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Berubicin

Phase 2

Glioblastoma Multiforme, Adult | Small molecule | Oncology |CNS Pharmaceuticals, Inc.|Last Updated: Apr 15, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedACTIVE_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment252
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04762069A Study of Berubicin in Adult Subjects With Recurrent Glioblastoma MultiformePHASE2 ACTIVE NOT_RECRUITING 252May 18, 2021Jul 15, 2026Apr 15, 202648 United States, France +3
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Study Endpoints
Primary Endpoints
Overall Survival
Through study completion an average of 4 years.

To assess the effect of berubicin compared with lomustine on overall survival (OS) in adult patients with GBM that has recurred or progressed after standard initial therapy

Secondary Endpoints
Progression Free Survival
Through study completion an average of 4 years.
Event Free Survival
Through study completion an average of 4 years.
Overall Response Rate
Through study completion an average of 4 years.
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Study Design & Arms
AllocationRANDOMIZED
MaskingSINGLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
BerubicinEXPERIMENTALBerubicin intravenously infused will be administered at a dose of 7.1 mg/m2 as free base as a 2 hour intravenous (IV) infusion once daily for 3 consecutive days followed by 18 days off study drug (each cycle = 21 days) Each treatment cycle is 21 days. Subjects will be allowed to continue on treatment at the discretion of the Investigator if there is no evidence of disease progression and the subject is not experiencing unacceptable toxicity as well as if both the subject and Investigator agree that further therapy is in the subject's best interest.
Lomustine (CCNU, CeeNU®, or Gleostine®) capsulesACTIVE_COMPARATORLomustine (CCNU, CeeNU®, or Gleostine®) capsules will be administered at the institutionally-approved dose and regimen or per the full prescribing information/summary of product characteristics.
Interventions
NameTypeDescription
BerubicinDRUGBerubicin HCl is a novel synthetic anthracycline with a chemical structure similar to doxorubicin HCl, a cytotoxic anthracycline topoisomerase II inhibitor isolated from cultures of Streptomyces peucetius var. caesius.
LomustineDRUGLomustine is an anti-cancer ("antineoplastic" or "cytotoxic") chemotherapy drug. This medication is classified as an "alkylating agent.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites48

Patients will be eligible for the study if they meet all of the following inclusion criteria and none of the exclusion criteria. Inclusion criteria 1. Written informed consent from the patient or their legally authorized representative (LAR) prior to any study-related procedure, and willing and ab...

Countries:United StatesFranceItalySpainSwitzerland
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Recent Changes (Last 90 Days)
MEDIUMMay 26, 2026NCT04762069Enrollment: 210 → 252
LOWMay 24, 2026NCT04762069studyFirstPostDate: changed