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VERVE-102

Phase 1

Heterozygous Familial Hypercholesterolemia | Small molecule | Cardiovascular |Verve Therapeutics, Inc.|Last Updated: Sep 2, 2026

Target and mechanism

Molecular targetPCSK9
Target classProtein
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment85

FDA Designations

No designations recorded

Clinical trial landscape

VERVE-102 · 1 trial · 2 indications

Phase 1 1
NCT06164730A Study of VERVE-102 in Patients With Familial Hypercholesterolemia or Premature Coronary Artery DiseaseHeterozygous Familial Hypercholesterolemia
RECRUITING85 Analytics
PHASE1RECRUITING
A Study of VERVE-102 in Patients With Familial Hypercholesterolemia or Premature Coronary Artery Disease
Heterozygous Familial HypercholesterolemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence of treatment-emergent adverse events (TEAEs) and serious adverse events (SAEs)
up to Day 365

Secondary Endpoints

Evaluation of maximum observed concentration (Cmax)
up to Day 365
Evaluation of time to maximum observed concentration (tmax)
up to Day 365
Evaluation of terminal elimination half-life (t1/2)
up to Day 365
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cohort 1: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-102.
Cohort 2: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-102.
Cohort 3: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-102.
Cohort 4: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-102.
Cohort 5: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-102.
Cohort 6: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-102.
Cohort 7: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-102.
Cohort 8: Single Ascending Dose EscalationEXPERIMENTALParticipants will receive a single dose of VERVE-102.
Cohort 9: Single Fixed DoseEXPERIMENTALParticipants will receive a single dose of VERVE-102.
Cohort 10: Single Fixed DoseEXPERIMENTALParticipants will receive a single dose of VERVE-102.

Interventions

NameTypeDescription
VERVE-102DRUGIntravenous (IV) infusion
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Eligibility Criteria

Age Range18 Years to 70 Years
SexALL
Healthy VolunteersNo
Study Sites27

Inclusion Criteria: * Diagnosis of HeFH or premature CAD Exclusion Criteria: * Homozygous familial hypercholesterolemia * Active or history of chronic liver disease * Current treatment with PCSK9 inhibitor or prior treatment within specified timeframe * Clinically significant or abnormal laborato...

Countries:United StatesAustraliaCanadaIsraelNew ZealandUnited Kingdom
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Recent Changes (Last 90 Days)

LOWSep 2, 2026NCT06164730primaryCompletionDate: changed
LOWSep 2, 2026NCT06164730primaryCompletionDate: changed
LOWSep 2, 2026NCT06164730primaryCompletionDate: changed
LOWAug 3, 2026NCT06164730lastUpdatePostDate: changed
LOWJul 13, 2026NCT06164730lastUpdatePostDate: changed
LOWJul 13, 2026NCT06164730lastUpdatePostDate: changed
LOWJun 29, 2026NCT06164730lastUpdatePostDate: changed
LOWJun 29, 2026NCT06164730lastUpdatePostDate: changed

Frequently asked questions about VERVE-102

What is VERVE-102 used for?

VERVE-102 is an investigational small molecule being developed for heterozygous familial hypercholesterolemia, a genetic condition causing high cholesterol. It is also being studied in patients with premature coronary artery disease. The drug is currently in Phase 1 clinical development and has not been approved by regulatory authorities.

What does VERVE-102 target?

VERVE-102 targets PCSK9, a protein that regulates cholesterol levels in the blood. By targeting PCSK9, the drug aims to lower LDL cholesterol in patients with heterozygous familial hypercholesterolemia. The drug is in Phase 1 clinical trials, and its mechanism of action is being evaluated in the ongoing study.

Who is developing VERVE-102?

VERVE-102 is being developed by Verve Therapeutics, Inc., a biopharmaceutical company traded on the Nasdaq under the ticker symbol VERV. The company is conducting a Phase 1 clinical trial of VERVE-102 in patients with familial hypercholesterolemia or premature coronary artery disease.

What phase is VERVE-102 in?

VERVE-102 is in Phase 1 clinical development. It is an investigational drug and has not been approved by the FDA or other regulatory agencies. The ongoing Phase 1 trial is recruiting participants to evaluate the safety and tolerability of VERVE-102 in patients with heterozygous familial hypercholesterolemia.

What clinical trials is VERVE-102 in?

VERVE-102 is being studied in a Phase 1 clinical trial registered as NCT06164730. This trial is recruiting an estimated 85 participants with heterozygous familial hypercholesterolemia or premature coronary artery disease. The study is being conducted in the United States, Australia, Canada, Israel, New Zealand, and the United Kingdom.