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BTRX-246040

Phase 2

Major Depressive Disorder | Small molecule | Psychiatry |Neumora Therapeutics, Inc.|Last Updated: Jun 24, 2025

Success Probability

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment104

FDA Designations

No designations recorded

Clinical trial landscape

BTRX-246040 · 2 trials · 3 indications

Phase 2 2
NCT03608371BTRX-246040 Study in Participants With Parkinson's Disease With Motor FluctuationsParkinson Disease
COMPLETED24 Analytics
NCT03193398BTRX-246040 Administered Once Daily to Patients With Major Depressive DisorderMajor Depressive Disorder
COMPLETED104 Analytics
PHASE2COMPLETED
BTRX-246040 Study in Participants With Parkinson's Disease With Motor Fluctuations
Parkinson DiseaseUnlock trial analytics
PHASE2COMPLETED
BTRX-246040 Administered Once Daily to Patients With Major Depressive Disorder
Major Depressive DisorderUnlock trial analytics

Study Endpoints

Primary Endpoints

Maximal Change in UPDRS Part III From Predose to Postdose on Day 1
From pre-dose to 8 hours post-dose on Day 1

UPDRS = Unified Parkinson's Disease Rating Scale. The Unified Parkinson's Disease Rating Scale (UPDRS) Part III is a 14-item rating scale, which consists of the motor examination. Each item is scored from 0 (Normal) to 4 (Most severe). The score ranges from 0-56.

Change in Investigator-administered MADRS Total Score From Baseline BTRX-246040 and Placebo
Week 8

The Investigator-administered MADRS includes 10 items assessing the following symptoms: apparent sadness, reported sadness, inner tension, reduced sleep, reduced appetite, concentration difficulties, lassitude, inability to feel, pessimistic thoughts, and suicidal thoughts. Each item is scored from 0 (absence of symptom) to 6 (severe symptom); the overall score ranges from 0 to 60. MADRS total scores from 0 to 6 indicate normal/symptom absent, from 7 to 19 indicate mild depression, from 20 to 34 indicate moderate depression, and from 35 to 60 indicate severe depression.

Secondary Endpoints

Duration of ON Time on Day 1
From dose to 8 hours post-dose on Day 1
Percentage of Participants Who Turned ON on Day 1
From dose to 8 hours post-dose on Day 1
Time to ON on Day 1
From dose to 8 hours post-dose on Day 1
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
BTRX-246040 Cohort 1EXPERIMENTALBTRX-246040 40 mg administered orally
BTRX-246040 Cohort 2EXPERIMENTALBTRX-246040 80 mg administered orally
BTRX-246040 Cohort 3EXPERIMENTALBTRX-246040 120 mg administered orally
Placebo Cohorts 1-3PLACEBO_COMPARATORPlacebo is administered orally at the same number of capsules as active drug in each Cohort. Placebo capsules consist of inactive ingredients and look identical to BTRX-246040.
BTRX-246040EXPERIMENTAL40 mg administered orally as 1 capsule QD for 1 week, followed by 80 mg as 2 capsules QD for 7 weeks.
PlaceboPLACEBO_COMPARATORadministered orally as 1 capsule QD for 1 week, followed by 2 capsules QD for 7 weeks.

Interventions

NameTypeDescription
BTRX-246040DRUGoral capsule
PlaceboDRUGoral capsule matching BTRX-246040 capsule
BTRX-246040 oral capsule(s)DRUGBTRX-246040 administered once daily to patients with MDD for 8 weeks
Placebo oral capsule(s)DRUGadministered once daily to patients with MDD for 8 weeks
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Eligibility Criteria

Age Range30 Years to 76 Years
SexALL
Healthy VolunteersNo
Study Sites4

Inclusion Criteria: * Diagnosed with Parkinson's disease (PD), consistent with the United Kingdom PD Society Brain Bank Criteria for the Diagnosis of PD * Men or women ≥ 30 years old and ≤ 76 years old * Female participants must be either surgically sterilized or 2 years post menopausal at screenin...

Countries:United States
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Frequently asked questions about BTRX-246040

What is BTRX-246040 used for?

BTRX-246040 is an investigational small molecule being studied for the treatment of Major Depressive Disorder and Parkinson's Disease with motor fluctuations. It is developed by Neumora Therapeutics, Inc. (NASDAQ: NMRA) and is currently in Phase 2 clinical development.

What does BTRX-246040 target?

BTRX-246040 is a small molecule that targets the nociceptin/orphanin FQ peptide receptor. This receptor is involved in modulating various neurological and psychiatric functions, and its modulation is being explored for potential therapeutic effects in depression and Parkinson's disease.

Who makes BTRX-246040?

BTRX-246040 is developed by Neumora Therapeutics, Inc., a biopharmaceutical company traded on NASDAQ under the ticker symbol NMRA. The company is advancing this investigational drug through clinical trials for psychiatric and neurological indications.

What phase is BTRX-246040 in?

BTRX-246040 is in Phase 2 clinical development. Two Phase 2 trials have been completed, one in Major Depressive Disorder and one in Parkinson's Disease with motor fluctuations. The drug is investigational and has not been approved by regulatory authorities.

What clinical trials is BTRX-246040 in?

BTRX-246040 has completed two Phase 2 clinical trials. NCT03193398 evaluated the drug in 104 patients with Major Depressive Disorder in the United States. NCT03608371 studied 24 participants with Parkinson's Disease and motor fluctuations. Both trials were randomized, double-blind, and placebo-controlled.

Is BTRX-246040 the same as any other drug?

BTRX-246040 is the sole name provided for this investigational compound. No alternative names have been reported in the clinical trial records. It is being studied under this identifier in trials for Major Depressive Disorder and Parkinson's Disease.