Recent Updates
Recently added Catalysts

VERVE-201

Phase 1

Hypercholesterolemia | Small molecule | Metabolic |Verve Therapeutics, Inc.|Last Updated: Jul 17, 2026

Target and mechanism

Molecular targetANGPTL3
ModalitySmall molecule

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment36

FDA Designations

No designations recorded

Clinical trial landscape

VERVE-201 · 1 trial · 3 indications

Phase 1 1
NCT06451770Phase 1b Study of VERVE-201 in Patients With Refractory HyperlipidemiaHypercholesterolemia
RECRUITING36 Analytics
PHASE1RECRUITING
Phase 1b Study of VERVE-201 in Patients With Refractory Hyperlipidemia
HypercholesterolemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence of treatment-emergent adverse events (TEAEs) and serious adverse events (SAEs)
Up to Day 365

Secondary Endpoints

Evaluation of maximum observed concentration (Cmax)
Up to Day 365
Evaluation of time to maximum observed concentration (tmax)
Up to Day 365
Evaluation of terminal elimination half-life (t1/2)
Up to Day 365
Unlock Study Endpoints

Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cohort 1: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-201.
Cohort 2: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-201.
Cohort 3: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-201.
Cohort 4: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-201.
Cohort 5: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-201.
Cohort 6: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-201.

Interventions

NameTypeDescription
VERVE-201DRUGIntravenous (IV) infusion
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to 70 Years
SexALL
Healthy VolunteersNo
Study Sites16

Inclusion Criteria: * Refractory hypercholesterolemia * Refractory hypertriglyceridemia Exclusion Criteria: * Active or history of chronic liver disease * Current treatment with monoclonal antibody targeting ANGPTL3 or prior treatment within specified timeframe * Clinically significant or abnorma...

Countries:United StatesAustraliaCanadaNetherlandsSouth AfricaUnited Kingdom
Unlock Eligibility Criteria

Recent Changes (Last 90 Days)

LOWJul 17, 2026NCT06451770lastUpdatePostDate: changed
LOWJul 17, 2026NCT06451770lastUpdatePostDate: changed

Frequently asked questions about VERVE-201

What is VERVE-201 used for?

VERVE-201 is an investigational small molecule being developed for the treatment of hypercholesterolemia, a condition characterized by high cholesterol levels. It is also being studied in patients with refractory hyperlipidemia, which includes both hypercholesterolemia and hypertriglyceridemia. The drug is currently in Phase 1 clinical development.

What does VERVE-201 target?

VERVE-201 targets ANGPTL3, a protein that regulates lipid metabolism. By targeting ANGPTL3, the drug aims to address elevated cholesterol and triglyceride levels. This mechanism is being evaluated in a Phase 1b study for patients with refractory hyperlipidemia.

Who is developing VERVE-201?

VERVE-201 is being developed by Verve Therapeutics, Inc., a biopharmaceutical company traded on the Nasdaq under the ticker symbol VERV. The company is conducting a Phase 1b clinical trial of VERVE-201 in patients with refractory hyperlipidemia.

What phase is VERVE-201 in?

VERVE-201 is in Phase 1 clinical development. The ongoing trial is a Phase 1b study designed to evaluate the drug in patients with refractory hyperlipidemia. The study is currently recruiting participants and has not yet been completed.

What clinical trials is VERVE-201 in?

VERVE-201 is being studied in a Phase 1b clinical trial registered as NCT06451770. This trial is recruiting patients with refractory hyperlipidemia, including those with hypercholesterolemia and hypertriglyceridemia. The study is enrolling 36 participants across multiple countries, including the United States, Australia, Canada, the Netherlands, South Africa, and the United Kingdom.

Is VERVE-201 FDA approved?

VERVE-201 is not FDA approved. It is an investigational drug currently in Phase 1 clinical development. The ongoing Phase 1b trial is recruiting patients to evaluate the drug's safety and efficacy in treating refractory hyperlipidemia, but it has not yet received regulatory approval.