized to receive GSK4771261 Dose level 8, as per the recommendation from DEC.
Part B: Cohort 1: Participants receiving GSK4771261 Dose level 9EXPERIMENTALParticipant with Autosomal dominant polycystic kidney disease (ADPKD) will be randomized to receive GSK4771261 Dose level 9.
Part B: Cohort 2: Participants receiving GSK4771261 Dose level 10EXPERIMENTALParticipant with ADPKD will be randomized to receive GSK4771261 Dose level 10.
Part B: Cohort 3: Participants receiving GSK4771261 Dose level 11EXPERIMENTALParticipant with ADPKD will be randomized to receive GSK4771261 Dose level11.
Part B: Cohort 4 (optional): Participants receiving GSK4771261 Dose level 12EXPERIMENTALParticipant with ADPKD will be randomized to receive GSK4771261 Dose level 12 as the recommendation from DEC.
Part B: Cohort 5 (optional): Participants receiving GSK4771261 Dose level 13EXPERIMENTALParticipant with ADPKD will be randomized to receive GSK4771261 Dose level 13, as per the recommendation from DEC.
Part A: Participants receiving Placebo matching GSK4771261PLACEBO_COMPARATORParticipants will receive placebo matching GSK4771261
Part B: Participants receiving placebo matching GSK4771261PLACEBO_COMPARATORParticipants will receive placebo matching GSK4771261

Interventions

NameTypeDescription
GSK4771261DRUGGSK4771261 will be administered.
PlaceboDRUGPlacebo will be administered.
Placebo matching GSK4771261DRUGPlacebo matching GSK4771261 will be administered.
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Eligibility Criteria

Age Range25 Years to 55 Years
SexALL
Healthy VolunteersYes

Inclusion Criteria: * Participants who are overtly healthy as determined by medical evaluation including medical history, physical examination, and laboratory tests. A participant with a clinical abnormality or laboratory parameter(s) which is/are not specifically listed in the inclusion or exclusi...

Countries:United StatesBelgiumCanadaFranceGermanyNetherlandsSpainUnited Kingdom
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Recent Changes (Last 90 Days)

LOWJul 30, 2026NCT06734234primaryCompletionDate: changed
LOWJul 30, 2026NCT06734234primaryCompletionDate: changed
MEDIUMJul 15, 2026NCT06734234Status: RECRUITING → ACTIVE_NOT_RECRUITING
MEDIUMJul 15, 2026NCT06734234Status: RECRUITING → ACTIVE_NOT_RECRUITING

Frequently asked questions about GSK4771261

What is GSK4771261 used for?

GSK4771261 is an investigational small molecule being developed for kidney disease, specifically studied in participants with autosomal dominant polycystic kidney disease. It is currently in Phase 1 clinical development and is not yet approved by regulatory authorities.

Who makes GSK4771261?

GSK4771261 is being developed by GSK plc, a global biopharmaceutical company listed on the stock exchange under the ticker GSK. The company is conducting Phase 1 clinical trials to evaluate the drug's safety, tolerability, and effects on blood and urine markers.

What phase is GSK4771261 in?

GSK4771261 is in Phase 1 clinical development. It is an investigational drug, meaning it has not been approved for any use. Two Phase 1 trials are listed, one active and one not yet recruiting, both involving healthy participants and those with kidney disease.

What clinical trials is GSK4771261 in?

GSK4771261 is being studied in two Phase 1 trials. NCT06734234 evaluates single ascending doses in healthy participants and those with autosomal dominant polycystic kidney disease, with 86 enrolled. NCT07600450 is a study in healthy participants aged 25 to 55, with 30 planned participants.

Is GSK4771261 being studied in autosomal dominant polycystic kidney disease?

Yes, GSK4771261 is being studied in autosomal dominant polycystic kidney disease. The trial NCT06734234 includes participants with this condition and healthy volunteers, assessing safety, tolerability, and effects on blood and urine markers. The trial is active but not recruiting.