Recent Updates
Recently added Catalysts

Alisertib

Phase 2

Hormone Receptor Positive HER-2 Negative Breast Cancer | Small molecule | Oncology |Puma Biotechnology Inc|Last Updated: Aug 17, 2026

Target and mechanism

Molecular targetAURKA
Target classInhibitor
ModalitySmall molecule

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedCONTROLLEDDMC
Total Trials1
Total Enrollment225

FDA Designations

No designations recorded

Clinical trial landscape

Alisertib · 3 trials · 5 indications

Phase 2 3
NCT07465757A Study of Alisertib and Paclitaxel in Patients With Small Cell Lung Cancer (SCLC)Small Cell Lung Cancer ( SCLC )
NOT YET_RECRUITING50 Analytics
NCT06369285A Study of Alisertib in Combination With Endocrine Therapy in Patients With HR-positive, HER2-negative Recurrent or Metastatic Breast CancerHormone Receptor Positive HER-2 Negative Breast Cancer
RECRUITING225 Analytics
NCT06095505A Study of Alisertib in Patients With Extensive Stage Small Cell Lung CancerSmall Cell Lung Cancer
RECRUITING120 Analytics
PHASE2NOT YET_RECRUITING
A Study of Alisertib and Paclitaxel in Patients With Small Cell Lung Cancer (SCLC)
Small Cell Lung Cancer ( SCLC )Unlock trial analytics
PHASE2RECRUITING
A Study of Alisertib in Combination With Endocrine Therapy in Patients With HR-positive, HER2-negative Recurrent or Metastatic Breast Cancer
Hormone Receptor Positive HER-2 Negative Breast CancerUnlock trial analytics
PHASE2RECRUITING
A Study of Alisertib in Patients With Extensive Stage Small Cell Lung Cancer
Small Cell Lung CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Percentage of Participants with Treatment-Emergent Adverse Events (Adverse Events and Serious Adverse Events)
From date of first dose through last dose plus 28 days, assessed up to 24 months

Treatment emergent adverse events are those events reported on or after the first dose of investigational product and up to 28 days after the last dose.

Objective Response Rate (ORR) Within Dose Subgroup
From date of randomization to first confirmed Complete or Partial Response, whichever came earlier, assessed up to 48 months

Objective response rate is defined as the percentage of participants demonstrating a confirmed objective response during the study.

Duration of Response (DOR) Within Dose Subgroup
From start date of response (after date of randomization) to first PD, assessed up to 48 months

Duration of response is measured from the time at which measurement criteria are first met for Complete Response (CR) or Partial Response (PR) (whichever status is recorded first) until the first date of recurrence or progressive disease (PD) or death is objectively documented.

Disease Control Rate (DCR) Within Dose Subgroup
From date of randomization to first confirmed Complete or Partial Response, whichever came earlier, assessed up to 48 months

Disease control rate is the proportion of participants who achieve overall tumor response (confirmed CR or PR) or Stable Disease (SD) lasting for at least 24 weeks from randomization.

Progression Free Survival (PFS) Within Dose Subgroup
From date of randomization to date of recurrence, progression or death, assessed up to 48 months

Progression Free Survival (PFS) is measured in months and based on the local tumor assessment. The time interval from the date of randomization until the first date on which recurrence, progression, or death due to any cause, is documented.

Overall Survival (OS) Within Dose Subgroup
From date of randomization to death, assessed up to 48 months

Overall survival (OS) is defined as the time from randomization to death due to any cause, censored at the last date known alive on or prior to the data cutoff employed for the analysis, whichever was earlier.

Percentage of Participants With Treatment-Emergent Adverse Events (Adverse Events and Serious Adverse Events) in the Enrolled Population
From date of first dose through last dose plus 28 days, assessed up to 48 months

Treatment emergent adverse events are those events reported on or after the first dose of investigational product and up to 28 days after last dose.

Objective response rate (ORR) within biomarker-defined subgroup
From date of first dose to first confirmed Complete or Partial Response, whichever came earlier, assessed up to 36 months

Objective response rate is defined as the percentage of participants demonstrating a confirmed objective response during the study

Duration of response (DOR) within biomarker-defined subgroup
From start date of response (after date of first dose) to first PD, assessed up to 36 months

Duration of response is measured from the time at which measurement criteria are first met for CR or PR (whichever status is recorded first) until the first date of recurrence or progressive disease (PD) or death is objectively documented.

Disease Control Rate (DCR) within biomarker-defined subgroup
From date of first dose to first confirmed Complete or Partial Response, whichever came earlier, assessed up to 36 months

Disease control rate is the proportion of patients who achieve overall tumor response (confirmed CR or PR) or SD lasting for at least 8 weeks from first dose of investigational product.

Progression Free Survival (PFS) within biomarker-defined subgroup
From date of first dose to date of recurrence, progression or death, assessed up to 36 months

Progression Free Survival (PFS) is measured in months and based on the local tumor assessment. The time interval from the date of first dose until the first date on which recurrence, progression, or death due to any cause, is documented.

Overall Survival (OS) within biomarker-defined subgroup
From date of first dose to death, assessed up to 36 months

Overall survival (OS) is defined as the time from date of first dose to death due to any cause, censored at the last date known alive on or prior to the data cutoff employed for the analysis, whichever was earlier.

Secondary Endpoints

Objective Response Rate (ORR)
From date of first dose to first confirmed Complete or Partial Response, assessed up to 24 months
Duration of response (DOR)
From start date of response to first PD or death, assessed up to 24 months
Disease Control Rate (DCR)
From date of first dose to first confirmed Complete or Partial Response, whichever came earlier, assessed up to 24 months
Unlock Study Endpoints

Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cohort 1: Alisertib 30 mg BID + PaclitaxelEXPERIMENTALApproximately ten participants will be enrolled in the cohort. Alisertib dose may be increased by 10 mg BID in the next cohort if 3 or fewer participants experience an Event during Cycle 1.
Cohort 2: Alisertib 40 mg BID + PaclitaxelEXPERIMENTALApproximately ten participants will be enrolled in the cohort. Alisertib dose may be increased by 10 mg BID in the next cohort if 3 or fewer participants experience an Event during Cycle 1.
Cohort 3: Alisertib 50 mg BID + PaclitaxelEXPERIMENTALApproximately ten participants will be enrolled in the cohort. Alisertib dose may be increased by 10 mg BID in the next cohort if 3 or fewer participants experience an Event during Cycle 1.
Cohort 4: Alisertib 60 mg BID + PaclitaxelEXPERIMENTALApproximately ten participants will be enrolled in the cohort. Alisertib dose may be increased by 10 mg BID in the next cohort if 3 or fewer participants experience an Event during Cycle 1.
Cohort 5: Alisertib 70 mg BID + PaclitaxelEXPERIMENTALApproximately ten participants will be enrolled in the cohort.
Alisertib 50 mgEXPERIMENTALAlisertib with selected endocrine therapy
Alisertib 40 mgEXPERIMENTALAlisertib with selected endocrine therapy
Alisertib 30 mgEXPERIMENTALAlisertib with selected endocrine therapy
AlisertibEXPERIMENTAL50 mg (Prior to Amendment 2) or 60 mg (Amendment 2) or 70 mg (Amendment 3 or later) of alisertib PO BID on days 1-7 of each 21-day cycle

Interventions

NameTypeDescription
AlisertibDRUGAlisertib enteric-coated tablets, 30 mg BID self-administered orally on Days 1-7 of every 21-day cycle
PaclitaxelDRUG60 mg/m\^2 IV on Days 1 and 8 of every 21-day cycle
Endocrine therapyDRUGInvestigator selected endocrine therapy will be taken in 28-day dosing cycles according to the approved prescribing information. 1 mg of anastrozole tablet by mouth once daily or 2.5 mg of letrozole tablet by mouth once daily or 25 mg of exemestane tablet by mouth once daily or 20 mg of tamoxifen tablet by mouth once daily or 500 mg of fulvestrant intramuscular injection on Study Day 1, 15, 29, and once every 28 days thereafter
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo

Inclusion Criteria: * Aged ≥18 years at signing of informed consent * Pathologically confirmed SCLC * Prior treatment with one platinum-based chemotherapy and an anti-PD-1/PD-L1 immunotherapy. Up to one additional systemic anti-cancer therapy for SCLC is allowed, for a total of up to 2 prior treatm...

Countries:United StatesPortugalSpain
Unlock Eligibility Criteria

Recent Changes (Last 90 Days)

LOWAug 17, 2026NCT06095505lastUpdatePostDate: changed
LOWAug 17, 2026NCT06095505lastUpdatePostDate: changed
MEDIUMJul 27, 2026NCT06369285Enrollment: 150 → 225
MEDIUMJul 27, 2026NCT06369285Enrollment: 150 → 225
MEDIUMJul 27, 2026NCT06369285Enrollment: 150 → 225

Frequently asked questions about Alisertib

What is Alisertib used for?

Alisertib is an investigational small molecule being studied for the treatment of small cell lung cancer (SCLC) and hormone receptor positive, HER2 negative breast cancer. It is currently in Phase 2 clinical trials for these oncology indications.

Who makes Alisertib?

Alisertib is being developed by Puma Biotechnology Inc (NASDAQ: PBYI). The company is conducting Phase 2 clinical trials to evaluate the drug in patients with small cell lung cancer and hormone receptor positive, HER2 negative breast cancer.

What phase is Alisertib in?

Alisertib is in Phase 2 clinical development. It is an investigational drug and has not been approved by the FDA. There are three ongoing Phase 2 trials studying Alisertib in small cell lung cancer and breast cancer.

What clinical trials is Alisertib in?

Alisertib is being studied in three Phase 2 trials: NCT06095505 in extensive stage small cell lung cancer, NCT06369285 in HR-positive, HER2-negative recurrent or metastatic breast cancer, and NCT07465757 in combination with paclitaxel for small cell lung cancer.

Is Alisertib being studied in combination with other drugs?

Yes, one trial (NCT07465757) is studying Alisertib in combination with paclitaxel in patients with small cell lung cancer. Another trial (NCT06369285) is evaluating Alisertib in combination with endocrine therapy for HR-positive, HER2-negative breast cancer.

Is Alisertib the same as MLN8237?

Alisertib is also known by the research code MLN8237. It is an investigational Aurora kinase A inhibitor being developed by Puma Biotechnology Inc for the treatment of certain cancers, including small cell lung cancer and breast cancer.