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Mosliciguat

Phase 2

Pulmonary Hypertension | Small molecule | Cardiovascular |Roivant Sciences Ltd.|Last Updated: Jun 16, 2026

Target and mechanism

ModalitySmall molecule

Also known as inhaled mosliciguat

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment155

FDA Designations

ORPHAN_DRUG

Clinical trial landscape

Mosliciguat · 3 trials · 8 indications

Phase 2 2Phase 1 1
NCT07333183A Study of Mosliciguat in Combination With Inhaled Treprostinil in PH-ILDPulmonary Hypertension
RECRUITING20 Analytics
NCT06635850A Study of Mosliciguat in PH-ILDPulmonary Hypertension
ACTIVE NOT_RECRUITING135 Analytics
PHASE2RECRUITING
A Study of Mosliciguat in Combination With Inhaled Treprostinil in PH-ILD
Pulmonary HypertensionUnlock trial analytics
PHASE2ACTIVE NOT_RECRUITING
A Study of Mosliciguat in PH-ILD
Pulmonary HypertensionUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence and nature of participant TEAEs, SAEs, and AEs leading to discontinuation
Baseline, Week 16
Change from Baseline to Week 16 in Pulmonary Vascular Resistance (PVR)
Baseline, Week 16

PVR evaluated using right heart catheterization (RHC).

Determine the absolute bioavailability (ABA) of mosliciguat following administration of a single inhaled dose of mosliciguat followed by an IV microtracer dose of [14C]-mosliciguat in healthy adult males
Baseline, Day 7

Absolute bioavailability of inhaled mosliciguat

Area under the concentration-time curve (AUC) for mosliciguat
Baseline, Day 7
Assess the mass balance (i.e., cumulative excretion in urine and feces compared to the administered amount of radioactive isotope) of [14C] following a single oral dose of mosliciguat solution
Baseline, Day 28

Urine and fecal recovery of total \[14C\] radioactivity, \[14C\]-mosliciguat

Maximum observed concentration (Cmax)
Baseline, Day 7

Secondary Endpoints

Change from Baseline to Week 16 in Distance Achieved on the Six-Minute Walk Test (6MWT)
Baseline, Week 16
Change from Baseline to Week 16 in N-terminal pro-brain natriuretic peptide (NT-proBNP)
Baseline, Week 16
Evaluate the incidence of Treatment-Emergent Adverse Events (safety and tolerability of mosliciguat)
Baseline, Day 44
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Active Comparator: inhaled mosliciguatEXPERIMENTALParticipants will receive inhaled mosliciguat daily for 16 weeks
Extension: inhaled mosliciguatEXPERIMENTALAfter Week 16, all participants will continue to receive inhaled mosliciguat through an Extension period
MosliciguatACTIVE_COMPARATORParticipants will be randomized to receive inhaled mosliciguat or placebo daily for 24 weeks
Matched PlaceboPLACEBO_COMPARATORParticipants will be randomized to receive inhaled mosliciguat or placebo daily for 24 weeks
ExtensionEXPERIMENTALAfter Week 24, all participants may receive mosliciguat through an Extension period
Mosliciguat (RVT-2301)EXPERIMENTALMosliciguat administered daily via dry powder inhaler.
14C mosliciguatEXPERIMENTALAdministered orally and via IV

Interventions

NameTypeDescription
inhaled mosliciguatDRUGDose level 1, 2, or 3 for inhalation
Dry Powder InhalerDEVICEDry powder inhaler for mosliciguat delivery
MosliciguatDRUGDose level 1, 2, or 3 for inhalation
PlaceboDRUGMatching placebo for inhalation
14C mosliciguatDRUGDose level
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Eligibility Criteria

Age Range18 Years to 85 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Participants willing and able to provide informed consent * Participants on inhaled treprostinil * Participants with diagnosis of Interstitial Lung Disease (ILD). Diagnosis will be confirmed by a high-resolution computerized tomography (HR-CT) scan showing diffuse parenchymal ...

Countries:United States
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Frequently asked questions about Mosliciguat

What is Mosliciguat used for?

Mosliciguat is an investigational small molecule being developed for pulmonary hypertension associated with interstitial lung disease (PH-ILD). It is also studied in healthy volunteers for early-phase safety assessment. The drug is inhaled and has received orphan drug designation from the FDA.

Who makes Mosliciguat?

Mosliciguat is being developed by Roivant Sciences Ltd., a biopharmaceutical company traded on the NASDAQ under the ticker ROIV. The company is conducting clinical trials of the drug in the United States for pulmonary hypertension associated with interstitial lung disease.

What phase is Mosliciguat in?

Mosliciguat is in Phase 1 and Phase 2 clinical development. A Phase 1 study in healthy adult males has been completed, and two Phase 2 studies in patients with pulmonary hypertension and interstitial lung disease are ongoing or recruiting. It is investigational and not yet approved.

What clinical trials is Mosliciguat in?

Mosliciguat has three clinical trials: NCT06635850, a Phase 2 study in PH-ILD with 135 participants, active but not recruiting; NCT07185321, a completed Phase 1 study in healthy males with 8 participants; and NCT07333183, a recruiting Phase 2 study combining Mosliciguat with inhaled treprostinil in PH-ILD with 20 participants.

Is Mosliciguat the same as inhaled mosliciguat?

Yes, Mosliciguat is also known as inhaled mosliciguat, reflecting its route of administration. The drug is delivered via inhalation for the treatment of pulmonary hypertension associated with interstitial lung disease. It is a small molecule and has been granted orphan drug designation.

Does Mosliciguat have FDA orphan drug designation?

Yes, Mosliciguat has received orphan drug designation from the FDA. This designation is granted to drugs intended for the treatment of rare diseases and may provide benefits such as market exclusivity and development incentives. The drug is being studied for pulmonary hypertension associated with interstitial lung disease.