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MN-166

Phase 2

Amyotrophic Lateral Sclerosis | Small molecule | Neurology |MediciNova, Inc.|Last Updated: Mar 6, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials2
Total Enrollment304

FDA Designations

ORPHAN_DRUGFAST_TRACK

Clinical trial landscape

MN-166 · 5 trials · 6 indications

Phase 2 2Phase 1 3
NCT04057898Evaluation of MN-166 (Ibudilast) for 12 Months Followed by an Open-label Extension for 6 Months in Patients With ALSAmyotrophic Lateral Sclerosis
ACTIVE NOT_RECRUITING234 Analytics
NCT02238626Ibudilast (MN-166) in Subjects With Amyotrophic Lateral Sclerosis (ALS)Amyotrophic Lateral Sclerosis
COMPLETED70 Analytics
PHASE2ACTIVE NOT_RECRUITING
Evaluation of MN-166 (Ibudilast) for 12 Months Followed by an Open-label Extension for 6 Months in Patients With ALS
Amyotrophic Lateral SclerosisUnlock trial analytics
PHASE2COMPLETED
Ibudilast (MN-166) in Subjects With Amyotrophic Lateral Sclerosis (ALS)
Amyotrophic Lateral SclerosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Change from baseline in ALSFRS-R score at Month 12 (or last measurement before death in case of censoring) and survival time.
12 months

The amyotrophic lateral sclerosis functional rating scale-revised, or ALSFRS-R, measures the functional status of subjects with ALS. It is based on 12 items, each of which is rated on a 5-point scale (0 to 4). The rate of total functional disability thus ranges from 0 (maximum disability) to 48 (normal function) points.

Safety and Tolerability of MN-166 60 mg/d Versus Placebo When Administered With Riluzole in Subjects With ALS
6 months

Safety will be assessed by monitoring and recording all treatment-emergent adverse events (TEAEs) including serious adverse events (SAEs) and discontinuations due to TEAEs and Additional assessments will include regular monitoring of hematology, blood chemistry, and urine values, regular measurement of vital signs, ECGs, medical history, physical and neurological examinations.

Compare the pharmacokinetic profile of ER and IR formulations in single-dose administration of MN-166 (ibudilast)
From the time of pre-dose (immediately prior to taking the assigned MN-166/ibudilast formulation) to 0.5, 1, 2, 4, 6, 8, 10, 12, 24, 32, 48, 72, 96, and 168 hours post-single treatment dose.

Compare the maximum plasma concentrations (Cmax) of MN-166 (ibudilast) of ER 50 mg tablet and IR 10 mg capsule (5 capsules) formulations, in a single-dose regimen in healthy volunteers.

Compare the pharmacokinetic profile of ER and IR formulations in single-dose administration of MN-166 (ibudilast) under fed or fasting states
From the time of pre-dose (immediately prior to taking the assigned MN-166/ibudilast formulation under either feeding or fasting conditions) to 0.5, 1, 2, 4, 6, 8, 10, 12, 24, 32, 48, 72, 96, and 168 hours post-single treatment dose.

Cmax of MN-166 (ibudilast) of ER 50 mg tablet and IR 10 mg capsule (5 capsules) formulations, in a single-dose regimen in healthy volunteers fed a high-fat meal 1 hour prior to dosing or fasted 8 hours prior to dosing.

Evaluate safety and tolerability of ibudilast and temozolomide combination treatment
1-6 months

Determine the proportion of patients with * Treatment-emergent adverse events (TEAEs) as measured by the CTCAE v4.0 and * Treatment discontinuations due to TEAEs and Dose-Limiting Toxicities (DLTs).

Evaluate efficacy of ibudilast and TMZ combination treatment
1-6 months

Proportion of patients who are progression free at 6 months (PFS6) using the RANO criteria.

Compare the PK Profile of two new formulations in Single-day dose of MN-166
5 weeks

Compare the maximum plasma concentrations \[Cmax\] of MN-166 of two different formulations MN-166 50mg, extended release (ER) tablets with MN-166 10mg capsules in a single-dose regimen in healthy volunteers.

Secondary Endpoints

Mean change from baseline of muscle strength measured by hand-held dynamometry
Baseline, Treatment Phase Week 6, Months 3, 6, 9 and12 time points.
Mean change from baseline on quality of life assessed by ALSAQ-5 at Month 12
12 months
Mean change from baseline of functional activity measured by ALSFRS-R at Month 12
12 months
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
MN-166EXPERIMENTALSubjects will take MN-166 10 mg capsules, up to 50 mg twice a day for 12 months.
placeboPLACEBO_COMPARATORSubjects will take up to 5 matching placebo capsules twice a day for 12 months.
Placebo (for MN-166)PLACEBO_COMPARATORSugar pill manufactured for MN-166 10 mg tablets plus 50 mg riluzole by mouth twice daily for 6 months.
Sequence 1ACTIVE_COMPARATORTwo participants will be randomly assigned to sequence 1 comprising 3 treatments (ER fasted, ER fed, and IR fasted) in a crossover design, administered one week apart: Day 1-7: ER fasted; Day 8-15: ER fed Day 15-22: IR fasted
Sequence 2ACTIVE_COMPARATORTwo participants will be randomly assigned to sequence 2 comprising 3 treatments in a crossover design, administered one week apart: Day 1-7: ER fed; Day 8-15: IR fasted; Day 15-22: ER fasted
Sequence 3ACTIVE_COMPARATORTwo participants will be randomly assigned to sequence 3 comprising 3 treatments in a crossover design, administered one week apart: Day 1-7: IR fasted; Day 8-15: ER fasted; Day 15-22: ER fed
Sequence 4ACTIVE_COMPARATORTwo participants will be randomly assigned to sequence 4 comprising 3 treatments in a crossover design, administered one week apart: Day 1-7: IR fasted; Day 8-15: ER fed; Day 15-22: ER fasted
Sequence 5ACTIVE_COMPARATORTwo participants will be randomly assigned to sequence 5 comprising 3 treatments in a crossover design, administered one week apart: Day 1-7: ER fasted; Day 8-15: IR fasted; Day 15-22: ER fed
Sequence 6ACTIVE_COMPARATORTwo participants will be randomly assigned to sequence 6 comprising 3 treatments in a crossover design, administered one week apart: Day 1-7: ER fed; Day 8-15: ER fasted; Day 15-22: IR fasted
MN-166 and temozolomideEXPERIMENTALPart 1: Combination treatment of MN-166 60 mg/day (30 mg twice a day) for 28 days and temozolomide 150 mg/m² on Days 1-5 of 28-day cycle. Part 2: Open-label, fixed-dose MN-166 and temozolomide combination treatment for 6 cycles until disease progression, unacceptable tolerability and/or toxicity or loss of life.
Extended-release formulation 1 (ER1)EXPERIMENTAL50mg MN-166 tablet. This formulation is intended for once-a-day dosing, hence, the label of extended-release.
Extended-release formulation 2 (ER2)EXPERIMENTAL50mg MN-166 tablet. This formulation is intended for once-a-day dosing, hence, the label of extended-release.
Intermediate-release formulation (IR)ACTIVE_COMPARATOR10mg MN-166 capsule. This formulation is typically given two or three times daily, hence, the label of intermediate-release.

Interventions

NameTypeDescription
MN-166DRUGSubjects will take MN-166 for 12 months followed by a 6-month open-label extension phase.
placeboDRUGSubjects will take matching placebo for 12 months followed by a 6-month open-label extension phase.
Placebo (for MN-166)DRUG -
riluzoleDRUGPatient is given 50 mg riluzole twice daily.
TemozolomideDRUGTemozolomide is an oral chemotherapy drug. It is an alkylating agent used as a treatment of some brain cancers; and a first-line treatment for glioblastoma multiforme.
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Eligibility Criteria

Age Range18 Years to 80 Years
SexALL
Healthy VolunteersNo
Study Sites16

Major Inclusion Criteria: * Male or female subjects age 18 - 80 years, inclusive; * Diagnosis of familial or sporadic ALS as defined by the El Escorial-Revised (2000) research diagnostic criteria for ALS \[clinically definite, clinically probable, probable-laboratory-supported\]; * ALS onset of ≤18...

Countries:United StatesCanada
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Frequently asked questions about MN-166

What is MN-166 used for?

MN-166, also known as ibudilast, is an investigational small molecule being studied for neurological conditions. It is in clinical trials for glioblastoma, amyotrophic lateral sclerosis (ALS), and has been tested in healthy volunteers. The drug is being developed by MediciNova, Inc. (ticker: MNOV).

How does MN-166 work?

MN-166 works by targeting specific molecular pathways involved in neuroinflammation and neurodegeneration. It is a small molecule that modulates the activity of certain enzymes, including phosphodiesterases and macrophage migration inhibitory factor, which are thought to play a role in the progression of neurological diseases like ALS and glioblastoma.

Who makes MN-166?

MN-166 is being developed by MediciNova, Inc., a biopharmaceutical company traded on the NASDAQ under the ticker symbol MNOV. The company is conducting clinical trials of MN-166 for neurological indications, including amyotrophic lateral sclerosis and glioblastoma.

What phase is MN-166 in?

MN-166 is in Phase 2 clinical development for amyotrophic lateral sclerosis (ALS), with an active Phase 2 trial ongoing. It has also completed Phase 1 trials in healthy volunteers and in glioblastoma patients. The drug has received Orphan Drug and Fast Track designations from the FDA for ALS.

What clinical trials is MN-166 in?

MN-166 has an active Phase 2 trial (NCT04057898) in ALS patients, with 234 participants enrolled across the United States and Canada. Completed trials include a Phase 2 ALS study (NCT02238626), a Phase 1 healthy volunteer study (NCT03533387), and a Phase 1 glioblastoma study (NCT03782415).

Is MN-166 the same as ibudilast?

Yes, MN-166 is the same drug as ibudilast. The compound is referred to by both names in clinical trial records and scientific literature. MediciNova is developing ibudilast under the code name MN-166 for neurological conditions, including ALS and glioblastoma.