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Donepezil

Phase 3

Alzheimer Disease | Small molecule | Neurology |Pfizer, Inc.|Last Updated: Apr 19, 2021

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment249

FDA Designations

No designations recorded

Clinical trial landscape

Donepezil · 3 trials · 4 indications

Phase 3 2Phase 2 1
NCT00096473Efficacy and Safety of Aricept in the Treatment of Severe Alzheimer's DiseaseAlzheimer's Disease
COMPLETED229 Analytics
NCT00630851A Study of the Efficacy and Safety of Aricept in Patients With Severe Alzheimer's Disease Who Are Living in Skilled Nursing HomesAlzheimer Disease
COMPLETED249 Analytics
PHASE3COMPLETED
Efficacy and Safety of Aricept in the Treatment of Severe Alzheimer's Disease
Alzheimer's DiseaseUnlock trial analytics
PHASE3COMPLETED
A Study of the Efficacy and Safety of Aricept in Patients With Severe Alzheimer's Disease Who Are Living in Skilled Nursing Homes
Alzheimer DiseaseUnlock trial analytics

Study Endpoints

Primary Endpoints

Assessments of global and cognitive function of Severe AD patients
Change from baseline in modified Alzheimer's Disease Cooperative Study Activities of Daily Living Inventory for Severe Alzheimer's Disease (ADCS-ADL-severe) total score
Month 6
Change from baseline in Severe Impairment Battery (SIB) total score
Month 6
Mean Change From Baseline in V-Scale Composite Score (Sum of 9 Sub-Domains) of Vineland Adaptive Behavior Scales Second Edition-Parent Caregiver Rating Form (VABS-II/PCRF) at Week 10-Last Observation Carried Forward (LOCF)
Baseline, Week 10

The VABS-II/PCRF instrument was used in this study to assess 3 domains (each with 3 sub-domains): communication (sub-domains: receptive, expressive, and writing), daily living skills (sub-domains: personal, domestic, community), and socialization (sub-domains: interpersonal relationships, play/leisure time, coping skills). Raw scores (2=always present, 1=sometimes present, 0=seldom or never present) rated by the parent/caregiver from each sub-domain were converted to standardized scores called V-scores, which are based on age and a national sample of normal children. Each sub-domain v-scale score ranged from 1 (weakness) to 24 (strength). V-scores for the 9 sub-domains were summed to obtain a composite V-score ranging from 9 to 216. Higher scores indicate a higher level of adaptive functioning. A positive change from baseline indicates an improvement in adaptive functioning. Composite V-scores have a mean (50th percentile) of 100 and a standard deviation (SD) of 15.

Secondary Endpoints

Assessment of behavior and performance on Activity of Daily Living in severe AD patients
Assessment of caregiver burden
Change from baseline in SIB total score
Month 3
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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
1EXPERIMENTAL -
2PLACEBO_COMPARATOR -
Donepezil HClACTIVE_COMPARATOR -
PlaceboPLACEBO_COMPARATOR -

Interventions

NameTypeDescription
Donepezil hydrochlorideDRUG -
Donepezil (Aricept)DRUGDonepezil (Aricept) 5 mg tablet orally once daily for 30 days, followed by 10 mg tablet orally once daily to complete 6 months of treatment
PlaceboDRUGMatching placebo tablets orally once daily for 6 months
Donepezil HClDRUGBlinded donepezil 2.5 milligram per day (mg/day) (2.5 milliliter per day \[mL/day\]) orally for participants with body weight (BW) 20 and less than (\<) 25 kilogram (kg), 5 mg/day (5 mL/day) orally for participants with BW 25 to \<50 kg, and 10 mg/day (10 mL/day) orally for participants with BW greater than or equal to (\>=) 50 kg liquid formulation (1 milligram per 1 milliliter \[1 mg/1 mL\]) (titrated to 0.1 to 0.2 milligram per kilogram per day \[mg/kg/day\] based on BW).
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Eligibility Criteria

Age Range50 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites42

Inclusion Criteria: * Clinically diagnosed Alzheimer's Disease with MMSE score 1\~12 * Have not been treated by any medication for Alzheimer's Disease in past 3 months * Live in community or Assisted Living Facility * Healthy or with chronic diseases that are medically controlled or stabilized * Ab...

Countries:United StatesAustraliaCanadaFranceIrelandUnited KingdomSweden
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Frequently asked questions about Donepezil

What is Donepezil used for?

Donepezil is used for Alzheimer's Disease, including severe Alzheimer's Disease and dementia, and for cognitive dysfunction in children with Down Syndrome. It is being studied in clinical trials for these conditions, with completed trials in Alzheimer's Disease and Down Syndrome.

What does Donepezil target?

Donepezil is a small molecule that targets the cholinergic system, specifically inhibiting acetylcholinesterase, which increases acetylcholine levels in the brain. This mechanism is relevant to cognitive symptoms in Alzheimer's Disease and Down Syndrome.

Who makes Donepezil?

Donepezil is developed by Pfizer, Inc., which trades under the ticker PFE. The company is conducting clinical trials for the drug in Alzheimer's Disease and Down Syndrome.

What phase is Donepezil in?

Donepezil is in Phase 3 clinical development for Alzheimer's Disease, with completed Phase 3 trials. It has also completed a Phase 2 trial for Down Syndrome. It is investigational and not yet approved for these indications.

What clinical trials is Donepezil in?

Donepezil has completed several clinical trials, including NCT00096473 for severe Alzheimer's Disease, NCT00570128 for Down Syndrome, and NCT00630851 for severe Alzheimer's Disease in nursing homes. These trials were placebo-controlled and double-blind.

Is Donepezil the same as Aricept?

Yes, Donepezil is also known as Aricept. Clinical trials such as NCT00096473 and NCT00630851 refer to Aricept, while NCT00570128 uses the name Donepezil Hydrochloride (HCl) (Aricept).