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BLEX 404 Liquid

Phase 2

Myelodysplastic Syndrome (MDS) | Small molecule | Hematology |ABVC BioPharma, Inc.|Last Updated: Apr 13, 2026

Target and mechanism

ModalitySmall molecule

Also known as BLEX 404 Oral Liquid

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment52

FDA Designations

No designations recorded

Clinical trial landscape

BLEX 404 Liquid · 2 trials · 2 indications

Phase 2 1Phase 1 1
NCT02944955A Study of BLEX 404 Oral Liquid in Patients With International Prognostic Scoring System (IPSS) Intermediate-1, Intermediate-2 or High-Risk Myelodysplastic Syndrome (MDS) and Chronic Myelomonocytic Leukemia (CMML)Myelodysplastic Syndrome (MDS)
NOT YET_RECRUITING52 Analytics
PHASE2NOT YET_RECRUITING
A Study of BLEX 404 Oral Liquid in Patients With International Prognostic Scoring System (IPSS) Intermediate-1, Intermediate-2 or High-Risk Myelodysplastic Syndrome (MDS) and Chronic Myelomonocytic Leukemia (CMML)
Myelodysplastic Syndrome (MDS)Unlock trial analytics

Study Endpoints

Primary Endpoints

Part I: Recommended dose level (RDL) of BLEX 404 Oral Liquid
8 weeks (2 cycles of azacitidine)

RDL is defined by BLEX 404 Oral Liquid-related prohibited toxicity in subjects undergoing 2 cycles of azacitidine treatment. When one of the stopping criteria is met during the study treatment period, RDL will be set at the lower dose level.

Part II: Incidence of infections
24 weeks (6 cycles of azacitidine)

Number of subjects experience infection events and inpatient hospitalization due to infections.

Phase I: Dose-limiting toxicity (DLT) observation
3 weeks (1 cycle)

Presence or absence of dose-limiting toxicity (DLT) related to BLEX 404 Oral Liquid for each patient during first cycle of Docetaxel monotherapy to determine the recommended dose level (RDL).

Phase II: Overall response rate (PR + CR)
12 weeks (4 cycles)

Overall response rate (PR + CR) after 4 cycles of combination use in BLEX 404 + Docetaxel monotherapy.

Secondary Endpoints

Part I: (A) Number of subjects experience infections events and inpatient hospitalization due to infections
8 weeks (2 cycles of azacitidine)
Part I: (B) Treatments and duration of each infections
8 weeks (2 cycles of azacitidine)
Part I: (C) Complete remission (CR) or partial remission (PR) of bone marrow, peripheral blood, cytogenetic response (defined by 2006 IWG Criteria)
8 weeks (2 cycles of azacitidine)
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
BLEX 404 Oral LiquidEXPERIMENTALPart I: Part I-1: Low Dose BLEX 404 Oral Liquid (3 mg/kg, BID) is administered in combination with 2 cycles of azacitidine. Part I-2: High Dose BLEX 404 Oral Liquid (4.5 mg/kg, BID) is administered in combination with 2 cycles of azacitidine. Part II: Recommended Dose Level (RDL) of BLEX 404 Oral Liquid will be determined by results from Part I. BLEX 404 Oral Liquid at RDL is administered in combination with 6 cycles of azacitidine.

Interventions

NameTypeDescription
BLEX 404 Oral LiquidDRUGBLEX 404 Oral Liquid is orally administered twice daily in combination with azacitdine treatment cycles (2 cycles in Part I and 6 cycles in Part II). Azacitidine treatment: SC or IV injections at 75 mg/m2, QD for 7 days each cycle. 28 days/cycle, and repeat cycles every 4 weeks.
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Eligibility Criteria

Age Range20 Years to N/A
SexALL
Healthy VolunteersNo

Inclusion Criteria: * Age 20 or older, able to sign informed consent, understand and comply with protocol requirements and instructions. * Body weight between 30 to 120 kg * International Prognostic Scoring System (IPSS) intermediate-1 (int-1), intermediate-2 (int-2) or high-risk myelodysplastic sy...

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Frequently asked questions about BLEX 404 Liquid

What is BLEX 404 Liquid used for?

BLEX 404 Liquid is an investigational oral liquid being studied for the treatment of Myelodysplastic Syndrome (MDS) and Triple Negative Breast Cancer. It is a small molecule developed by ABVC BioPharma, Inc. (NASDAQ: ABVC). The drug is currently in Phase 2 clinical development for these indications.

What does BLEX 404 target?

BLEX 404 is a small molecule, but its specific molecular target has not been disclosed in available information. The drug is being evaluated in clinical trials for its safety and efficacy in treating Myelodysplastic Syndrome and Triple Negative Breast Cancer, though the exact mechanism of action is not publicly detailed.

Who makes BLEX 404?

BLEX 404 is being developed by ABVC BioPharma, Inc., a biopharmaceutical company traded on NASDAQ under the ticker symbol ABVC. The company is conducting clinical trials to evaluate the drug's safety and efficacy in patients with Myelodysplastic Syndrome and Triple Negative Breast Cancer.

What phase is BLEX 404 in?

BLEX 404 is in Phase 2 clinical development. It is an investigational drug and has not been approved by regulatory authorities. The company is currently conducting trials to assess its safety and efficacy in treating Myelodysplastic Syndrome and Triple Negative Breast Cancer.

What clinical trials is BLEX 404 in?

BLEX 404 is involved in two clinical trials. NCT02944955 is a Phase 2 study in patients with Myelodysplastic Syndrome, with an enrollment of 52 participants. NCT02802423 is a Phase 1/2 study combining BLEX 404 with docetaxel in patients with advanced or metastatic Triple Negative Breast Cancer, enrolling 44 participants. Both trials are not yet recruiting.

Is BLEX 404 the same as BLEX 404 Oral Liquid?

Yes, BLEX 404 Liquid is also known as BLEX 404 Oral Liquid. Both names refer to the same investigational drug developed by ABVC BioPharma, Inc. The drug is being studied in oral liquid form for the treatment of Myelodysplastic Syndrome and Triple Negative Breast Cancer.