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amobarbital/One

Phase 1

Osteoarthritis | Small molecule | Musculoskeletal |United Therapeutics Corporation|Last Updated: Mar 26, 2024

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment5

FDA Designations

No designations recorded

Clinical trial landscape

amobarbital/One · 1 trial · 2 indications

Phase 1 1
NCT04589611Translating Metabolic Responses to Mechanical Insult Into Early Interventions to Prevent PTOAOsteoarthritis
COMPLETED5 Analytics
PHASE1COMPLETED
Translating Metabolic Responses to Mechanical Insult Into Early Interventions to Prevent PTOA
OsteoarthritisUnlock trial analytics

Study Endpoints

Primary Endpoints

Determine the number of participants with systemic adverse events including the change in laboratory values to assess the systemic safety of amobarbital.
Pre-op baseline on the day before external fixation surgery (within 24 hours of injury), immediately post-op, and at 1, 2, and 4 days post-op. At the time of internal fixation (3-21 days after external fixation) and at 1, 2, and 4 days post-op.]

By using CBC and standard clinical chemistry assays to quantify circulating, ALT, AST, Bilirubin, Creatinine, and BUN and the measurement of urine protein content, the number of participants that have abnormal laboratory values will be determined.

Determine the number of participants with a change of local toxicity in tissues.
Pre-op baseline on the day before external fixation surgery (within 24 hours of injury), immediately post-op, and at 1, 2, and 4 days post-op. At the time of internal fixation (3-21 days after external fixation) and at 1, 2, and 4 days post-op.

By using osteochondral fragments obtained during the internal fixation surgery, local toxicity will be determined by examining the tissue for cartilage and synovial histological changes.

Secondary Endpoints

Patient Reported Outcome Measurement Information Systems (PROMIS) - Pain Interference
3, 6, 12, and 24 months
Patient Reported Outcome Measurement Information Systems (PROMIS) Physical Function
Global Health - T-score - mean of 50 and a standard deviation (SD) of 10. Therefore a person with a T-score of 40 is one SD below the mean. Higher is better.
Patient Reported Outcome Measurement Information Systems (PROMIS) Global Health questionnaires.
3, 6, 12, and 24 months
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Study Design & Arms

AllocationRANDOMIZED
MaskingTRIPLE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Phase I single amobarbital/Gel-One doseEXPERIMENTALPhase I: An open label study of 3 patients will be done. If no dose limiting toxic (DLT) side effects occur, then an additional 3 patients will be done. If no DLT events occur, the study will proceed to Phase II.
Phase IIa Part 1 amobarbital/Gel-One doseACTIVE_COMPARATOR20 subjects will be randomized to amobarbital/Gel-One single dose.
Phase IIa Part 1 PlaceboPLACEBO_COMPARATOR10 subjects will be randomized to amobarbital/Gel-One single dose.
Phase IIa Part 2 amobarbital/Gel-One doseACTIVE_COMPARATOR20 subjects will be randomized to one dose of amobarbital/Gel-One during the initial surgical intervention. A second dose will be administered during the second surgical intervention.
Phase IIa Part 2 placeboPLACEBO_COMPARATOR20 subjects will be randomized to one dose of placebo during the initial surgical intervention. A second dose will be administered during the second surgical intervention.

Interventions

NameTypeDescription
amobarbital/Gel-One (one dose)DRUGOne dose of amobarbital/Gel-One during the initial surgical intervention
Placebo (single dose)DRUGOne dose of placebo during the initial surgical intervention
amobarbital/Gel-One (two doses)DRUGOne dose of amobarbital/Gel-One during the initial surgical intervention. A second dose will be administered during the second surgical intervention.
Placebo (two doses)DRUGOne dose of placebo during the initial surgical intervention. A second dose will be administered during the second surgical intervention.
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Eligibility Criteria

Age Range18 Years to 60 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Age 18-60 years * Acute closed or type 1 open ankle fractures (classified as OTA/AO 43 B 1-3 and 43 C 1- 3 or classified as 42 B and C fractures with 25% talar displacement and one of the following; syndesmosis injury or medial malleolar fracture at or above the shoulder) (Mar...

Countries:United States
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Frequently asked questions about amobarbital/One

What is amobarbital/One used for?

Amobarbital/One is an investigational small molecule being developed for osteoarthritis, including post-traumatic osteoarthritis. It is in Phase 1 clinical development and is not yet approved by the FDA. The drug is being studied in the context of early interventions to prevent post-traumatic osteoarthritis.

Who makes amobarbital/One?

Amobarbital/One is being developed by United Therapeutics Corporation, a publicly traded company listed on NASDAQ under the ticker symbol UTHR. The company is conducting clinical research on this investigational drug for osteoarthritis.

What phase is amobarbital/One in?

Amobarbital/One is in Phase 1 clinical development. It is an investigational drug and has not been approved by the FDA. One Phase 1 clinical trial has been completed, and the drug remains in early-stage clinical testing for osteoarthritis.

What clinical trials is amobarbital/One in?

Amobarbital/One has one completed Phase 1 clinical trial, registered as NCT04589611. The trial, titled "Translating Metabolic Responses to Mechanical Insult Into Early Interventions to Prevent PTOA," enrolled 5 participants in the United States and studied the drug in osteoarthritis and post-traumatic osteoarthritis.

Is amobarbital/One the same as amobarbital?

Amobarbital/One is a distinct drug asset being developed by United Therapeutics Corporation for osteoarthritis. It is a small molecule in Phase 1 clinical trials. No other alternative names for this drug have been disclosed in the available clinical trial information.