Recent Updates
Recently added Catalysts

Gemtuzumab ozogamicine- Cytarabine- Gilteritinib

Phase 2

AML | Small molecule | Oncology |Pfizer, Inc.|Last Updated: Jan 5, 2026

Target and mechanism

Molecular targetCD33
Target classBinding Agent
ModalitySmall molecule

Also known as Gemtuzumab ozogamicine - Cytarabine - Gilteritinib

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment19

FDA Designations

No designations recorded

Clinical trial landscape

Gemtuzumab ozogamicine- Cytarabine- Gilteritinib · 1 trial · 2 indications

Phase 2 1
NCT05199051A Phase 2 Study of Gemtuzumab Ozogamicin (GO)-Gilteritinib Combination in Adults With FLT3-ITD and/or FLT3-TKD Relapse/Refractory (R/R) AMLAML
ACTIVE NOT_RECRUITING19 Analytics
PHASE2ACTIVE NOT_RECRUITING
A Phase 2 Study of Gemtuzumab Ozogamicin (GO)-Gilteritinib Combination in Adults With FLT3-ITD and/or FLT3-TKD Relapse/Refractory (R/R) AML
AMLUnlock trial analytics

Study Endpoints

Primary Endpoints

Stage 1 - Safety of the addition of gilteritinib to the AGORA treatment platform
18 months

The primary objective of the first stage is to evaluate the safety of combining gilteritinib with the Gemtuzumab Ozogamicin (GO) -cytarabine AGORA platform in patients with FLT3-ITD and/or FLT3-TKD mutated Relapse/Refractory (R/R) Acute Myeloïd Leukemia (AML), through occurrence of dose-limiting toxicity (DLT).

Stage 2 - Event-free survival (EFS)
60 months

The primary objective of the second extension stage is to evaluate the efficacy of combining gilteritinib with the Gemtuzumab Ozogamicin (GO)-cytarabine AGORA platform in patients with FLT3-ITD and/or FLT3-TKD mutated Relapse/Refractory (R/R) Acute Myeloïd Leukemia (AML) through event-free survival (EFS).

Secondary Endpoints

Response rates to the study treatment
60 months
Early mortality rates, at day-30
30 months
Incidence of subsequent allogeneic Hematopoietic Stem Cell Transplantation (HSCT) overall.
60 months
Unlock Study Endpoints

Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Gemtuzumab ozogamicine - Cytarabine - GilteritinibEXPERIMENTALFor Gemtuzumab ozogamicine administrated during the induction phase at D1, D4 and D7, 3mg/m2/day (5mg max), IV, 2h of infusion. For Cytarabine during induction and consolidation phase at D1 to D5, 1000 mg/m2, IV, 2h of infusion. For Gilteritinib during induction phase from D10 for 14 consecutive days, per os, two doses level study with dose level 1 (80mg/d) in part 1 or dose level 2 (80 or 120mg/d depending of the result of part 1) in part 2. During consolidation (2 cycles max) from D8 for 14 consecutive days, per os, 120mg/d or reduced dose of 80 mg/kg is planned to be used in patients receiving concomitantly CYP3A4 inhibitors. During the maintenance (24 months max) dose level 2 (120mg/d), per os.

Interventions

NameTypeDescription
Gemtuzumab ozogamicine - Cytarabine - GilteritinibCOMBINATION_PRODUCTSee Arms description paragraph
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites12

Inclusion Criteria: * Patients aged 18 years old or more * Confirmed diagnosis of R/R AML positive for CD33 antigen as determined locally by immunophenotyping according to routine practice, defined as: * AML refractory to 1 or 2 intensive chemotherapy courses or a treatment by hypomethylating ag...

Countries:France
Unlock Eligibility Criteria

Frequently asked questions about Gemtuzumab ozogamicine- Cytarabine- Gilteritinib

What is Gemtuzumab ozogamicine-Cytarabine-Gilteritinib used for?

Gemtuzumab ozogamicine-Cytarabine-Gilteritinib is an investigational combination being studied for the treatment of acute myeloid leukemia (AML), specifically in adults with FLT3-ITD and/or FLT3-TKD relapse/refractory (R/R) AML. It is currently in Phase 2 clinical development.

What does Gemtuzumab ozogamicine-Cytarabine-Gilteritinib target?

Gemtuzumab ozogamicine-Cytarabine-Gilteritinib is a combination therapy that includes gemtuzumab ozogamicin, an antibody-drug conjugate targeting CD33, and gilteritinib, a small molecule that targets FLT3 mutations. The combination is being studied in AML patients with FLT3-ITD and/or FLT3-TKD mutations.

Who makes Gemtuzumab ozogamicine-Cytarabine-Gilteritinib?

Gemtuzumab ozogamicine-Cytarabine-Gilteritinib is being developed by Pfizer, Inc. (NYSE: PFE). The company is conducting a Phase 2 clinical trial of this combination in adults with relapse/refractory AML.

What phase is Gemtuzumab ozogamicine-Cytarabine-Gilteritinib in?

Gemtuzumab ozogamicine-Cytarabine-Gilteritinib is in Phase 2 clinical development. It is an investigational combination and has not been approved by regulatory authorities. The ongoing Phase 2 trial is active but not recruiting participants.

What clinical trials is Gemtuzumab ozogamicine-Cytarabine-Gilteritinib in?

Gemtuzumab ozogamicine-Cytarabine-Gilteritinib is being studied in a single Phase 2 trial, NCT05199051, which is active but not recruiting. The trial enrolls adults with FLT3-ITD and/or FLT3-TKD relapse/refractory AML and is being conducted in France.

Is Gemtuzumab ozogamicine-Cytarabine-Gilteritinib the same as Gemtuzumab ozogamicine-Cytarabine-Gilteritinib?

Yes, Gemtuzumab ozogamicine-Cytarabine-Gilteritinib is also known as Gemtuzumab ozogamicine-Cytarabine-Gilteritinib. The combination includes gemtuzumab ozogamicin, cytarabine, and gilteritinib, and is being evaluated in AML.