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Puxitatug Samrotecan

Phase 3

Endometrial Cancer | Small molecule | Oncology |AstraZeneca PLC|Last Updated: May 20, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedACTIVE_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment700
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07044336Puxitatug Samrotecan (AZD8205) Monotherapy vs Chemotherapy in B7-H4-selected Endometrial Cancer (Bluestar-Endometrial01)PHASE3 RECRUITING 700Aug 1, 2025Jul 17, 2029May 20, 2026314 United States, Argentina +26
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Study Endpoints
Primary Endpoints
Progression Free Survival (PFS) for Arm A vs Arm B
Approximately 3 years

PFS is defined as the time from randomization until progression per RECIST 1.1 as assessed by BICR or death due to any cause.

Overall survival (OS) for Arm A vs Arm B
Approximately 3 years

OS is defined as the time from randomization until the date of death due to any cause.

Secondary Endpoints
Assessment of Overall Response Rate (ORR) for Arm A vs Arm B
Approximately 3 years
Assessment of Duration of response (DoR) for Arm A vs Arm B
Approximately 3 years
Assessment of progression-free survival 2 (PFS2) for Arm A vs Arm B
Approximately 3 years
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Study Design & Arms
AllocationRANDOMIZED
MaskingSINGLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Puxitatug SamrotecanEXPERIMENTALPuxi-Sam IV (intravenous) Q3W .
ChemotherapyACTIVE_COMPARATORPhysician's choice of chemotherapy Doxorubicin IV Q3W or Paclitaxel IV on Days 1, 8, and 15 in 28 day cycles.
Interventions
NameTypeDescription
Puxitatug SamrotecanDRUG2.4 mg/kg on Day 1 Q3W Route of administration: IV infusion
DoxorubicinDRUG60 mg/m2 on Day 1 Q3W Route of administration: IV
PaclitaxelDRUG80 mg/m2 on Days 1, 8, and 15 in 28-day cycle Route of Administration: IV
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Eligibility Criteria
Age Range18 Years — N/A
SexFEMALE
Healthy VolunteersNo
Study Sites314

The main inclusion criteria include but are not limited to the following: * Histologically confirmed diagnosis of endometrial carcinoma or carcinosarcoma. * Recurrent/metastatic EC ie, with radiological or objective evidence of recurrence or progression. * Has received prior platinum-based chemothe...

Countries:United StatesArgentinaAustraliaAustriaBelgiumBrazilCanadaChinaCzechiaDenmarkFinlandFranceGeorgiaGermanyGreeceHungaryIsraelItalyJapanLithuaniaNetherlandsPolandSingaporeSloveniaSouth KoreaSpainTaiwanUnited Kingdom
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Competitive Landscape -Endometrial Cancer 113 trials
CompanyTickerTrialsLead PhaseDrugs
Merck & Co., Inc.MRK6PHASE3Sacituzumab tirumotecan, Doxorubicin, Paclitaxel, Nab-paclitaxel, Pembrolizumab
AstraZeneca PLCAZN14PHASE3olaparib, durvalumab, Carboplatin, Paclitaxel, Durvalumab + Chemotherapy phase
Gilead Sciences, Inc.GILD2PHASE3Sacituzumab govitecan-hziy, Doxorubicin, Paclitaxel
GSK plc Sponsored ADRGSK3PHASE3Mocertatug rezetecan, Paclitaxel, Doxorubicin, Dostarlimab, Carboplatin
BioNTech SE Sponsored ADRBNTX1PHASE3BNT323/DB-1303, Doxorubicin, Paclitaxel, Docetaxel
Genmab A/S Sponsored ADRGMAB3PHASE3Rina-S, IC, GEN1047 is a bispecific antibody that induces T-cell mediated cytotoxicity of B7H4-positive tumor cells., Carboplatin, Bevacizumab
Karyopharm Therapeutics, Inc.KPTI1PHASE3Selinexor
Pfizer Inc.PFE4PHASE2tucatinib, trastuzumab, fulvestrant, disitamab vedotin, PF-08052666
HUTCHMED (China) Limited Sponsored ADRHCM1PHASE3fruquintinib, sintilimab, paclitaxel, doxorubicin
Eli Lilly and CompanyLLY5PHASE1LY3537982, Pembrolizumab, Cetuximab, Pemetrexed, Cisplatin
Incyte CorporationINCY1PHASE2retifanlimab, epacadostat, pemigatinib, INCAGN02385, INCAGN02390
Jazz Pharmaceuticals Public Limited CompanyJAZZ2PHASE2Zanidatamab
Corcept Therapeutics Incorporated.CORT1PHASE2Relacorilant once daily, Nab-paclitaxel /m^2, Bevacizumab /kg
Xencor, Inc.XNCR2PHASE2vudalimab, XmAb541
Acrivon Therapeutics, Inc.ACRV1PHASE2ACR-368, Gemcitabine
MacroGenics, Inc.MGNX2PHASE2Lorigerlimab, MGC026 Dose Escalation
Iovance Biotherapeutics IncIOVA1PHASE2Lifileucel
Regeneron Pharmaceuticals, Inc.REGN2PHASE1REGN5668, Cemiplimab, Ubamatamab, Sarilumab, Tocilizumab
IDEAYA Biosciences, Inc.IDYA2PHASE1IDE-161, Pembrolizumab, IDE034
Bristol-Myers Squibb CompanyBMY1PHASE1BMS-986463
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT07044336primaryCompletionDate: changed
LOWMay 24, 2026NCT07044336studyFirstPostDate: changed