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GB004

Phase 1

Ulcerative Colitis | Small molecule | Immunology |Gossamer Bio, Inc.|Last Updated: Jan 14, 2020

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment34
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03860896GB004 in Adult Subjects With Active Ulcerative ColitisPHASE1 COMPLETED 34Apr 24, 2019Dec 17, 2019Jan 14, 20203 United States, Georgia +1
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Study Endpoints
Primary Endpoints
Incidence of treatment emergent adverse events
56 Days

To evaluate the safety and tolerability of GB004 for 56 days in terms of incidence of treatment emergent adverse events reported.

Secondary Endpoints
Pharmacokinetics: Time to Reach Maximum Concentration (Tmax) of GB004
Day 1 to Day 28
Pharmacokinetics: Maximum Concentration (Cmax) of GB004
Day 1 to Day 28
Pharmacokinetics: Area Under the Concentration Curve (AUC) of GB004
Day 1 to Day 28
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
GB004EXPERIMENTALGB004 for oral administration daily
PlaceboPLACEBO_COMPARATORPlacebo for oral administration daily
Interventions
NameTypeDescription
GB004DRUGGB0004 high dose
PlaceboDRUGPlacebo
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Eligibility Criteria
Age Range18 Years — 74 Years
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: * Patients aged 18-74, receiving therapy for active ulcerative colitis confirmed by Mayo Score assessment, and evidence of colonic inflammation. Exclusion Criteria: * Evidence of Crohn's disease, indeterminate colitis, or presence of bacterial or parasitic infection. * Patient...

Countries:United StatesGeorgiaMoldova
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