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XMT-1001

Phase 1

Small Cell Lung Cancer | Small molecule | Oncology |Day One Biopharmaceuticals, Inc.|Last Updated: Jan 31, 2018

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment30
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00455052A Study of Intravenous XMT-1001 in Patients With Advanced Solid TumorsPHASE1 COMPLETED 30Mar 1, 2011Dec 1, 2011Jan 31, 201812 United States
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Study Endpoints
Primary Endpoints
Adverse Events
Every 7 days in each 21 day cycle
Secondary Endpoints
Tumor response
Every 2 cycles
Time to tumor progression
Every 2 cycles
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
XMT-1001EXPERIMENTALXMT-1001 is administered I.V. every 21 days. Groups of 3 patients are given one dose and the dose increases for each group. The first dose level is 17 mg/m\^2, the next dose level is 30 mg/m\^2, followed by dose levels: 50 mg/m\^2, 80 mg/m\^2, 120 mg/m\^2, 150 mg/m\^2, and 190 mg/m\^2 until disease progressions or unacceptable side effects are experienced.
Interventions
NameTypeDescription
XMT-1001DRUGXMT-1001 is administered as an IV infusion once every 21 days. This expansion of the Phase 1 study is to confirm the MTD.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites12

Inclusion Criteria: 1. At least 18 years old 2. Have histological or cytological documentation of one of the following: A. NSCLC with Stage IV disease according to the American Joint Cancer Commission TNM Staging (7th Edition) * Have received at least one prior chemotherapy regimen but no mo...

Countries:United States
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Competitive Landscape -Non-Small Cell Lung Cancer 406 trials
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