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AV-101

Phase 2

Major Depressive Disorder | Small molecule | Psychiatry |Vistagen Therapeutics, Inc.|Last Updated: Feb 17, 2022

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment180

FDA Designations

No designations recorded

Clinical trial landscape

AV-101 · 3 trials · 3 indications

Phase 2 1Phase 1 2
NCT03078322AV-101 as Adjunct Antidepressant Therapy in Patients With Major DepressionMajor Depressive Disorder
COMPLETED180 Analytics
PHASE2COMPLETED
AV-101 as Adjunct Antidepressant Therapy in Patients With Major Depression
Major Depressive DisorderUnlock trial analytics

Study Endpoints

Primary Endpoints

Montgomery Åsberg Depression Rating Scale 10-item version (MADRS-10)
2 weeks

Depression questionnaire

Mean 40-Hz Auditory Steady State Response Power
4 hours

Mean power (in microVolt squared; uV\^2) of 40-Hz Auditory Steady State Response (ASSR; an auditory task using 40Hz click trains) calculated across 38-42Hz. Mean +/- SE across pre-treatment baseline and 4 post-treatment measures one every hour controlled for time, with outcomes the mean per treatment arm obtained from Linear Mixed Model analysis.

Pharmacokinetics
PK samples will be collected at time 0, 0.5, 1.5, 2, 4, 6, 8, 12, and 24 hours post-dosing on Day 1 and Day 14.

To evaluate pharmacokinetics of three dose levels of orally-administered AV-101 given once a day for 14 days in healthy volunteers by measuring Cmax, half-life, Tmax, and AUC.

Safety
28 days

To evaluate the safety of three dose levels of orally-administered AV-101 given once a day for 14 days in healthy volunteers by evaluating the number of subjects with treatment-emergent adverse events and changes from baseline to end of study in vital signs, hematology, hepatic profile, renal profile, urinalysis, and clinical laboratory parameters.

Secondary Endpoints

Time course of improvement including response rates
2 weeks
Safety and tolerability will be assessed by incidence of adverse events (AEs)
2 weeks
Peak Change in Plasma Concentration of AV-101 Marker 4-Chloro-kynurenine
4 hours
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
AV-101EXPERIMENTALL-4-chlorokynurenine 1440 mg daily for 14 days
PlaceboPLACEBO_COMPARATORPlacebo
Placebo, then AV-101 720mg, then AV-101 1440mgPLACEBO_COMPARATORParticipants first received oral placebo. After at least 3 days wash-out participants get oral AV-101 720mg (matching placebo capsules). After at least 3 days wash-out participants get oral AV-101 1440mg (matching placebo capsules).
AV-101 720mg, then AV-101 1440mg, then placeboEXPERIMENTALParticipants first received oral AV-101 720mg (matching placebo capsules). After at least 3 days wash-out participants get oral AV-101 1440mg (matching placebo capsules). After at least 3 days wash-out participants get oral placebo.
AV-101 1440mg, then placebo, then AV-101 720mgEXPERIMENTALParticipants first received oral AV-101 1440mg (matching placebo capsules). After at least 3 days wash-out participants get oral placebo. After at least 3 days wash-out participants get oral AV-101 720mg (matching placebo capsules).
microcrystalline cellulosePLACEBO_COMPARATORSubjects will be randomized into one of three cohorts (360, 1,080, and 1,440 mg) to receive a daily oral dose for 14 consecutive days. Each cohort will have 12 subjects on active drug and 4 subjects on placebo.

Interventions

NameTypeDescription
AV-101DRUGOral capsules taken once daily (in addition to open-label treatment with a commercially available antidepressant)
PlaceboDRUGOral capsules taken once daily (in addition to open-label treatment with a commercially available antidepressant)
AV-101 720 mgDRUGSingle dose of 2 360 mg AV-101 oral capsules + 2 placebo oral capsules
AV-101 1440 mgDRUGSingle dose of 4 360 mg AV-101 oral capsules
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Eligibility Criteria

Age Range18 Years to 65 Years
SexALL
Healthy VolunteersNo
Study Sites22

Inclusion Criteria: * Diagnosed with MDD, single or recurrent, and currently experiencing a MDE of at least 8 weeks in duration. * Has a history of inadequate response to at least 1 approved antidepressant including at least 1 and no more than 3 during the current depressive episode. * Meet the thr...

Countries:United States
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Frequently asked questions about AV-101

What is AV-101?

AV-101 is an investigational small molecule being developed by Vistagen Therapeutics, Inc. It has been studied in healthy volunteers, major depressive disorder, and neuropathic pain. AV-101 is also known as AV-101 720 mg. It remains in clinical development and is not an approved therapy.

What is AV-101 used for?

AV-101 has been studied for major depressive disorder and neuropathic pain, and in healthy volunteers for biomarker and pharmacokinetic research. Its development programs have included an adjunct antidepressant therapy study in major depression and a safety, tolerability, and pharmacokinetics study in neuropathic pain.

Who makes AV-101?

AV-101 is developed by Vistagen Therapeutics, Inc., which trades under the ticker VTGN. The company has sponsored the clinical trials evaluating AV-101 in healthy volunteers, major depressive disorder, and neuropathic pain.

What phase is AV-101 in?

AV-101 is in Phase 1 development. Its clinical program includes Phase 1 studies in healthy volunteers and a Phase 2 study in major depressive disorder, all of which are completed. AV-101 is investigational and has not been approved for any indication.

What clinical trials is AV-101 in?

AV-101 has been evaluated in completed trials including NCT03583554, an electrophysiological biomarkers study in healthy volunteers; NCT03078322, a Phase 2 adjunct antidepressant therapy trial in major depressive disorder; and NCT01483846, a Phase 1 safety, tolerability, and pharmacokinetics study in healthy volunteers.