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custirsen

Phase 3

Non-small Cell Lung Cancer | Small molecule | Oncology |Achieve Life Sciences, Inc.|Last Updated: Apr 15, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedACTIVE_CONTROLLEDDMC
Total Trials2
Total Enrollment749

FDA Designations

No designations recorded

Clinical trial landscape

custirsen · 3 trials · 2 indications

Phase 3 1Phase 1 2
NCT01630733A Multinational, Randomized, Open-Label Study of Custirsen In Patients With Advanced or Metastatic (Stage IV) Non-Small Cell Lung CancerNon-Small Cell Lung Cancer
COMPLETED664 Analytics
PHASE3COMPLETED
A Multinational, Randomized, Open-Label Study of Custirsen In Patients With Advanced or Metastatic (Stage IV) Non-Small Cell Lung Cancer
Non-Small Cell Lung CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Overall Survival: All Randomized Population
From randomization to death or last known date alive (up to 1331 days for Docetaxel arm and up to 1271 days for Docetaxel + Custirsen arm)

Overall survival time is defined as the number of days from the date of randomization until the date of death from any cause. Participants who did not achieve the event (death) at the time of the analysis or who dropped out before completing the survival follow-up period will be censored at the date they were last known to be alive (i.e., right censored). Partial or missing dates of death or last contact were imputed.

Overall Survival: Stratified by Histology - Squamous vs. Non-Squamous
From randomization to death or last known date alive (up to 1331 days for Docetaxel arm and up to 1271 days for Docetaxel + Custirsen arm)

Overall survival time is defined as the number of days from the date of randomization until the date of death from any cause. Participants who did not achieve the event (death) at the time of the analysis or who dropped out before completing the survival follow-up period will be censored at the date they were last known to be alive (i.e., right censored). Partial or missing dates of death or last contact were imputed.

Individually-corrected QT interval (QTcI)
Up to 23.5 hours after the start of study drug infusion on Day 7

The primary ECG variable and endpoint for this study is the time-matched change from baseline in QTcI method on day 7 at each time point. Holter ECGs will be performed at baseline (day -1) and prior to the start of infusion on day 7 and 1, 2 (end of infusion), 2.5, 3, 4, 5, 6, 8, 12, 16, 20, and 23.5 hours after the start of infusion.

Objective Response Rate of OGX-011 in Combination With Gemcitabine/Platinum-based Regimen
Based on assessments at baseline and after Cycles 2, 4, and 6. All subjects were followed for survival for a minimum of 3 years after the first dose of OGX-011 or until death.

Per RECIST Criteria V 1.0 and based on radiographic evaluations a subject was defined as having an objective response (OR) if the subject achieved either a confirmed partial response (PR) or confirmed complete response (CR). The evaluations were conducted after every two cycles of treatment for a maximum of 6 cycles. CR: disappearance of clinical/radiological evidence of tumor. PR: \>= 30% decrease in the sum of the longest diameter of target lesions. SD: did not fulfill the criteria for CR or PR but not progressive disease.

Secondary Endpoints

Fridericia-corrected QT interval (QTcF)
Up to 23.5 hours after study drug infusion on Day 7
Heart rate, PR interval, QRS interval and uncorrected QT interval
Up to 23.5 hours after study drug infusion on Day 7
ECG morphological patterns
Up to 23.5 hours after study drug infusion on Day 7
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Custirsen + DocetaxelEXPERIMENTALCustirsen: Three loading doses of custirsen 640 mg intravenously (IV) over 2 hours administered in 5 to 9 days prior to Day 1 of Cycle 1, then custirsen 640 mg IV weekly every 21-day cycle. Docetaxel: 75 mg/m\^2 IV over 1 hour on Day 1 of every 21-day cycle. Continue treatment until disease progression, unacceptable toxicity, withdrawal of consent, or protocol-specified parameters to stop.
DocetaxelACTIVE_COMPARATORDocetaxel: 75 mg/m\^2 IV over 1 hour on Day 1 of every 21-day cycle. Continue treatment until disease progression, unacceptable toxicity, withdrawal of consent, or protocol-specified parameters to stop.
Group 1EXPERIMENTALGroup 1: investigational product (custirsen) will receive: * 320 mg of custirsen + 5 mg of dexamethasone on day 1 * 480 mg of custirsen + 5 mg of dexamethasone on day 3 * 640 mg of custirsen + 3 mg of dexamethasone on day 5 * 640 mg of custirsen on day 7 under fasting conditions
Group 2PLACEBO_COMPARATORGroup 2: placebo (normal saline) will receive: * placebo + 5 mg of dexamethasone on day 1 * placebo + 5 mg of dexamethasone on day 3 * placebo + 3 mg of dexamethasone on day 5 * placebo on day 7 under fasting conditions
Group 3ACTIVE_COMPARATORGroup 3: positive control (moxifloxacin) will receive: * placebo + 5 mg of dexamethasone on day 1 * placebo + 5 mg of dexamethasone on day 3 * placebo + 3 mg of dexamethasone on day 5 * 400 mg of moxifloxacin + placebo (immediately after moxifloxacin administration) on day 7 under fasting conditions

Interventions

NameTypeDescription
CustirsenDRUG -
DocetaxelDRUG -
PlaceboDRUGPlacebo (commercially available normal saline) will be administered iv using an infusion pump over a 2-hour period.
MoxifloxacinDRUGMoxifloxacin (400 mg) will be administered orally with 240 mL of room temperature still water.
custirsen sodiumDRUGCustirsen sodium (OGX-011) was to be infused intravenously over 2 hours on Days -7, -5, and 3 of Cycle 1 (pretreatment loading dose). OGX 011 was then to be infused for 2 hours weekly on Days 1, 8, and 15 of a 21-day cycle. Gemcitabine (GEM) was to be infused intravenously for 30 minutes on Days 1 and 8 and either cisplatin (CIS) or carboplatin (CARBO) were to be infused intravenously on Day 1 of this 21-day cycle. Patients were to receive a maximum of 6 cycles (1 cycle = 21 days)
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites78

Inclusion Criteria: 1. Patients must have a histologically or cytologically confirmed, unresectable, advanced or metastatic (Stage IV per American Joint Committee on Cancer 7th edition Tumor size, lymph Nodes affected, Metastases staging) non-small cell lung cancer (NSCLC). 2. Males or females ≥ 18...

Countries:United StatesAustraliaGermanyHungaryIsraelItalyNew ZealandPolandRussiaSouth KoreaSpainTaiwanThailandUkraineCanada
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Competitive Landscape -Non-Small Cell Lung Cancer 393 trials

Frequently asked questions about custirsen

What is Custirsen used for?

Custirsen is an investigational small molecule being studied for use in non-small cell lung cancer, prostate cancer, cardiac conduction and repolarization, and cancer. It is currently in Phase 1 clinical development and is not approved by the FDA.

Who makes Custirsen?

Custirsen is being developed by Achieve Life Sciences, Inc., a company traded under the ticker symbol ACHV. The drug is currently in Phase 1 clinical development.

What phase is Custirsen in?

Custirsen is in Phase 1 clinical development. It is an investigational drug and has not been approved by the FDA. Clinical trials have been completed for its evaluation in various conditions.

What clinical trials is Custirsen in?

Custirsen has been studied in several completed clinical trials, including NCT00138658 for non-small cell lung cancer, NCT00327340 and NCT01188187 for prostate cancer, and NCT01874561 for cardiac conduction and repolarization. These trials have been completed.

Is Custirsen the same as OGX-011?

Yes, Custirsen is also known as OGX-011. Clinical trials have used the name OGX-011 to refer to this drug, including studies in non-small cell lung cancer and prostate cancer.