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Siponimod

Phase 3

Multiple Sclerosis | Small molecule | Neurology |Novartis AG|Last Updated: Jun 20, 2024

Target and mechanism

Molecular targetS1PR1
Target classAgonist
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment185

FDA Designations

No designations recorded

Clinical trial landscape

Siponimod · 1 trial · 3 indications

Phase 3 1
NCT03623243Safety and Tolerability of Conversion From Oral, Injectable, or Infusion Disease Modifying Therapies to Dose-titrated Oral Siponimod (Mayzent) in Advancing RMS PatientsMultiple Sclerosis
COMPLETED185 Analytics
PHASE3COMPLETED
Safety and Tolerability of Conversion From Oral, Injectable, or Infusion Disease Modifying Therapies to Dose-titrated Oral Siponimod (Mayzent) in Advancing RMS Patients
Multiple SclerosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants With at Least One Treatment-emergent Adverse Event (TEAE) Related to Study Drug During the Treatment Period
From first dose of study drug up to 30 days after last dose of study drug (up to 7 months)

An Adverse Event (AE) is any untoward medical occurrence in a participant that does not necessarily have a causal relationship with the treatment. An AE can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding, for example), symptom, or disease temporarily associated with the use of a medicinal product, whether or not considered related to the medicinal product. TEAEs are defined as the AEs started after the first dose of siponimod to 30 days after the date of the last actual administration, or events present prior to start of treatment but which increased in severity. TEAEs suspected to be related to study drug are reported.

Secondary Endpoints

Number of Participants With at Least One Adverse Event (AE)
From first dose of study drug up to 30 days after last dose of study drug (up to 7 months)
Change From Baseline in Treatment Satisfaction Questionnaire for Medication (TSQM-9)
Baseline up to Day 168
Change in Heart Rate From Baseline to 6 Hours After First Treatment
From the first dose up to 6 hours
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
SiponimodEXPERIMENTALParticipants will receive titrated doses of siponimod tablets, orally, once daily of 0.25 mg on Day 2, 0.5 mg on Day 3, 0.75 mg on Day 4, 1.25 mg on Day 5, and maintenance dose of siponimod 2.0 mg tablets, orally, once daily from Day 6 up to 6 months. As of protocol amendment 3, participants entering the trial converting from fingolimod will start directly with 2 mg dose of siponimod.

Interventions

NameTypeDescription
SiponimodDRUGSiponimod 2mg tablets taken once daily
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Eligibility Criteria

Age Range18 Years to 65 Years
SexALL
Healthy VolunteersNo
Study Sites55

Key Inclusion Criteria: 1. Signed informed consent. 2. Male or female aged 18 to 65 years (inclusive). 3. Patients with advancing RMS as defined by the principal investigator. 4. Prior history of relapsing MS (RMS), with or without progressive features, according to the 2010 Revised McDonald or Lub...

Countries:United StatesPuerto Rico
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Frequently asked questions about Siponimod

What is Siponimod used for?

Siponimod is used for the treatment of Multiple Sclerosis, specifically in patients with relapsing, advancing, or relapsing-remitting forms of the disease. It is an oral small molecule being developed by Novartis AG for this neurological condition.

What does Siponimod target?

Siponimod is a small molecule that modulates the sphingosine 1-phosphate receptor. By targeting this receptor, it is believed to reduce the migration of lymphocytes into the central nervous system, which is thought to play a role in the inflammatory process of Multiple Sclerosis.

Who makes Siponimod?

Siponimod is being developed by Novartis AG, a multinational pharmaceutical company. Novartis is publicly traded under the ticker symbol NVS on the New York Stock Exchange.

What phase is Siponimod in?

Siponimod is in Phase 3 clinical development. It is an investigational drug and has not yet been approved by regulatory authorities. The Phase 3 trial has been completed, but the drug remains under clinical investigation.

What clinical trials is Siponimod in?

Siponimod has one completed Phase 3 clinical trial registered under NCT03623243. This trial, titled 'Safety and Tolerability of Conversion From Oral, Injectable, or Infusion Disease Modifying Therapies to Dose-titrated Oral Siponimod (Mayzent) in Advancing RMS Patients,' enrolled 185 participants in the United States and Puerto Rico.

Is Siponimod the same as Mayzent?

Yes, Siponimod is also known as Mayzent. The clinical trial NCT03623243 refers to Siponimod by its brand name Mayzent, indicating that these names are used interchangeably for the same drug.