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Palifermin 6 x 60 μg/kg/day

Phase 1

Leukemia | Small molecule | Oncology |Amgen Inc.|Last Updated: Oct 24, 2014

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLED
Total Trials1
Total Enrollment25
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00070616Pharmacokinetic Study of Palifermin in Subjects Receiving Radiation Therapy and Chemotherapy Followed by Blood Stem Cell SupportPHASE1 COMPLETED 25Dec 1, 2001Mar 1, 2005Oct 24, 2014 -
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Study Endpoints
Primary Endpoints
To characterize the PK profile of 3 daily intravenous (IV) doses of rHuKGF before total body irradiation (TBI) / high-dose chemotherapy conditioning treatment and after PBPC transplantation
Secondary Endpoints
To assess the safety and tolerability of rHuKGF in subjects with hematologic malignancies undergoing TBI and high-dose chemotherapy followed by PBPC transplantation.
To assess oral mucositis in subjects receiving rHuKGF.
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Palifermin 6 x 60 μg/kg/dayEXPERIMENTALThe first 3 consecutive daily doses were administered before the initiation of conditioning therapy (study days -11, -10, and -9); 3 additional consecutive daily doses were administered after administration of radiotherapy, chemotherapy and PBPC transplantation (study days 0, 1, and 2).
Palifermin 2 x 180 μg/kg/dayEXPERIMENTALThe first dose was administered on study day -11, 3 days before the initiation of conditioning therapy, and the second dose was given on day 0 after administration of radiotherapy, chemotherapy and the PBPC infusion
Interventions
NameTypeDescription
Palifermin 6 x 60 μg/kg/dayDRUG -
Palifermin 2 x 180 μg/kg/dayDRUG -
radiotherapyRADIATION -
ChemotherapyDRUG -
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Eligibility Criteria
Age Range18 Years — 76 Years
SexALL
Healthy VolunteersNo

* Patients diagnosed with Non-Hodgkin's Lymphoma, Hodgkin's Disease, Leukemia and Myeloma. - Eligible for treatment with radiation therapy and chemotherapy followed by blood stem cell support.

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Competitive Landscape -Leukemia 332 trials
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