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Prochymal adult human mesenchymal stem cells

Phase 3

Crohn's Disease | Small molecule | Gastrointestinal |Mesoblast Limited|Last Updated: Mar 11, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindCONTROLLEDDMC
Total Trials2
Total Enrollment108

FDA Designations

No designations recorded

Clinical trial landscape

Prochymal adult human mesenchymal stem cells · 2 trials · 1 indication

Phase 3 1Phase 2 1
NCT00543374Extended Evaluation of PROCHYMAL® Adult Human Stem Cells for Treatment-Resistant Moderate-to-Severe Crohn's DiseaseCrohn's Disease
COMPLETED98 Analytics
PHASE3COMPLETED
Extended Evaluation of PROCHYMAL® Adult Human Stem Cells for Treatment-Resistant Moderate-to-Severe Crohn's Disease
Crohn's DiseaseUnlock trial analytics

Study Endpoints

Primary Endpoints

Duration of clinical benefit (Crohn's disease activity index)
6 months
Re-induction of clinical benefit (Crohn's disease activity index)
6 months
Number of Participants with Reduction in Crohn's Disease Activity Index (CDAI) of at Least 100 Points
28 days

The CDAI is a composite index of 8 disease variables (stool frequency, severity of abdominal pain, degree of general well-being, presence or absence of extra-intestinal manifestations or fistula, use or non-use of antidiarrheal agents, presence or absence of an abdominal mass, hematocrit, and body weight). Scores range from approximately 0 to 600, with a higher score indicating more disease activity.

Secondary Endpoints

Improvement in quality of life (Inflammatory Bowel Disease Questionnaire [IBDQ] instrument)
6 months
Number of Participants with Reduction in CDAI of at Least 70 points
28 days
Improvement as Assessed by the Inflammatory Bowel Disease Questionnaire (IBDQ)
28 days
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
PlaceboPLACEBO_COMPARATORPlacebo
PROCHYMAL Low doseACTIVE_COMPARATORLow dose (total of 600 million cells).
PROCHYMAL High doseACTIVE_COMPARATORHigh dose (total of 1200 cells).
High doseEXPERIMENTALHigh dose (8 million cells per kg of body weight)
Low doseEXPERIMENTALLow dose: 2 million cells per kg body weight

Interventions

NameTypeDescription
PlaceboDRUG -
PROCHYMAL adult human mesenchymal stem cellsDRUGintravenous infusion four times over two weeks; possibly repeated once
Prochymal™ adult human mesenchymal stem cellsDRUGCells in plasmalyte and containing dimethylsulfoxide
adult human mesenchymal stem cellsDRUGtwo infusions, one week apart, each comprising adult human mesenchymal stem cells
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Eligibility Criteria

Age Range18 Years to 70 Years
SexALL
Healthy VolunteersNo
Study Sites58

Inclusion Criteria: * Participation in Osiris Protocol 603, with drop of at least 100 points in CDAI at Day 28 Exclusion Criteria: * Substance abuse * Failure to receive full dose of all interventions in Protocol 603

Countries:United StatesCanada
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Frequently asked questions about Prochymal adult human mesenchymal stem cells

What is Prochymal adult human mesenchymal stem cells used for in Crohn's Disease?

Prochymal adult human mesenchymal stem cells is an investigational therapy being studied for the treatment of moderate-to-severe Crohn's Disease, including treatment-resistant cases. It is a cell-based product derived from adult human mesenchymal stem cells. The therapy is currently in clinical development and has not been approved by regulatory authorities.

Who makes Prochymal adult human mesenchymal stem cells?

Prochymal adult human mesenchymal stem cells is being developed by Mesoblast Limited, a biopharmaceutical company. Mesoblast is focused on developing regenerative medicine products. The company's stock is traded under the ticker symbol MESO on the NASDAQ exchange.

What phase is Prochymal adult human mesenchymal stem cells in?

Prochymal adult human mesenchymal stem cells is in Phase 3 clinical development for Crohn's Disease. The Phase 3 trial, NCT00543374, has been completed. The therapy is investigational and has not received FDA approval. It is still undergoing clinical evaluation to determine its safety and efficacy.

What clinical trials is Prochymal adult human mesenchymal stem cells in?

Prochymal adult human mesenchymal stem cells has been studied in two completed clinical trials. The first, NCT00294112, was a Phase 2 study in 10 patients with moderate-to-severe Crohn's Disease in the United States. The second, NCT00543374, was a Phase 3 study in 98 patients with treatment-resistant moderate-to-severe Crohn's Disease in the United States and Canada.

Is Prochymal adult human mesenchymal stem cells the same as adult human mesenchymal stem cells?

Prochymal adult human mesenchymal stem cells is a specific product name for a therapy consisting of adult human mesenchymal stem cells. The product is also referred to as PROCHYMAL in clinical trial documentation. It is being developed by Mesoblast Limited for the treatment of Crohn's Disease.