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EGF816

Phase 1

Advanced Non-small Cell Lung Cancer | Small molecule | Oncology |Novartis AG|Last Updated: Jan 16, 2026

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment225

FDA Designations

No designations recorded

Clinical trial landscape

EGF816 · 2 trials · 2 indications

Phase 1 2
NCT03333343Study of EGF816 in Combination With Selected Targeted Agents in EGFR-mutant NSCLCEGFR-mutant Non-small Cell Lung Cancer
ACTIVE NOT_RECRUITING105 Analytics
NCT02108964A Phase I/II, Multicenter, Open-label Study of EGFRmut-TKI EGF816, Administered Orally in Adult Patients With EGFRmut Solid MalignanciesAdvanced Non-small Cell Lung Cancer
COMPLETED225 Analytics
PHASE1ACTIVE NOT_RECRUITING
Study of EGF816 in Combination With Selected Targeted Agents in EGFR-mutant NSCLC
EGFR-mutant Non-small Cell Lung CancerUnlock trial analytics
PHASE1COMPLETED
A Phase I/II, Multicenter, Open-label Study of EGFRmut-TKI EGF816, Administered Orally in Adult Patients With EGFRmut Solid Malignancies
Advanced Non-small Cell Lung CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of patients with adverse events and serious adverse events
Every day until study end, approximately 4 years

Assess safety and tolerability including incidence of dose limiting toxicities, adverse events, and serious adverse events.

Number of participants with DLTs in the first cycle of combination (Dose escalation only)
28 days

A Dose-Limiting Toxicity (DLT) is defined as an adverse event or abnormal laboratory value of Common Terminology Criteria for Adverse Events (CTCAE) grade ≥ 3 assessed as unrelated to disease, disease progression, inter-current illness or concomitant medications that occurs within the first 28 days of combination treatment during the dose escalation part of the study. Other clinically significant toxicities may be considered to be DLTs, even if not CTCAE grade 3 or higher.

Number of participants with dose interruptions and reductions
From first dose until study ends, approximately 4 years

Assessment of tolerability. For patients who do not tolerate the protocol-specified dosing schedule, dose adjustments may be permitted in order to allow patients to continue the study treatment.

Dose intensity of study drugs
From first dose until study ends, approximately 4 years

Dose intensity is computed as the ratio of actual cumulative dose received to actual duration of exposure.

ORR2
Every 8-12 weeks until study ends, approximately 4 years

Modified objective response rate (ORR2) per RECIST v1.1 (taking as baseline the most recent assessment prior to initiating combination)

Number of Participants With Dose Limiting Toxicities (DLTs) (Phase I Part)
First 28 days of dosing

Number of participants with DLTs during the first 28 days of therapy. A DLT is defined as an adverse event or abnormal laboratory value assessed as unrelated to disease, disease progression, inter-current illness, or concomitant medications that occurs within the first cycle of treatment with EGF816 and meets any of the criteria described in the protocol. A participant with multiple occurrences of DLTs under one treatment is counted only once.

Overall Response Rate (ORR) by Blinded Independent Review Committee (BIRC) (Phase II Part)
From baseline up to 64 weeks

ORR is defined as the percentage of patients with a best overall response of complete response (CR) or partial response (PR) determined by BIRC assessment in accordance to Response Evaluation Criteria in Solid Tumors (RECIST 1.1).

Secondary Endpoints

ORR
Every 8-12 weeks until study ends, approximately 4 years
PFS
Every 8-12 weeks until study ends, approximately 4 years
DCR
Every 8-12 weeks until study ends, approximately 4 years
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Arm 1EXPERIMENTALEGF816+ trametinib in escalation phase
Arm 2EXPERIMENTALEGF816 + ribociclib in escalation phase
Arm 3EXPERIMENTALEGF816 + LXH254 in escalation phase
Arm AEXPERIMENTALEGF816 + INC280 in expansion phase (patients with no known resistance mechanism)
Arm BEXPERIMENTALEGF816 + trametinib in expansion phase
Arm CEXPERIMENTALEGF816 + ribociclib in expansion phase
Arm DEXPERIMENTALEGF816 + LXH254 in expansion phase (patients with no known resistance mechanism)
Arm EEXPERIMENTALEGF816 + LXH254 in expansion phase (patients with known resistance mechanism)
Arm FEXPERIMENTALEGF816 + gefitinib in expansion phase
Arm GEXPERIMENTALEGF816 + INC280 in expansion phase (patients with known resistance mechanism)
Phase I partEXPERIMENTALParticipants with locally advanced or metastatic NSCLC harboring specific EGFR mutations will be administered escalated doses of EGF816 orally once a day as continuous daily dosing in each cycle (of 28 days) during Phase I part of the study. The starting dose for the Phase I part first cohort of patients will be 75 mg once per day capsule.
Phase II partEXPERIMENTALTreatment naïve participants with locally advanced or metastatic NSCLC harboring EGFR mutations will be administered with EGF816 at RP2D during Phase II part of the study.

Interventions

NameTypeDescription
EGF816DRUGStudy Drug
trametinibDRUGStudy Drug
ribociclibDRUGStudy Drug
LXH254DRUGStudy Drug
INC280DRUGStudy Drug
gefitinibDRUGStudy Drug
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Eligibility Criteria

Age Range18 Years to 100 Years
SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria: * Patients must have histologically or cytologically confirmed locally advanced (stage IIIB) or metastatic (stage IV) EGFR mutant (ex19del, L858R) NSCLC. * Requirements of EGFR mutation status and prior lines of treatment: * Treatment naive patients, who have locally advanced or...

Countries:CanadaGermanyHong KongItalySingaporeTaiwanUnited StatesJapanNetherlandsSouth KoreaSpain
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Competitive Landscape -Non-Small Cell Lung Cancer 389 trials (matched to "Advanced Non-small Cell Lung Cancer")

Frequently asked questions about EGF816

What is EGF816 used for?

EGF816 is an investigational small molecule being studied for the treatment of EGFR-mutant non-small cell lung cancer and advanced non-small cell lung cancer. It is administered orally and is currently in Phase 1 clinical development.

Who makes EGF816?

EGF816 is being developed by Novartis AG, a multinational pharmaceutical company listed on the New York Stock Exchange under the ticker symbol NVS.

What phase is EGF816 in?

EGF816 is in Phase 1 clinical development. It is an investigational drug and has not been approved by regulatory authorities. Clinical trials are ongoing to evaluate its safety and efficacy.

What clinical trials is EGF816 in?

EGF816 is being studied in two Phase 1 clinical trials. NCT02108964 is a completed study in patients with advanced non-small cell lung cancer, and NCT03333343 is an active, not recruiting study of EGF816 in combination with selected targeted agents in EGFR-mutant non-small cell lung cancer.

How does EGF816 work?

EGF816 is an EGFR-mutant tyrosine kinase inhibitor (TKI) that targets mutated forms of the epidermal growth factor receptor. By inhibiting this target, it aims to block signaling pathways that drive tumor growth in EGFR-mutant cancers.

Is EGF816 the same as nazartinib?

EGF816 is also known as nazartinib. It is an investigational EGFR inhibitor being developed by Novartis for the treatment of EGFR-mutant non-small cell lung cancer.