Recent Updates
Recently added Catalysts

LOXO-292

Phase 1

Non-Small Cell Lung Cancer | Small molecule | Oncology |Eli Lilly and Company|Last Updated: Apr 16, 2026

Target and mechanism

Molecular targetRET
Target classKinase
ModalitySmall molecule

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

CONTROLLED
Total Trials1
Total Enrollment857

FDA Designations

No designations recorded

Clinical trial landscape

LOXO-292 · 1 trial · 4 indications

Phase 1 1
NCT03157128A Study of Selpercatinib (LOXO-292) in Participants With Advanced Solid Tumors, RET Fusion-Positive Solid Tumors, and Medullary Thyroid Cancer (LIBRETTO-001)Non-Small Cell Lung Cancer
ACTIVE NOT_RECRUITING857 Analytics
PHASE1ACTIVE NOT_RECRUITING
A Study of Selpercatinib (LOXO-292) in Participants With Advanced Solid Tumors, RET Fusion-Positive Solid Tumors, and Medullary Thyroid Cancer (LIBRETTO-001)
Non-Small Cell Lung CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Phase 1: Maximum Tolerated Dose (MTD)
Cycle 1 (cycle length = 28 days)

The MTD is defined as the highest dose level at which none of the first 3 treated patients, or not more than 1 of the first 6 treated patients, experiences a DLT. A DLT is any adverse events that starts on or after first administration of study drug, as defined by National Cancer Institute's Common Terminology Criteria for Adverse Events (NCI CTCAE) v5.0. * Any Grade(G) ≥3 nonhematologic toxicity, excluding * G3 AST, ALT, and/or total bilirubin elevation for \<7 days. * G3 neutropenia \<7 days * G3 thrombocytopenia without clinically significant bleeding * G3 or G4 lymphopenia. * First occurrence of G3 or G4 electrolyte abnormalities * G3 fatigue, weakness, nausea; other manageable constitutional symptom * G3 or G4 vomiting or diarrhea that lasts for \<48hours with antiemetic/antidiarrheal medication in case of G3 and \<24 hours in case of G4 * G4 manageable constitutional symptom.

Phase 1: Recommended Phase 2 Dose (RP2D)
Cycle 1 (cycle length = 28 days)

Phase 1: RP2D

Phase 2: Objective Response Rate (ORR) Based on Independent Review Committee (IRC) Assessment
Approximately for up to 7 years 8 months

Objective Response Rate was defined as the percentage of participants with best overall response of confirmed response (CR), or Partial response (PR). Response was confirmed by a repeat assessment no less than 28 days. * CR is defined as disappearance of all target lesions. * PR is defined as at least a 30% decrease in the sum of diameter (LD for non-nodal lesions and short axis diameter \[SAD\] for nodal lesions) of target lesions, taking as reference the baseline sum LD. ORR was assessed by independent review committee (IRC) using Response Evaluation Criteria in Solid Tumors (RECIST) v1.1. 95% confidence interval was calculated using Clopper-Pearson method.

Secondary Endpoints

Phase 1: Number of Participants With a Treatment-Related Adverse Event(s) (TRAE[s])
Up to 28 days
Phase 1: Number of Participants With an Abnormal Laboratory Values
Up to 28 days
Phase 2: Overall Response Rate (ORR) Based on RECIST 1.1 or RANO, as Appropriate to Tumor Type
Approximately for up to 9 years 8 months
Unlock Study Endpoints

Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Phase 1: 20 mg Selpercatinib QDEXPERIMENTALParticipants received Selpercatinib 20 milligrams (mg) administered orally once daily (QD), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 1: 20 mg Selpercatinib BIDEXPERIMENTALParticipants received Selpercatinib 20 milligrams (mg) administered orally twice daily (BID), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 1: 40 mg Selpercatinib BIDEXPERIMENTALParticipants received Selpercatinib 40 milligrams (mg) administered orally twice daily (BID), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 1: 60 mg Selpercatinib BIDEXPERIMENTALParticipants received Selpercatinib 60 milligrams (mg) administered orally twice daily (BID), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 1: 160 mg Selpercatinib QDEXPERIMENTALParticipants received Selpercatinib 160 milligrams (mg) administered orally once daily (QD), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 1: 80 mg Selpercatinib BIDEXPERIMENTALParticipants received Selpercatinib 80 milligrams (mg) administered orally twice daily (BID), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 1: 120 mg Selpercatinib BIDEXPERIMENTALParticipants received Selpercatinib 120 milligrams (mg) administered orally twice daily (BID), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 1: 160 mg Selpercatinib BIDEXPERIMENTALParticipants received Selpercatinib 160 milligrams (mg) administered orally twice daily (BID), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 1: 200 mg Selpercatinib BIDEXPERIMENTALParticipants received Selpercatinib 200 milligrams (mg) administered orally twice daily (BID), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 1: 240 mg Selpercatinib BIDEXPERIMENTALParticipants received Selpercatinib 240 milligrams (mg) administered orally twice daily (BID), in a 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 2, Cohort 1: RET Fusion Solid TumorEXPERIMENTALParticipants with Rearranged during transfection (RET) Fusion solid tumor progressed on/intolerant to standard first line therapy received Selpercatinib 160 milligrams (mg) administered orally twice daily (BID), in a continuous 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 2, Cohort 2: RET Fusion Solid Tumor Without Standard TherapyEXPERIMENTALParticipants with RET Fusion solid tumor without standard first line therapy received Selpercatinib 160 milligrams (mg) administered orally twice daily (BID), in a continuous 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 2, Cohort 3: RET Mutant MTCEXPERIMENTALParticipants with RET mutant medullary thyroid cancer (MTC) progressed on/intolerant to standard first line therapy received Selpercatinib 160 milligrams (mg) administered orally twice daily (BID), in a continuous 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 2, Cohort 4: RET Mutant MTC Without Standard TherapyEXPERIMENTALParticipants with RET mutant MTC without prior standard first line therapy or other kinase inhibitor(s) with anti-RET activity received Selpercatinib 160 milligrams (mg) administered orally twice daily (BID), in a continuous 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 2, Cohort 5: Advanced RET Altered Solid TumorEXPERIMENTALParticipants with RET altered solid tumor (cohorts 1-4, disease not measurable; MTC not eligible for Cohort 3 or 4; MTC syndrome spectrum cancer; circulating free tumor DNA \[cfDNA+\] for RET alteration not known to be present in tumor) received Selpercatinib 160 milligrams (mg) administered orally twice daily (BID), in a continuous 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.
Phase 2, Cohort 6: RET Inhibitor-Discontinued ParticipantsEXPERIMENTALParticipants otherwise eligible for Cohorts 1-5 who discontinued other RET inhibitors received Selpercatinib 160 milligrams (mg) administered orally twice daily (BID), in a continuous 28-day treatment cycle. Treatment was continued until disease progression, unacceptable toxicity, or treatment discontinuation for other reasons.

Interventions

NameTypeDescription
LOXO-292DRUGOral LOXO-292
Unlock Study Design Details

Eligibility Criteria

Age Range12 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites85

Key Inclusion Criteria: For Phase 1: * Participants with a locally advanced or metastatic solid tumor that: * Has progressed on or is intolerant to standard therapy, or * For which no standard therapy exists, or in the opinion of the Investigator, are not candidates for or would be unlikely to tol...

Countries:United StatesAustraliaCanadaDenmarkFranceGermanyHong KongIsraelItalyJapanSingaporeSouth KoreaSpainSwitzerlandTaiwanUnited Kingdom
Unlock Eligibility Criteria

Competitive Landscape -Non-Small Cell Lung Cancer 389 trials

Frequently asked questions about LOXO-292

What is LOXO-292 used for?

LOXO-292 is an investigational small molecule being developed for the treatment of non-small cell lung cancer. It is also being studied in other RET fusion-positive solid tumors and medullary thyroid cancer. The drug is currently in Phase 1 clinical development and has not been approved by regulatory authorities.

What does LOXO-292 target?

LOXO-292 targets the RET kinase, a molecular target involved in tumor growth. As a kinase inhibitor, it is designed to block the activity of RET, which can drive cancer cell proliferation. This mechanism is being evaluated in clinical trials for non-small cell lung cancer and other RET fusion-positive tumors.

Who makes LOXO-292?

LOXO-292 is being developed by Eli Lilly and Company, a pharmaceutical company traded on the stock exchange under the ticker symbol LLY. The drug is currently in Phase 1 clinical development for non-small cell lung cancer and other solid tumors.

What phase is LOXO-292 in?

LOXO-292 is in Phase 1 clinical development. It is an investigational drug, meaning it has not been approved by the FDA or other regulatory agencies. The ongoing Phase 1 trial is actively enrolling participants to evaluate the drug's safety and efficacy in advanced solid tumors.

What clinical trials is LOXO-292 in?

LOXO-292 is being studied in a Phase 1 clinical trial with the identifier NCT03157128, known as the LIBRETTO-001 study. This trial is evaluating the drug in participants with advanced solid tumors, RET fusion-positive solid tumors, and medullary thyroid cancer. The trial is active but not recruiting participants.

Is LOXO-292 the same as selpercatinib?

Yes, LOXO-292 is also known as selpercatinib. The drug is being developed by Eli Lilly and Company for the treatment of non-small cell lung cancer and other RET fusion-positive solid tumors. It is currently in Phase 1 clinical development under the trial name LIBRETTO-001.