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sargramostim

Phase 3

Leukemia | Monoclonal antibody | Oncology |Eli Lilly and Company|Last Updated: Jul 5, 2023

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLEDDMC
Total Trials1
Total Enrollment449

FDA Designations

No designations recorded

Clinical trial landscape

sargramostim · 1 trial · 2 indications

Phase 3 1
NCT00046930Daunorubicin & Cytarabine +/- Zosuquidar inTreating Older Patients With Newly Diagnosed Acute Myeloid Leukemia or Refractory AnemiaLeukemia
COMPLETED449 Analytics
PHASE3COMPLETED
Daunorubicin & Cytarabine +/- Zosuquidar inTreating Older Patients With Newly Diagnosed Acute Myeloid Leukemia or Refractory Anemia
LeukemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Overall Survival (OS)
Assessed every 3 months for 2 years, then every 6 months for 3 years, then annually thereafter

Time from randomization to death. Patients alive at last follow-up were censored.

Secondary Endpoints

Progression-free Survival (PFS)
Assessed every 3 months for 2 years, then every 6 months for 3 years, then annually thereafter
Response
Assessed at the end of induction
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
ZosuquidarEXPERIMENTALInduction treatment with daunorubicin, cytarabine and zosuquidar (details provided in Intervention section), followed by consolidation with Cytarabine (1500 mg/m2 every 12 hours for 6 days), then additional consolidation with the same regimen as received during induction.
PlaceboACTIVE_COMPARATORInduction treatment with daunorubicin, cytarabine and placebo (details provided in Intervention section), followed by consolidation with Cytarabine (1500 mg/m2 every 12 hours for 6 days), then additional consolidation with the same regimen as received during induction.

Interventions

NameTypeDescription
filgrastimBIOLOGICAL250 μg/m2/day by either intravenous or subcutaneous injection starting day 12, provided marrow aplasia is achieved, through recovery of absolute neutrophil count (ANC) to \> 500 cells/μl, sustained for 3 consecutive days. The dose may be rounded to the nearest vial size.
sargramostimBIOLOGICAL5 μg/kg/day by either intravenous or subcutaneous injection starting day 12, provided marrow aplasia is achieved, through recovery of absolute neutrophil count (ANC) to \> 500 cells/μl, sustained for 3 consecutive days. The dose may be rounded to the nearest vial size.
cytarabineDRUG100 mg/m²/day by continuous intravenous infusion for 7 days (days 1-7).
daunorubicin hydrochlorideDRUG45 mg/m²/day by 10 - 15 minute intravenous infusion for 3 days (days 1, 2, and 3).
zosuquidar trihydrochlorideDRUGZosuquidar 550 mg/day by continuous intravenous infusion through a central venous catheter over approximately 6 hours on days 1, 2, and 3. The infusion will begin approximately one hour prior to daunorubicin on days 1, 2 and 3.
PlaceboDRUGPlacebo 550 mg/day by continuous intravenous infusion through a central venous catheter over approximately 6 hours on days 1, 2, and 3. The infusion will begin approximately one hour prior to daunorubicin on days 1, 2 and 3. Placebo consisted of a 1:1000 dilution of Infuvite, appropriately colored.
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Eligibility Criteria

Age Range60 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites92

Inclusion Criteria: One of the following disorders: * Acute myeloid leukemia (AML), defined as \>30% myeloblasts on the marrow aspirate or peripheral blood differential and any French-American-British (FAB) subtype except M3 (i.e., acute promyelocytic leukemia) * Refractory anemia with excess blas...

Countries:United StatesIsrael
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Competitive Landscape -Leukemia 327 trials

Top 20 of 63 competitors

CompanyTickerTrialsLead PhaseDrugs
Amgen Inc.AMGN8PHASE3Blinatumomab, Low-intensity chemotherapy regimen
Eli Lilly and CompanyLLY9PHASE3Pirtobrutinib, Idelalisib, Bendamustine, Rituximab
BeOne Medicines Ltd. Sponsored ADRONC13PHASE3Sonrotoclax, Zanubrutinib, Venetoclax, Obinutuzumab
AbbVie, Inc.ABBV24PHASE3Venetoclax
AstraZeneca PLCAZN18PHASE3Acalabrutinib, Rituximab, Chlorambucil
Merck & Co., Inc.MRK7PHASE3Nemtabrutinib, Fludarabine, Cyclophosphamide, Bendamustine, Rituximab
Johnson & JohnsonJNJ12PHASE3Ibrutinib, Venetoclax, Chlorambucil, Obinutuzumab
Novartis AG Sponsored ADRNVS21PHASE3Imatinib, Nilotinib, Bosutinib, Dasatinib, Asciminib
Kura Oncology, Inc.KURA5PHASE3Ziftomenib, Venetoclax, Azacitidine, Daunorubicin, Cytarabine
Nurix Therapeutics, Inc.NRIX5PHASE3NX-5948, Pirtobrutinib
Syndax Pharmaceuticals IncSNDX4PHASE3Revumenib, Intensive Chemotherapy Regimen
Takeda Pharmaceutical Co. Ltd. Sponsored ADRTAK1PHASE3Ponatinib, Imatinib, Vincristine, Dexamethasone, Cytarabine
SELLAS Life Sciences Group, Inc.SLS1PHASE3Galinpepimut-S, Azacitidine, Venetoclax, Decitabine, Cytarabine
Grifols, S.A. Sponsored ADR Class BGRFS1PHASE3Xembify
Bristol-Myers Squibb CompanyBMY7PHASE2Azacitidine
Pfizer Inc.PFE6PHASE2Gemtuzumab ozogamicine- Cytarabine- Gilteritinib
Ascentage Pharma Group International Unsponsored ADRAAPG11PHASE3Olverembatinib
Tango Therapeutics, Inc.TNGX7PHASE3AG-120, Azacitidine
Incyte CorporationINCY6PHASE2Ruxolitinib
Actinium Pharmaceuticals, Inc. (Delaware)ATNM2PHASE3Iomab-B, Conventional Care
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Frequently asked questions about sargramostim

What is sargramostim used for?

Sargramostim is an investigational monoclonal antibody being studied for the treatment of leukemia, specifically in older patients with newly diagnosed acute myeloid leukemia or refractory anemia. It is being developed by Eli Lilly and Company and is currently in Phase 3 clinical development.

What does sargramostim target?

Sargramostim is a monoclonal antibody, but its specific molecular target has not been disclosed. It is being studied in combination with chemotherapy drugs daunorubicin and cytarabine for the treatment of leukemia in older patients.

Who makes sargramostim?

Sargramostim is being developed by Eli Lilly and Company, a pharmaceutical company traded on the New York Stock Exchange under the ticker symbol LLY. The drug is currently in Phase 3 clinical trials for the treatment of leukemia.

What phase is sargramostim in?

Sargramostim is in Phase 3 clinical development. It is an investigational drug and has not been approved by regulatory authorities. One Phase 3 trial has been completed, involving 449 patients with leukemia or myelodysplastic syndromes.

What clinical trials is sargramostim in?

Sargramostim has been studied in one completed Phase 3 clinical trial, identified as NCT00046930. This trial evaluated the addition of sargramostim to daunorubicin and cytarabine in older patients with newly diagnosed acute myeloid leukemia or refractory anemia, enrolling 449 participants in the United States and Israel.