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NPC-1C/NEO-102

Phase 1

Metastatic Pancreatic Cancer | Small molecule | Oncology |Precision BioSciences, Inc.|Last Updated: Aug 4, 2017

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment94
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01040000QUILT-3.019: Phase 2 Study of NPC-1C Chimeric Monoclonal Antibody to Treat Pancreatic and Colorectal CancerPHASE1 COMPLETED 94Jan 1, 2012Mar 1, 2017Aug 4, 20176 United States
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Study Endpoints
Primary Endpoints
Efficacy will be assessed by analysis of CT scans pre and post therapy, clinical laboratory tests, and physical examinations.
10 weeks
Efficacy OS
5 months

Using the recommended phase 2 dose (RP2D) evaluate the overall survival (OS) associated with administration of NPC-1C (NEO-102) in subjects with metastatic, locally advanced unresectable or recurrent pancreatic cancer or metastatic colorectal cancer that express NPC-1C target on tumor.

Secondary Endpoints
Safety will be assessed by analysis of adverse experiences, clinical laboratory tests, and physical examinations.
10 weeks
Pharmacokinetics and select immune responses to the antibody will be assessed.
10 weeks
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
NPC-1C/NEO-102EXPERIMENTAL -
Interventions
NameTypeDescription
NPC-1C/NEO-102DRUGSubjects will receive NPC-1C at a dose of 3.0 mg/kg. NPC-1C will be given intravenously (by vein) over approximately 1-6 hours, once every 2 weeks for 4 doses per course. Courses will be repeated in the absence of disease progression or unacceptable toxicity.
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Eligibility Criteria
Age Range18 Years — 99 Years
SexALL
Healthy VolunteersNo
Study Sites6

INCLUSION CRITERIA: * Age: \>/= 18 * Diagnosis: * Histologically confirmed recurrent, locally advanced unresectable or metastatic adenocarcinoma of the pancreas who have progressed after front line chemotherapy, OR * Histologically confirmed metastatic colorectal adenocarcinoma who have progre...

Countries:United States
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