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CERE-110: Adeno-Associated Virus Delivery of NGF

Phase 1

Alzheimer's Disease | Gene therapy | Neurology |Sangamo Therapeutics, Inc.|Last Updated: Nov 10, 2022

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMC
Total Trials1
Total Enrollment10

FDA Designations

No designations recorded

Clinical trial landscape

CERE-110: Adeno-Associated Virus Delivery of NGF · 1 trial · 1 indication

Phase 1 1
NCT00087789CERE-110 in Subjects With Mild to Moderate Alzheimer's DiseaseAlzheimer's Disease
COMPLETED10 Analytics
PHASE1COMPLETED
CERE-110 in Subjects With Mild to Moderate Alzheimer's Disease
Alzheimer's DiseaseUnlock trial analytics

Study Endpoints

Primary Endpoints

Safety and tolerability of three different doses of CERE-110 in subjects with mild to moderate Alzheimer's disease
24 months
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Interventions

NameTypeDescription
CERE-110: Adeno-Associated Virus Delivery of NGFGENETICCERE-110 2.0 x 10\^10 vg, CERE-110 1.0 x 10\^11 vg, CERE-110 2.0 x 10\^11 vg
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Eligibility Criteria

Age Range50 Years to 80 Years
SexALL
Healthy VolunteersNo
Study Sites2

Inclusion Criteria: * Alzheimer's disease as determined by NINCDS/ADRDA criteria. * Score of ≤ 4 on a modified Hachinski Ischemia Scale * Mini-Mental State Exam (MMSE) score in the range of 16 to 28, inclusive * No significant neurological or medical abnormalities contraindicating surgery, MRI/PET ...

Countries:United States
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Frequently asked questions about CERE-110: Adeno-Associated Virus Delivery of NGF

What is CERE-110 used for in Alzheimer's Disease?

CERE-110 is an investigational gene therapy being studied for the treatment of mild to moderate Alzheimer's Disease. It delivers nerve growth factor (NGF) via an adeno-associated virus vector. The therapy is designed to potentially slow or prevent the degeneration of cholinergic neurons, which are affected in Alzheimer's Disease.

Who is developing CERE-110?

CERE-110 is being developed by Sangamo Therapeutics, Inc., a biopharmaceutical company traded on the Nasdaq under the ticker symbol SGMO. The company is focused on gene therapy and genome editing technologies.

What phase is CERE-110 in?

CERE-110 is in Phase 1 clinical development. It has completed a Phase 1 trial in patients with mild to moderate Alzheimer's Disease. The drug is investigational and has not been approved by the FDA.

What clinical trials is CERE-110 in?

CERE-110 has been studied in one clinical trial, identified as NCT00087789. This Phase 1 trial, titled 'CERE-110 in Subjects With Mild to Moderate Alzheimer's Disease,' was conducted in the United States and enrolled 10 participants aged 50 years and older. The trial has been completed.

Is CERE-110 the same as adeno-associated virus delivery of NGF?

Yes, CERE-110 is also known as Adeno-Associated Virus Delivery of NGF. This name reflects its mechanism of using an adeno-associated virus vector to deliver nerve growth factor (NGF) to the brain.