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MDX2004

Phase 1

Advanced Tumors | Small molecule | Oncology |Opko Health Inc.|Last Updated: Mar 5, 2026

Target and mechanism

Molecular targetCD3
Target classProtein
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment235

FDA Designations

No designations recorded

Clinical trial landscape

MDX2004 · 1 trial · 1 indication

Phase 1 1
NCT07110584Dose Escalation and Dose Expansion Study of MDX2004 in Participants With Advanced TumorsAdvanced Tumors
RECRUITING235 Analytics
PHASE1RECRUITING
Dose Escalation and Dose Expansion Study of MDX2004 in Participants With Advanced Tumors
Advanced TumorsUnlock trial analytics

Study Endpoints

Primary Endpoints

All Study Parts: Adverse Events (AEs)
Baseline until 90 days after the participant has the last dose of MDX2004

Incidence and severity of adverse events (AEs) and serious AEs (SAEs), including changes in clinical laboratory parameters, graded according to the National Cancer Institute Common Terminology Criteria for Adverse Events (CTCAE) v5.0 or American Society for Transplantation and Cellular Therapy (ASTCT) consensus grading criteria, including changes in clinical laboratory parameters

Part A only - Maximum Tolerated Dose (MTD) or Recommended Phase 2 dose (RP2D)
28 days

Maximum Tolerated Dose or Recommended Phase 2 dose is determined following the evaluation of MDX2004 safety including the incidences of dose limiting toxicities (DLTs), MDX2004 anti-tumor activity, and MDX2004 pharmacokinetics/pharmacodynamics.

Part B, C, and D: Objective response rate of MDX2004
From date of enrollment until the end of treatment, up to approximately 6 months

Objective response rate is defined as the proportion of patients who achieve a complete response (CR) or partial response (PR) per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1.

Secondary Endpoints

All Study Parts: Measure of terminal half-life (t1/2) of MDX2004
6 months
All Study Parts: Measure of area under the serum concentration-time curve (AUC) of MDX2004
6 months
All Study Parts: Measure of time to maximum concentration (Tmax) of MDX2004
6 months
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Dose Escalation - Part AEXPERIMENTALParticipants with advanced tumors will receive MDX2004 as intravenous (IV) infusion.
Indication Optimization - Part BEXPERIMENTALParticipants with select advanced tumors will receive MDX2004 as intravenous (IV) infusion.
Dose Optimization - Part CEXPERIMENTALParticipants with select advanced tumors will receive one of two recommended doses of MDX2004 as intravenous (IV) infusion.
Dose Expansion - Part DEXPERIMENTALParticipants with select advanced tumors will receive the recommended Phase 2 dose of MDX2004 as intravenous (IV) infusion.

Interventions

NameTypeDescription
MDX2004DRUGMDX2004 intravenous infusion
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites6

Inclusion Criteria: * Participant must be ≥ 18 years of age. * Histologically or cytologically confirmed diagnosis of locally advanced or metastatic malignancy. * Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1. * All participants should have at least 1 measurable site of dis...

Countries:AustraliaIsrael
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Recent Changes (Last 90 Days)

LOWAug 1, 2026NCT07110584primaryCompletionDate: changed
LOWAug 1, 2026NCT07110584primaryCompletionDate: changed
LOWAug 1, 2026NCT07110584primaryCompletionDate: changed

Frequently asked questions about MDX2004

What is MDX2004 used for?

MDX2004 is an investigational small molecule being developed for the treatment of advanced tumors. It is currently in Phase 1 clinical development, with a study evaluating dose escalation and dose expansion in participants with advanced tumors.

What does MDX2004 target?

MDX2004 targets CD3, a protein involved in T-cell signaling. By targeting CD3, the drug is designed to modulate immune responses in the context of oncology, though the specific mechanism of action is not fully detailed.

Who is developing MDX2004?

MDX2004 is being developed by Opko Health Inc., a biopharmaceutical company traded on the stock exchange under the ticker OPK. The company is conducting a Phase 1 clinical trial for this investigational therapy.

What phase is MDX2004 in?

MDX2004 is in Phase 1 clinical development. It is an investigational drug, not yet approved by regulatory authorities, and is being studied in a dose escalation and dose expansion trial for advanced tumors.

What clinical trials is MDX2004 in?

MDX2004 is being studied in a Phase 1 clinical trial with the identifier NCT07110584. This trial is titled 'Dose Escalation and Dose Expansion Study of MDX2004 in Participants With Advanced Tumors' and is currently recruiting participants in Australia and Israel.

Is MDX2004 the same as any other drug?

MDX2004 is the primary name for this investigational drug. No alternative names have been reported for this asset, which is being developed by Opko Health Inc. for advanced tumors.