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CPPC PET ligand

Phase 1

ALS | Small molecule | Neurology |United Therapeutics Corporation|Last Updated: Apr 13, 2026

Target and mechanism

ModalitySmall molecule

Also known as [11C]CPPC PET ligand

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment20

FDA Designations

No designations recorded

Clinical trial landscape

CPPC PET ligand · 1 trial · 1 indication

Phase 1 1
NCT05602142Study of [11C]CPPC as a Clinical PET Radioligand Biomarker of Microglial Activation in ALSALS
NOT YET_RECRUITING20 Analytics
PHASE1NOT YET_RECRUITING
Study of [11C]CPPC as a Clinical PET Radioligand Biomarker of Microglial Activation in ALS
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Study Endpoints

Primary Endpoints

Safety of use of [11C]CPPC in patients with ALS as assessed by adverse events
Up to 180 days after scan

Safety of use of \[11C\]CPPC in positron emission tomography (PET) neuroimaging of patients with a diagnosis of ALS. Safety will be assessed by number of adverse events during and up to 180 days after the injection

Safety of use of [11C]CPPC in patients with ALS as assessed by a change in neurological status
Baseline and 180 days after scan

Safety of use of \[11C\]CPPC in positron emission tomography (PET) neuroimaging of patients with a diagnosis of ALS. Safety will be assessed by neurological physical exam to determine if there is a change in the findings from baseline.

Safety of use of [11C]CPPC in patients with ALS as assessed by a change in complete blood count (CBC) test
Baseline and 180 days after scan

Safety of use of \[11C\]CPPC in positron emission tomography (PET) neuroimaging of patients with a diagnosis of ALS. Safety will be assessed by monitoring of the complete blood count (CBC) for a change from baseline that is outside of the normal range.

Safety of use of [11C]CPPC in patients with ALS as assessed by a change in complete metabolic panel (CMP) test
Baseline and 180 days after scan

Safety of use of \[11C\]CPPC in positron emission tomography (PET) neuroimaging of patients with a diagnosis of ALS. Safety will be assessed by a change in the CMP from baseline that is outside of the normal range.

Secondary Endpoints

Sensitivity of use of [11C]CPPC as assessed by a radiologist
Up to 180 days after scan
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeDIAGNOSTIC

Treatment Arms

ArmTypeDescription
[11C]CPPCEXPERIMENTALAll participants will receive \[11C\]CPPC which is a radiotracer ligand that specifically binds to CSF1R.

Interventions

NameTypeDescription
[11C]CPPC PET ligandDRUGRadioactive PET ligand to determine microglia expression of colony stimulating factor 1 receptor (CSF1R).
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersYes

Inclusion Criteria 1. Have the ability to understand the requirements of the study, provide written informed consent, understand and provide written authorization for the use and disclosure of Protected Health Information (PHI) \[per Health Insurance Portability and Accountability Act (HIPAA) Priva...

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Frequently asked questions about CPPC PET ligand

What is CPPC PET ligand used for?

CPPC PET ligand is an investigational small molecule being developed for use in amyotrophic lateral sclerosis (ALS). It is a positron emission tomography (PET) radioligand intended to serve as a clinical biomarker of microglial activation in ALS. The drug is currently in Phase 1 clinical development.

What does CPPC PET ligand target?

CPPC PET ligand is designed to target microglial activation, which is a biological process associated with neuroinflammation in ALS. As a PET radioligand, it is intended to enable visualization of this process in the brain using positron emission tomography imaging. The drug is being studied as a biomarker in ALS.

Who makes CPPC PET ligand?

CPPC PET ligand is being developed by United Therapeutics Corporation, a biopharmaceutical company traded on the NASDAQ under the ticker symbol UTHR. The company is conducting a Phase 1 clinical trial of the drug in ALS patients.

What phase is CPPC PET ligand in?

CPPC PET ligand is in Phase 1 clinical development. It is an investigational drug and has not been approved by regulatory authorities. The drug is being studied in an early-stage clinical trial to evaluate its use as a PET radioligand biomarker in ALS.

What clinical trials is CPPC PET ligand in?

CPPC PET ligand is being studied in one Phase 1 clinical trial with the identifier NCT05602142. The trial is titled 'Study of [11C]CPPC as a Clinical PET Radioligand Biomarker of Microglial Activation in ALS' and is designed to enroll 20 participants with ALS. The trial is not yet recruiting.

Is CPPC PET ligand the same as [11C]CPPC PET ligand?

Yes, CPPC PET ligand is also known as [11C]CPPC PET ligand. The two names refer to the same investigational drug, with the [11C] designation indicating the carbon-11 radioisotope used in the PET imaging agent. Both names are used in the clinical trial context.