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Treprostinil

Phase 1

Pulmonary Arterial Hypertension | Small molecule | Cardiovascular |MannKind Corporation|Last Updated: Oct 30, 2018

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment36

FDA Designations

No designations recorded

Clinical trial landscape

Treprostinil · 1 trial · 1 indication

Phase 1 1
NCT03464864Pharmacokinetics, Safety and Tolerability of Treprostinil Inhalation Powder in Healthy Normal VolunteersPulmonary Arterial Hypertension
COMPLETED36 Analytics
PHASE1COMPLETED
Pharmacokinetics, Safety and Tolerability of Treprostinil Inhalation Powder in Healthy Normal Volunteers
Pulmonary Arterial HypertensionUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence and severity of treatment-related adverse events (safety and tolerability) of single ascending doses of Treprostinil Inhalation Powder
At protocol-specified time points from the time of screening (day 0) to end of study (day 6)

Incidence and severity of treatment-related adverse events determined by changes from screening (baseline) of findings from physical examinations, laboratory evaluations, vital signs measurements, pulmonary testing, and ECG measurements.

Secondary Endpoints

Systemic exposure and pharmacokinetics of treprostinil administered as Treprostinil Inhalation Powder in healthy normal volunteers
At protocol-specified time points throughout day 1
Dose proportionality
10 months
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeOTHER

Treatment Arms

ArmTypeDescription
Treprostinil Inhalation Powder 30 mcgEXPERIMENTAL -
Treprostinil Inhalation Powder 60 mcgEXPERIMENTAL -
Treprostinil Inhalation Powder 90 mcgEXPERIMENTAL -
Treprostinil Inhalation Powder 120 mcgEXPERIMENTAL -
Treprostinil Inhalation Powder 150 mcgEXPERIMENTAL -
Treprostinil Inhalation Powder 180 mcgEXPERIMENTAL -
Treprostinil Inhalation Powder 240 mcgEXPERIMENTAL -
Treprostinil Inhalation Powder 300 mcgEXPERIMENTAL -

Interventions

NameTypeDescription
Treprostinil Inhalation PowderDRUGSingle ascending dose
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Eligibility Criteria

Age Range18 Years to 55 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria: 1. Voluntarily consents to participate in this study and provides written informed consent prior to the start of any study-specific procedures. 2. Male or female. Females must not be pregnant or breastfeeding. 3. Is between 18 and 55 years of age (inclusive). 4. Female subjects ...

Countries:United States
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Frequently asked questions about Treprostinil

What is Treprostinil used for?

Treprostinil is an investigational small molecule being developed for the treatment of Pulmonary Arterial Hypertension (PAH), a type of high blood pressure affecting the arteries in the lungs. It is currently in Phase 1 clinical development, meaning it has not yet been approved by regulatory authorities and remains under investigation for safety and efficacy.

Who makes Treprostinil?

Treprostinil is being developed by MannKind Corporation, a biopharmaceutical company traded on the NASDAQ under the ticker symbol MNKD. The company is conducting clinical trials to evaluate the drug's pharmacokinetics, safety, and tolerability in patients with Pulmonary Arterial Hypertension.

What phase is Treprostinil in?

Treprostinil is in Phase 1 clinical development. A Phase 1 trial has been completed, which focused on evaluating the drug's pharmacokinetics, safety, and tolerability in healthy volunteers. The drug is investigational and has not received FDA approval for any indication.

What clinical trials is Treprostinil in?

Treprostinil has one completed clinical trial registered under NCT03464864, titled "Pharmacokinetics, Safety and Tolerability of Treprostinil Inhalation Powder in Healthy Normal Volunteers." This Phase 1 study enrolled 36 participants in the United States and was a controlled, open-label trial involving healthy adults aged 18 years and older.

How does Treprostinil work?

Treprostinil is a small molecule designed to treat Pulmonary Arterial Hypertension. While the specific molecular target is not disclosed, the drug is being developed as an inhalation powder intended to deliver the medication directly to the lungs, potentially improving local delivery and reducing systemic side effects compared to other routes of administration.