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RO7303509

Phase 1

Systemic Sclerosis | Small molecule | Immunology |Roche Holding AG|Last Updated: Jul 20, 2025

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindCONTROLLEDDMC
Total Trials1
Total Enrollment56

FDA Designations

No designations recorded

Clinical trial landscape

RO7303509 · 1 trial · 1 indication

Phase 1 1
NCT05462522A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of RO7303509 in Participants With Systemic SclerosisSystemic Sclerosis
COMPLETED56 Analytics
PHASE1COMPLETED
A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of RO7303509 in Participants With Systemic Sclerosis
Systemic SclerosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants With Treatment Emergent Adverse Events (TEAEs)
Up to approximately 17 months
Number of Participants With Clinically Significant Change From Baseline in Vital Signs
Up to approximately 17 months
Number of Participants With Clinically Significant Change From Baseline in Clinical Laboratory Test Results
Up to approximately 17 months
Number of Participants With Clinically Significant Change From Baseline in Electrocardiogram (ECG) Parameters
Up to approximately 17 months

Secondary Endpoints

MAD Stage: Maximum Serum Concentration (Cmax) of RO7303509
Predose on Day 1 and at multiple timepoints up to Day 113 or early termination (ET) visit
MAD Stage: Area Under the Concentration vs Time Curve (AUC) of RO7303509
Predose on Day 1 and at multiple timepoints up to Day 113 or ET visit
MAD Stage: Time to Maximum Concentration (Tmax) of RO7303509
Predose on Day 1 and at multiple timepoints up to Day 113 or ET visit
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
MAD StageEXPERIMENTALParticipants will be randomized in a ratio of 4:1 to receive RO7303509 or placebo, as subcutaneous (SC) injection, one time per month for 3 months. You have a 20% chance of getting placebo.
OSE StageEXPERIMENTALEvery participant in the OSE stage will receive study drug and no participant will receive placebo. Participants will receive RO7303509 as SC injection at the same dose as that administered during the MAD stage, one time per month for up to a year.

Interventions

NameTypeDescription
RO7303509DRUGRO7303509 will be administered as SC injection monthly, as specified in each treatment group.
PlaceboDRUGRO7303509 matching placebo will be administered as SC injection monthly, during the MAD stage.
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites25

Inclusion Criteria: Inclusion Criteria for the MAD Stage: * Weight of 45-150 kg at screening * Diagnosis of SSc, as defined by 2013 American College of Rheumatology (ACR)/European League Against Rheumatism (EULAR) criteria and ≤ 10 years disease duration from first non-Raynaud's symptom * Agreemen...

Countries:United StatesArgentinaBelgiumFranceIsraelPolandPortugalPuerto RicoSerbiaSpainUnited Kingdom
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Frequently asked questions about RO7303509

What is RO7303509 used for in systemic sclerosis?

RO7303509 is an investigational small molecule being studied for the treatment of systemic sclerosis, a chronic autoimmune disease that causes hardening and tightening of the skin and connective tissues. It is currently in Phase 1 clinical development and has not been approved by regulatory authorities.

Who makes RO7303509?

RO7303509 is being developed by Roche Holding AG, a multinational healthcare company. Roche's stock is traded on the OTC market under the ticker symbol RHHBY. The drug is in Phase 1 clinical trials for systemic sclerosis.

What phase is RO7303509 in?

RO7303509 is in Phase 1 clinical development. A Phase 1 study evaluating its safety, tolerability, and pharmacokinetics in participants with systemic sclerosis has been completed. The drug is investigational and has not received regulatory approval.

What clinical trials is RO7303509 in?

RO7303509 has one completed clinical trial, identified as NCT05462522. This Phase 1 study evaluated the safety, tolerability, and pharmacokinetics of the drug in 56 participants with systemic sclerosis. The trial was conducted across multiple countries, including the United States, Argentina, Belgium, France, Israel, Poland, Portugal, Puerto Rico, Serbia, Spain, and the United Kingdom.

Is RO7303509 a small molecule?

Yes, RO7303509 is a small molecule drug. It is being developed as a potential treatment for systemic sclerosis and is currently in Phase 1 clinical trials. The drug is administered to adult participants aged 18 years and older.