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Lapaquistat and atorvastatin

Phase 3

Hypercholesterolemia | Small molecule | Metabolic |Takeda Pharmaceutical Company Limited|Last Updated: May 24, 2012

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindACTIVE_CONTROLLEDBiomarker
Total Trials7
Total Enrollment4,649
FDA Designations
No designations recorded
Clinical Trials (7)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00286481Efficacy of Lapaquistat Acetate Alone or Combined With Simvastatin in Subjects With HypercholesterolemiaPHASE3 COMPLETED 1,362Mar 1, 2006May 1, 2007May 24, 201267 United States, Canada
NCT00868127Safety of Lapaquistat Acetate in Subjects With HypercholesterolemiaPHASE3 COMPLETED 574Dec 1, 2005Jul 1, 2007May 24, 2012 -
NCT00249912Efficacy of Lapaquistat Acetate Alone or Combined With Rosuvastatin in Subjects With HypercholesterolemiaPHASE3 COMPLETED 415Oct 1, 2005Apr 1, 2007May 24, 201292 United States, Canada
NCT00256178Efficacy of Lapaquistat Acetate and Simvastatin in Subjects With Primary Dyslipidemia.PHASE3 COMPLETED 411Oct 1, 2005Mar 1, 2007May 24, 201253 Czechia, Estonia +5
NCT00268697Efficacy of Lapaquistat Acetate Alone and With Ezetimibe in Subjects With Primary Dyslipidemia.PHASE3 COMPLETED 1,267Oct 1, 2005Jan 1, 2007May 24, 20129 Estonia, Latvia +2
NCT00143676Efficacy of Lapaquistat Acetate and Atorvastatin on Blood Cholesterol Levels in Subjects With Primary HypercholesterolemiaPHASE3 COMPLETED 448Aug 1, 2005Aug 1, 2006May 24, 201278 United States
NCT00864643Efficacy and Safety of Lapaquistat Acetate Coadministered With Atorvastatin in Subjects With HypercholesterolemiaPHASE2 COMPLETED 172Sep 1, 2004Feb 1, 2005May 24, 2012 -
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Study Endpoints
Primary Endpoints
Change from Baseline in Low Density Lipoprotein cholesterol
Week 12 or Final Visit
Adverse Events
Weeks 2, 4, 8, 12, 24, 36 and 48
Vital Signs
Weeks 2, 4, 8, 12, 24, 36 and 48
Clinical Laboratory Blood Sample for Lipid Panel
Weeks 2, 4, 8, 12, 24, 36 and 48
Clinical Laboratory Serum Chemistries
Weeks 2, 4, 8, 12, 24, 36 and 48
Clinical Laboratory Hematology
Weeks 2, 4, 8, 12, 24, 36 and 48
Clinical Laboratory Serum Human Chorionic Gonadotropin
Weeks 2, 4, 8, 12, 24, 36 and 48
Clinical Laboratory Urinalysis
Weeks 2, 4, 8, 12, 24, 36 and 48
Physical Examination
Week 48
12-lead Electrocardiogram
Week 48
Best Corrected Visual Acuity
Week 48
Change from Baseline in fasting plasma Low Density Lipoprotein cholesterol
Week 24 or Final Visit
Percent change from Baseline in Low Density Lipoprotein Cholesterol
Week 6
Secondary Endpoints
Adverse Events
Weeks: 2, 4, 8, and 12 or Final Visit
Physical Examination
Week 12 or Final Visit
Safety Laboratory Tests
Weeks: 2, 4, 8, and 12 or Final Visit
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelFACTORIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Lapaquistat Acetate 50 mg QD + SimvastatinEXPERIMENTAL -
Lapaquistat Acetate 100 mg QD + SimvastatinEXPERIMENTAL -
SimvastatinACTIVE_COMPARATOR -
Lapaquistat Acetate 100 mg QDEXPERIMENTAL -
Lapaquistat Acetate 100 mg QD + Added TherapyEXPERIMENTAL -
Lapaquistat Acetate 50 mg QD + RosuvastatinEXPERIMENTAL -
Lapaquistat Acetate 100 mg QD + RosuvastatinEXPERIMENTAL -
RosuvastatinACTIVE_COMPARATOR -
Lapaquistat Acetate 100 mg QD + EzetimibeEXPERIMENTAL -
EzetimibeACTIVE_COMPARATOR -
Lapaquistat Acetate 50 mg QD + AtorvastatinEXPERIMENTAL -
Lapaquistat Acetate 100 mg QD + AtorvastatinEXPERIMENTAL -
AtorvastatinACTIVE_COMPARATOR -
Lapaquistat Acetate 100 mg QD + Atorvastatin QDEXPERIMENTAL -
Atorvastatin QDACTIVE_COMPARATOR -
Interventions
NameTypeDescription
Lapaquistat acetate and simvastatinDRUGLapaquistat acetate 50 mg, tablets, orally, once daily and stable dose of simvastatin for up to 12 weeks.
SimvastatinDRUGLapaquistat acetate placebo-matching tablets, orally, once daily and stable dose of simvastatin for up to 12 weeks.
Lapaquistat acetateDRUGParticipants from 01-04-TL-475-008 Monotherapy Study: Lapaquistat acetate 100 mg, tablets, orally, once daily for up to 48 weeks.
Lapaquistat acetate and additional lipid-lowering therapyDRUGParticipants from 01-04-TL-475-009 Atorvastatin Add-on Study: Lapaquistat acetate 100 mg, tablets, orally, once daily and current Atorvastatin therapy for up to 4 weeks. Then, Lapaquistat 100 mg, tablets, orally, once daily and dose adjustment of Atorvastatin OR additional companion lipid-lowering therapy as needed for target LDL-C for up to 42 weeks.
Lapaquistat acetate and rosuvastatinDRUGLapaquistat acetate 50 mg, tablets, orally, once daily and stable Rosuvastatin therapy (10 or 20 mg) for up to 24 weeks.
RosuvastatinDRUGLapaquistat acetate placebo-matching tablets, orally, once daily and stable Rosuvastatin therapy (10 or 20 mg) for up to 24 weeks.
Lapaquistat acetate and ezetimibeDRUGLapaquistat acetate 100 mg, tablets, orally, once daily and stable ezetimibe therapy for up to 24 weeks.
EzetimibeDRUGLapaquistat acetate placebo-matching tablets, orally, once daily and stable ezetimibe therapy for up to 24 weeks.
Lapaquistat acetate and atorvastatinDRUGLapaquistat acetate 50 mg, tablets, orally, once daily and Atorvastatin 10 mg to 40 mg stable dose for up to 24 weeks.
AtorvastatinDRUGLapaquistat acetate placebo-matching tablets, orally, once daily and Atorvastatin 10 mg to 40 mg stable dose for up to 24 weeks.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites67

Inclusion Criteria: * Woman of childbearing potential can not to be pregnant, lactating, not planning on becoming pregnant, and agree to use acceptable forms of contraception throughout the course of the study. * Prior to Randomization, has a low-density lipoprotein cholesterol level mean greater t...

Countries:United StatesCanadaCzechiaEstoniaFinlandGermanyPolandSouth AfricaUnited KingdomLatviaRussiaSerbia
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