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UBX0101

Phase 2

Osteoarthritis, Knee | Small molecule | Musculoskeletal |Unity Biotechnology, Inc.|Last Updated: Dec 29, 2021

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials2
Total Enrollment261

FDA Designations

No designations recorded

Clinical trial landscape

UBX0101 · 3 trials · 2 indications

Phase 2 1Phase 1 2
NCT04129944A Study to Assess the Safety and Efficacy of a Single Dose of UBX0101 in Patients With Osteoarthritis of the KneeOsteoarthritis, Knee
COMPLETED183 Analytics
PHASE2COMPLETED
A Study to Assess the Safety and Efficacy of a Single Dose of UBX0101 in Patients With Osteoarthritis of the Knee
Osteoarthritis, KneeUnlock trial analytics

Study Endpoints

Primary Endpoints

Change From Baseline to Week 12 of the Western Ontario and McMaster Universities Osteoarthritis Index Pain Subscale (WOMAC-A) Score in Patients Receiving a Single Dose of UBX0101 Versus Those Receiving Placebo
Baseline to Week 12

WOMAC-A is assessed by a Likert scale on a range from 0 (none) to 4 (extreme), with higher scores indicating higher levels of pain

Safety and tolerability of a single and repeat dose intra-articular administration of UBX0101 evaluated by the incidence of serious and non-serious adverse events
Baseline to Week 24
Safety and tolerability of a single intra articular injection of UBX0101 evaluated by the incidence of serious and non-serious adverse events
12 weeks

Secondary Endpoints

Change From Baseline to Week 12 of the Western Ontario and McMaster Universities Osteoarthritis Index Function Subscale (WOMAC-C) Score in Patients Receiving a Single Dose of UBX0101 Versus Those Receiving Placebo
Baseline to Week 12
Change From Baseline to Week 12 of the Weekly Mean of the Average Daily Pain (ADP) Intensity Scores on the 11-point Numeric Rating Scale (NRS) in Patients Receiving a Single Dose of UBX0101 Versus Those Receiving Placebo
Baseline to Week 12
Change From Baseline (Over the Entire 24-week Period, Including Both the Primary Study Period and the 12-week Follow-up Period) to Week 24 for the WOMAC-A, NRS, and WOMAC-C Scores in Patients Receiving a Dose of UBX0101 Versus Those Receiving Placebo
Baseline to Week 24
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Study Design & Arms

AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
PlaceboPLACEBO_COMPARATOR -
UBX0101 0.5 mgEXPERIMENTAL -
UBX0101 2.0 mgEXPERIMENTAL -
UBX0101 4.0 mgEXPERIMENTAL -
UBX0101 single dose (SD)EXPERIMENTALCohort 1 (n=18): UBX0101 8.0 mg or placebo IA at Week 0 Patients will be randomized in a 2:1 ratio to UBX0101 and placebo
UBX0101 repeat dose (RD)EXPERIMENTALCohort 2 (n=18): UBX0101 4.0 mg or placebo IA at Weeks 0 and 4 Patients will be randomized in a 2:1 ratio to UBX0101 and placebo
Part A: UBX0101EXPERIMENTALPart A: UBX0101, single intra-articular injection, ascending dose
Part A: PlaceboPLACEBO_COMPARATORPart A: Placebo, single intra-articular injection, ascending dose
Part B: UBX0101EXPERIMENTALPart B: UBX0101, single intra-articular injection, fixed dose
Part B: PlaceboPLACEBO_COMPARATORPart B: Placebo, single intra-articular injection, fixed dose

Interventions

NameTypeDescription
UBX0101DRUGInvestigational drug intra-articular injection
PlaceboOTHERPlacebo intra-articular injection
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Eligibility Criteria

Age Range40 Years to 85 Years
SexALL
Healthy VolunteersNo
Study Sites20

Key Inclusion Criteria: * Patients who are ambulatory with a diagnosis of OA of the knee and who have baseline pain with a mean of ≥ 4 and ≤ 9 on the 11-point (0-10) average daily pain NRS for at least five of seven days during the Screening period. * Kellgren-Lawrence grade of 1-4 on a weight-bear...

Countries:United States
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Frequently asked questions about UBX0101

What is UBX0101 used for?

UBX0101 is an investigational small molecule being developed for the treatment of osteoarthritis of the knee. It is designed to address the underlying cellular mechanisms of the disease, though the specific molecular target has not been disclosed. The drug is administered as a single dose or repeat doses directly into the knee joint.

Who makes UBX0101?

UBX0101 is being developed by Unity Biotechnology, Inc., a company traded on the NASDAQ under the ticker symbol UBX. The company is focused on developing therapies that target age-related diseases, including osteoarthritis.

What phase is UBX0101 in?

UBX0101 has completed Phase 1 and Phase 2 clinical trials. The Phase 1 trials assessed safety and tolerability, while the Phase 2 trial evaluated safety and efficacy of a single dose. All three trials are completed, and the drug remains investigational, not yet approved by regulatory authorities.

What clinical trials is UBX0101 in?

UBX0101 has been studied in three completed clinical trials: NCT03513016 (Phase 1, safety and tolerability, 78 patients), NCT04129944 (Phase 2, safety and efficacy of a single dose, 183 patients), and NCT04229225 (Phase 1, single and repeat dose administration, 35 patients). All trials were conducted in the United States.

Is UBX0101 the same as any other drug?

No alternative names for UBX0101 have been disclosed. It is identified solely by its compound designation UBX0101 in clinical trial registries and scientific literature. No other brand or generic names are associated with this investigational drug.