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Treprostinil Palmitil

Phase 3

Pulmonary Arterial Hypertension | Small molecule | Cardiovascular |Insmed Incorporated|Last Updated: May 28, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials3
Total Enrollment537
FDA Designations
No designations recorded
Clinical Trials (3)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07481981A Study to Evaluate the Efficacy and Safety of Once Daily Treprostinil Palmitil Inhalation Powder (TPIP) in Participants With Pulmonary Arterial Hypertension (PAH)PHASE3 RECRUITING 344Jun 26, 2026Jan 28, 2029May 26, 20261 United States
NCT05649748An Extension Study of Treprostinil Palmitil Inhalation Powder (TPIP) for Pulmonary Arterial Hypertension (PAH)PHASE2 ACTIVE NOT_RECRUITING 91Mar 7, 2023Dec 31, 2026May 28, 202645 United States, Argentina +13
NCT05147805A Study to Evaluate the Efficacy, Safety and Pharmacokinetics of Treprostinil Palmitil Inhalation Powder in Participants With Pulmonary Arterial HypertensionPHASE2 COMPLETED 102Aug 24, 2022Mar 27, 2025Mar 30, 202692 United States, Argentina +15
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Study Endpoints
Primary Endpoints
Change in 6-Minute Walk Distance (6MWD) Measured at 1 to 3 Hours Post-Dose From Baseline at Week 24
Baseline, Week 24
Number of Participants Who Experience at Least one Treatment Emergent Adverse Event (TEAE) and TEAEs by Severity
From screening up to last follow up visit (Up to approximately 26 months)
Change from Baseline in Pulmonary Vascular Resistance at Week 16
Baseline to Week 16
Secondary Endpoints
Percentage of Participants With an Improvement From Baseline in World Health Organization (WHO) Functional Class at Week 24
Baseline, Week 24
Change in 6MWD Measured at 24 Hours (±2) Since the Last Dose From Baseline at Week 22
Baseline, Week 22
Change From Baseline in the Concentration of N-Terminal Pro Hormone Brain Natriuretic Peptide (NT-proBNP) at Week 24
Baseline, Week 24
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Treprostinil Palmitil Inhalation PowderEXPERIMENTALParticipants will receive TPIP, once daily (QD), at a starting dose of 80 micrograms (μg) up to maximum tolerated dose (up to 1280 μg) for 24 weeks.
PlaceboPLACEBO_COMPARATORParticipants will receive a TPIP-matching placebo, QD, for 24 weeks.
Treprostinil Palmitil Inhalation Powder (TPIP)EXPERIMENTALParticipants who are not transitioning immediately from other TPIP studies:INS1009-201(NCT04791514), INS1009-202(NCT05147805) and other lead-in studies, will be given TPIP, once daily (QD), starting with 80 micrograms (μg), up-titrated to highest tolerated dose between 80 μg and 640 μg during 3-week titration period that maybe increased upto maximum dose of 1280 μg QD post initial titration, per investigator's assessment. Overall treatment period=24 months. Participants transitioning immediately from randomized blinded lead-in TPIP study and who previously received: 1. TPIP- will be given placebo QD(80 μg upto achieved TPIP dose from previous study)along with achieved TPIP dose from previous study in blinded manner during 3-week titration period. 2. Placebo- will be given TPIP QD (80 μg up to achieved placebo dose from previous study)along with achieved placebo dose from previous study in blinded manner during 3-week titration period.Overall treatment period=24 months.
Interventions
NameTypeDescription
Treprostinil Palmitil Inhalation PowderDRUGOral inhalation using a capsule-based dry powder inhaler device.
PlaceboDRUGOral inhalation using a capsule-based dry powder inhaler device.
Treprostinil PalmitilDRUGAdministered by oral inhalation, using a Plastiape capsule-based dry powder inhaler.
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria * Participants must have a diagnosis of World Health Organisation (WHO) Group 1 pulmonary hypertension (PAH) in any of the following subtypes, in accordance with European Society of Cardiology European Respiratory Society (ESC/ERS) Guidelines: * Idiopathic PAH * Heritable PA...

Countries:United StatesArgentinaAustriaBelgiumBrazilDenmarkGermanyItalyJapanMalaysiaMexicoPhilippinesSerbiaSpainUnited KingdomAustraliaSwitzerland
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Recent Changes (Last 90 Days)
LOWMay 29, 2026NCT05649748lastUpdatePostDate: changed
LOWMay 29, 2026NCT05649748lastUpdatePostDate: changed
LOWMay 29, 2026NCT05649748lastUpdatePostDate: changed
LOWMay 27, 2026NCT07481981Status: NOT_YET_RECRUITING → RECRUITING
LOWMay 27, 2026NCT07481981Status: NOT_YET_RECRUITING → RECRUITING
LOWMay 26, 2026NCT07481981primaryCompletionDate: changed
LOWMay 26, 2026NCT05649748primaryCompletionDate: changed
LOWMay 24, 2026NCT07481981studyFirstPostDate: changed
LOWMay 24, 2026NCT05649748studyFirstPostDate: changed