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AZD4248

Phase 1

Chronic Kidney Disease | Small molecule | Nephrology |AstraZeneca PLC|Last Updated: Apr 20, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindNO_TREATMENT_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment124
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07024823A Study to Investigate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AZD4248 in Healthy Participants and Participants With Chronic Kidney Disease and Type 2 Diabetes and to Assess Home Measurements of Creatinine in a Non Interventional CohortPHASE1 RECRUITING 124Jun 9, 2025Jun 18, 2026Apr 20, 20265 United States
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Study Endpoints
Primary Endpoints
Parts A, B, and C: Number of Participants with Adverse Events (AEs) and Serious Adverse Events (SAEs)
From Day 1 to Follow Up visit (Part A: up to 12 days; Part B and C: up to 19 days)

To assess the safety and tolerability of AZD4248 following single oral ascending doses or single IV administration to healthy participants and multiple oral ascending doses to healthy participants and participants with CKD and T2D (DKD).

Part D: Intra- and inter-participant variability of estimated glomerular filtration rate (eGFR) derived from home self-testing device measurements
Day 1 to Day 169

To assess intra- and inter-participant variability of twice weekly home-based serum creatinine measurements.

Secondary Endpoints
Area under concentration-time curve from time 0 to infinity (AUCinf)
Part A1 and A2: Days 1-7, Part A3: Days 1-3, Part B: Days 1-17. Part C: Days 1-17
Area under concentration-curve from time 0 to the last quantifiable concentration (AUClast)
Part A1 and A2: Days 1-7, Part A3: Days 1-3, Part B: Days 1-17. Part C: Days 1-17
Dose normalized AUClast (AUClast/D)
Part A1 and A2: Days 1-7, Part A3: Days 1-3, Part B: Days 1-17. Part C: Days 1-17
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Part A1 SADEXPERIMENTALParticipants will receive single ascending oral dose of AZD4248 or placebo.
Part A2 SAD Chinese CohortEXPERIMENTALParticipants will receive single oral dose of AZD4248 or placebo.
Part A3 SAD IV CohortEXPERIMENTALParticipants will receive single IV infusion of AZD4248 or placebo.
Part B1 MADEXPERIMENTALParticipants will receive multiple ascending oral doses of AZD4248 or placebo.
Part B2 MAD JapaneseEXPERIMENTALParticipants will receive multiple ascending oral doses of AZD4248 or placebo.
Part C Multiple Dosing DKDEXPERIMENTALParticipants will receive multiple oral doses of AZD4248 or placebo.
Part D Observational CohortNO_INTERVENTIONParticipants will participate in home-based creatinine self-measurement.
Interventions
NameTypeDescription
AZD4248DRUGAZD4248 will be administered orally.
PlaceboDRUGPlacebo will be administered orally.
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersYes
Study Sites5

Key Inclusion Criteria: \- Healthy participants with suitable veins for cannulation or repeated venipuncture. Parts A and B: * Have a body mass index (BMI) between 18 and 30 kilograms per millimeter (kg/m2), inclusive. * For Chinese participants (Part A2): participants are to be Chinese, defined ...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT07024823primaryCompletionDate: changed
LOWMay 24, 2026NCT07024823studyFirstPostDate: changed